Inhibition of mutant huntingtin expression by RNA duplex targeting expanded CAG repeats

Nucleic Acids Research

Volumn 39, Issue 13, 2011, Pages 5578-5585

  Fiszer, Agnieszka ^a   Mykowska, Agnieszka ^a   Krzyzosiak, Wlodzimierz J ^a  

^a INSTITUTE OF BIOORGANIC CHEMISTRY   (Poland)

Author keywords

[No Author keywords available]

Indexed keywords

ADENINE; CYTOSINE; DOUBLE STRANDED RNA; GUANINE; HUNTINGTIN; MESSENGER RNA; SMALL INTERFERING RNA; URACIL;

ALLELE; ARTICLE; CELL LINE; CONTROLLED STUDY; DRUG TARGETING; GENE ACTIVATION; GENE MUTATION; GENE SILENCING; HUMAN; HUMAN CELL; HUNTINGTON CHOREA; INHIBITION KINETICS; PRIORITY JOURNAL; PROTEIN EXPRESSION; RNA INTERFERENCE; TRINUCLEOTIDE REPEAT;

ALLELES; CELLS, CULTURED; HUMANS; MUTATION; NERVE TISSUE PROTEINS; NUCLEAR PROTEINS; RNA INTERFERENCE; RNA, DOUBLE-STRANDED; RNA, MESSENGER; RNA, SMALL INTERFERING; TRINUCLEOTIDE REPEAT EXPANSION;

EID: 80052250736     PISSN: 03051048     EISSN: 13624962     Source Type: Journal    
DOI: 10.1093/nar/gkr156     Document Type: Article

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