The treatment of hemophilia A: From protein replacement to AAV-mediated gene therapy

Biotechnology Letters

Volumn 31, Issue 3, 2009, Pages 321-328

  Youjin, Shen ^a   Jun, Yin ^a  

^a THE SECOND AFFILIATED HOSPITAL OF SHANTOU UNIVERSITY MEDICAL COLLEGE   (China)

Author keywords

Adeno associated virus; Factor VIII; Gene therapy; Hemophilia A

Indexed keywords

COAGULATION; VIRUSES;

ADENO-ASSOCIATED VIRUS; BLEEDING DISORDERS; BLOOD COAGULATIONS; CLINICAL APPLICATIONS; ESSENTIAL COMPONENTS; FACTOR VIII; GENE THERAPY; GENETIC DISEASE; HEMOPHILIA A; HIGH COSTS; LIFE EXPECTANCIES; SOMATIC CELLS;

GENETIC ENGINEERING;

BLOOD CLOTTING FACTOR 8;

ADENO ASSOCIATED VIRUS; GENE THERAPY; GENE VECTOR; GENETICS; HEMOPHILIA A; HUMAN; METHODOLOGY; REVIEW;

DEPENDOVIRUS; FACTOR VIII; GENE THERAPY; GENETIC VECTORS; HEMOPHILIA A; HUMANS;

ADENO-ASSOCIATED VIRUS;

EID: 59149093795     PISSN: 01415492     EISSN: 15736776     Source Type: Journal    
DOI: 10.1007/s10529-008-9869-0     Document Type: Review

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