Double-target antisense U7 snRNAs promote efficient skipping of an aberrant exon in three human β-thalassemic mutations

Human Molecular Genetics

Volumn 8, Issue 13, 1999, Pages 2415-2423

  Suter, Daniel ^a   Tomasini, Reto ^a   Reber, Ueli ^a   Gorman, Linda ^b   Kole, Ryszard ^b   Schümperli, Daniel ^a  

^a UNIVERSITY OF BERN   (Switzerland)

^b UNIVERSITY OF NORTH CAROLINA SCHOOL OF MEDICINE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

BETA GLOBIN; COMPLEMENTARY RNA; MESSENGER RNA; SMALL NUCLEAR RNA;

ARTICLE; BETA THALASSEMIA; EXON; GENE MUTATION; GENE SEQUENCE; HELA CELL; HUMAN; HUMAN CELL; INTRON; PRIORITY JOURNAL; RNA SPLICING;

EID: 0032714173     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/8.13.2415     Document Type: Article

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