Retinitis pigmentosa: Genetics and gene-based approaches to therapy

Expert Review of Ophthalmology

Volumn 3, Issue 4, 2008, Pages 417-429

  Kannabiran, Chitra ^a  

^a Hyderabad Eye Research Foundation   (India)

Author keywords

Gene therapy; Genetics; Mutation; Retinal dystrophy; Retinitis pigmentosa

Indexed keywords

ABC TRANSPORTER A1; ADENOVIRUS VECTOR; BRAIN DERIVED NEUROTROPHIC FACTOR; CERAMIDE KINASE; CILIARY NEUROTROPHIC FACTOR; DNA TOPOISOMERASE; FASCIN; FIBROBLAST GROWTH FACTOR 2; G PROTEIN COUPLED RECEPTOR; GUANYLATE CYCLASE ACTIVATOR; HOMEODOMAIN PROTEIN; INOSINATE DEHYDROGENASE; LENTIVIRUS VECTOR; LEUCINE ZIPPER PROTEIN; OUTER MEMBRANE PROTEIN; PARVOVIRUS VECTOR; PERIPHERIN; PHOSPHODIESTERASE; PHOSPHODIESTERASE 6; PIGMENT EPITHELIUM DERIVED FACTOR; PROTEIN TYROSINE KINASE; RETINA S ANTIGEN; RETINOID BINDING PROTEIN; RETINOL ACYLTRANSFERASE; RETROVIRUS VECTOR; RHODOPSIN; SEMAPHORIN; SMALL INTERFERING RNA; UNCLASSIFIED DRUG; UNINDEXED DRUG; X LINKED INHIBITOR OF APOPTOSIS;

AUTOSOMAL INHERITANCE; CAT; CLINICAL TRIAL; DOG; DRUG EFFICACY; DRUG SAFETY; EXTRACHROMOSOMAL INHERITANCE; GENE IDENTIFICATION; GENE MUTATION; GENE THERAPY; GENETIC ANALYSIS; HIGH THROUGHPUT SCREENING; HUMAN; MUTATION RATE; NONHUMAN; PATHOGENESIS; PHENOTYPE; PHOTORECEPTOR; RETINITIS PIGMENTOSA; REVIEW; RNA INTERFERENCE; VIRAL GENE DELIVERY SYSTEM; X CHROMOSOMAL INHERITANCE;

EID: 55149118368     PISSN: 17469899     EISSN: 17469902     Source Type: Journal    
DOI: 10.1586/17469899.3.4.417     Document Type: Review

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