Magnetic resonance imaging-guided delivery of adeno-associated virus type 2 to the primate brain for the treatment of lysosomal storage disorders

Human Gene Therapy

Volumn 21, Issue 9, 2010, Pages 1093-1103

  Salegio, E Aguilar ^a   Kells, A P ^a   Richardson, R M ^a   Hadaczek, P ^a   Forsayeth, J ^a   Bringas, J ^a   Sardi, S P ^b   Passini, M A ^b   Shihabuddin, L S ^b   Cheng, S H ^b   Fiandaca, M S ^a   Bankiewicz, K S ^a  

^a UNIVERSITY OF CALIFORNIA   (United States)

^b Genzyme   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

EPITOPE; HEMAGGLUTININ; PARVOVIRUS VECTOR; SPHINGOMYELIN PHOSPHODIESTERASE;

ANIMAL EXPERIMENT; ANIMAL TISSUE; ARTICLE; BRAIN STEM; CINGULATE GYRUS; CONTROLLED STUDY; DRUG DELIVERY SYSTEM; DRUG DISTRIBUTION; EXPERIMENTAL MONKEY; FRONTAL CORTEX; GENETIC TRANSDUCTION; LYSOSOME STORAGE DISEASE; MOTOR CORTEX; NONHUMAN; NUCLEAR MAGNETIC RESONANCE IMAGING; PREFRONTAL CORTEX; PROTEIN EXPRESSION; SOMATOSENSORY CORTEX; THALAMUS;

ANIMALS; BRAIN; DEPENDOVIRUS; GENE THERAPY; GENE TRANSFER TECHNIQUES; HUMANS; INTRAOPERATIVE CARE; LYSOSOMAL STORAGE DISEASES; MAGNETIC RESONANCE IMAGING; NEURONS; PRIMATES; SPHINGOMYELIN PHOSPHODIESTERASE; TRANSDUCTION, GENETIC; TRANSGENES;

ADENO-ASSOCIATED VIRUS - 2; PRIMATES;

EID: 77957830388     PISSN: 10430342     EISSN: None     Source Type: Journal    
DOI: 10.1089/hum.2010.040     Document Type: Article

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