TgAAG76, an adeno-associated virus delivered gene therapy for the potential treatment of vision loss caused by RPE65 gene abnormalities

Current Opinion in Molecular Therapeutics

Volumn 12, Issue 4, 2010, Pages 471-477

  Stieger, K ^a  

^a JUSTUS LIEBIG UNIVERSITY   (Germany)

Author keywords

[No Author keywords available]

Indexed keywords

ADENOVIRUS VECTOR; COMPLEMENTARY DNA; TGAAG76; UNCLASSIFIED DRUG; CARRIER PROTEIN; CIS TRANS ISOMERASE; EYE PROTEIN; RETINOID ISOMEROHYDROLASE;

B WAVE; CLONING; DOG; DRUG METABOLISM; DRUG SAFETY; DRUG SYNTHESIS; FOLLOW UP; GENE EXPRESSION; GENE MUTATION; GENE THERAPY; HUMAN; LEBER CONGENITAL AMAUROSIS; LOW DRUG DOSE; MOBILIZATION; NONHUMAN; OPTICAL COHERENCE TOMOGRAPHY; POLYADENYLATION; PROMOTER REGION; PROTEIN EXPRESSION; RETINA DISEASE; REVIEW; SIDE EFFECT; SIMIAN VIRUS; T LYMPHOCYTE; VISION; VISUAL ACUITY; ANIMAL; BLINDNESS; BOVINAE; DEPENDOPARVOVIRUS; DRUG SCREENING; GENETICS; PATENT; STRUCTURE ACTIVITY RELATION; TRANSGENE;

ANIMALS; BLINDNESS; CARRIER PROTEINS; CATTLE; DEPENDOVIRUS; DRUG EVALUATION, PRECLINICAL; EYE PROTEINS; GENE THERAPY; HUMANS; PATENTS AS TOPIC; STRUCTURE-ACTIVITY RELATIONSHIP; TRANSGENES; CIS-TRANS-ISOMERASES; GENETIC THERAPY;

ADENO-ASSOCIATED VIRUS; BOVINAE;

EID: 77955343579     PISSN: 14648431     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Review

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