Allele-specific silencing of dominant disease genes

Proceedings of the National Academy of Sciences of the United States of America

Volumn 100, Issue 12, 2003, Pages 7195-7200

  Miller, Victor M ^a   Xia, Haibin ^a   Marrs, Ginger L ^a   Gouvion, Cynthia M ^a   Lee, Gloria ^a   Davidson, Beverly L ^a   Paulson, Henry L ^a  

^a UNIVERSITY OF IOWA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; NUCLEOTIDE; POLYGLUTAMINE; RNA;

ALLELE; ANIMAL CELL; ARTICLE; CERCOPITHECIDAE; DEGENERATIVE DISEASE; DNA SEQUENCE; FRONTOTEMPORAL DEMENTIA; GENE; GENE SILENCING; HUMAN; HUMAN CELL; IMMUNOBLOTTING; IMMUNOFLUORESCENCE; MACHADO JOSEPH DISEASE; MUTATION; NONHUMAN; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; SINGLE NUCLEOTIDE POLYMORPHISM; SPINOCEREBELLAR DEGENERATION;

ALLELES; ANIMALS; BASE SEQUENCE; COS CELLS; DEMENTIA; GENE SILENCING; GENE THERAPY; GENES, DOMINANT; GENETIC DISEASES, INBORN; HELA CELLS; HUMANS; MACHADO-JOSEPH DISEASE; PEPTIDES; POINT MUTATION; POLYMORPHISM, SINGLE NUCLEOTIDE; RNA, SMALL INTERFERING; TAU PROTEINS;

ANIMALIA; CERCOPITHECIDAE; MAMMALIA;

EID: 0038132996     PISSN: 00278424     EISSN: None     Source Type: Journal    
DOI: 10.1073/pnas.1231012100     Document Type: Article

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