Engineering U7snRNA gene to reframe transcripts

Methods in Molecular Biology

Volumn 867, Issue , 2012, Pages 259-271

  Goyenvalle, Aurélie ^a  

^a UNIVERSITY OF OXFORD   (United Kingdom)

Author keywords

Antisense; Ducenne muscular dystrophy; Exon skipping; Exonic splicing silencer; Gene therapy; U7snRNA

Indexed keywords

DYSTROPHIN; SMALL NUCLEAR RNA; U7 SMALL NUCLEAR RNA;

ANIMAL; ARTICLE; CELL LINE; DUCHENNE MUSCULAR DYSTROPHY; EXON; GENE EXPRESSION; GENE THERAPY; GENE VECTOR; GENETIC TRANSDUCTION; GENETICS; HUMAN; LENTIVIRINAE; METABOLISM; METHODOLOGY; MOUSE; MYOBLAST;

ANIMALS; CELL LINE; DYSTROPHIN; EXONS; GENE EXPRESSION; GENE THERAPY; GENETIC VECTORS; HUMANS; LENTIVIRUS; MICE; MUSCULAR DYSTROPHY, DUCHENNE; MYOBLASTS; RNA, SMALL NUCLEAR; TRANSDUCTION, GENETIC;

EID: 84859824278     PISSN: 10643745     EISSN: None     Source Type: Book Series    
DOI: 10.1007/978-1-61779-767-5_17     Document Type: Article

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