DRG-targeted helper-dependent adenoviruses mediate selective gene delivery for therapeutic rescue of sensory neuronopathies in mice

Journal of Clinical Investigation

Volumn 119, Issue 7, 2009, Pages 2100-2112

  Terashima, Tomoya ^a   Oka, Kazuhiro ^a   Kritz, Angelika B ^b   Kojima, Hideto ^a   Baker, Andrew H ^b   Chan, Lawrence ^a  

^a BAYLOR COLLEGE OF MEDICINE   (United States)

^b UNIVERSITY OF GLASGOW   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

BETA N ACETYLHEXOSAMINIDASE BETA CHAIN; CRE RECOMBINASE; INTEGRASE;

ADENOVIRIDAE; ANIMAL; C57BL MOUSE; CELL CULTURE; GENE THERAPY; GENE TRANSFER; GENE VECTOR; GENETICS; MALE; METABOLISM; MOUSE; SANDHOFF DISEASE; SPINAL GANGLION; TRANSGENE;

ADENOVIRIDAE; ANIMALS; BETA-HEXOSAMINIDASE BETA CHAIN; CELLS, CULTURED; GANGLIA, SPINAL; GENE TRANSFER TECHNIQUES; GENETIC THERAPY; GENETIC VECTORS; INTEGRASES; MALE; MICE; MICE, INBRED C57BL; SANDHOFF DISEASE; TRANSGENES;

EID: 68849128353     PISSN: 00219738     EISSN: 15588238     Source Type: Journal    
DOI: 10.1172/jci39038     Document Type: Article

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