Physiological transgene regulation and functional complementation of a neurological disease gene deficiency in neurons

Molecular Therapy

Volumn 17, Issue 9, 2009, Pages 1517-1526

  Peruzzi, Pier Paolo ^a   Lawler, Sean E ^a   Senior, Steve L ^b   Dmitrieva, Nina ^a   Edser, Pauline A H ^b   Gianni, Davide ^a   Chiocca, E Antonio ^a   Wade Martins, Richard ^b  

^a THE OHIO STATE UNIVERSITY COLLEGE OF MEDICINE   (United States)

^b UNIVERSITY OF OXFORD   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA SYNUCLEIN; TAU PROTEIN;

ANIMAL CELL; ANIMAL TISSUE; ARTICLE; BACTERIAL ARTIFICIAL CHROMOSOME; CONTROLLED STUDY; DISEASE PREDISPOSITION; ENZYME LINKED IMMUNOSORBENT ASSAY; GENE EXPRESSION; GENE FUNCTION; GENE LOCUS; GENE MUTATION; GENETIC TRANSDUCTION; GENETIC VARIABILITY; HERPES SIMPLEX VIRUS 1; HUMAN; HUMAN CELL; IMMUNOCYTOCHEMISTRY; MOUSE; NERVE CELL; NERVE CELL DIFFERENTIATION; NEUROLOGIC DISEASE; NONHUMAN; PHENOTYPE; RAT; REGULATORY MECHANISM;

ALPHA-SYNUCLEIN; ANIMALS; CELLS, CULTURED; CHROMOSOMES, ARTIFICIAL, BACTERIAL; GENE THERAPY; GENETIC VECTORS; HUMANS; IMMUNOHISTOCHEMISTRY; MICE; NERVOUS SYSTEM DISEASES; NEURONS; RATS; TAU PROTEINS; TRANSGENES;

BACTERIA (MICROORGANISMS); HUMAN HERPESVIRUS 1; MUS;

EID: 69949172894     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2009.64     Document Type: Article

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