Polyethylenimine-modified pluronics (PCMs) improve morpholino oligomer delivery in cell culture and dystrophic mdx mice

Molecular Therapy

Volumn 21, Issue 1, 2013, Pages 210-216

  Wang, Mingxing ^a   Wu, Bo ^a   Lu, Peijuan ^a   Cloer, Caryn ^a   Tucker, Jay D ^a,b   Lu, Qilong ^a  

^a Neuromuscular/ALS Center   (United States)

^b UNIVERSITY OF NORTH CAROLINA AT CHARLOTTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COPOLYMER; DYSTROPHIN; GREEN FLUORESCENT PROTEIN; MORPHOLINO OLIGONUCLEOTIDE; PLURONIC COPOLYMER; POLYETHYLENEIMINE; UNCLASSIFIED DRUG;

ANIMAL CELL CULTURE; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CELL ASSAY; CONTROLLED STUDY; CYTOTOXICITY; DRUG DELIVERY SYSTEM; DRUG EFFICACY; DRUG FORMULATION; DRUG SAFETY; EXON SKIPPING; HYDROPHILICITY; IN VITRO STUDY; IN VIVO STUDY; LIPOPHILICITY; MOLECULAR WEIGHT; MOUSE; MUSCULAR DYSTROPHY; MYOBLAST; NONHUMAN; PROCESS OPTIMIZATION;

MUS;

EID: 84871927085     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2012.236     Document Type: Article

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