메뉴 건너뛰기




Volumn 105, Issue 2-4, 2004, Pages 435-441

Sequence-specific modification of mouse genomic DNA mediated by gene targeting techniques

Author keywords

[No Author keywords available]

Indexed keywords

BLOOD CLOTTING FACTOR 9; DNA FRAGMENT; DYSTROPHIN; GENOMIC DNA; GLUCURONOSYLTRANSFERASE; LIPOSOME; OLIGONUCLEOTIDE; POLYETHYLENEIMINE DERIVATIVE;

EID: 3242798871     PISSN: 14248581     EISSN: None     Source Type: Journal    
DOI: 10.1159/000078216     Document Type: Review
Times cited : (13)

References (51)
  • 2
    • 0031734471 scopus 로고    scopus 로고
    • Stable and inheritable changes in genotype and phenotype of albino melanocytes induced by an RNA-DNA oligonucleotide
    • Alexeev V and Yoon K: Stable and inheritable changes in genotype and phenotype of albino melanocytes induced by an RNA-DNA oligonucleotide. Nat Biotechnol 16:1343-1346 (1998).
    • (1998) Nat Biotechnol , vol.16 , pp. 1343-1346
    • Alexeev, V.1    Yoon, K.2
  • 4
    • 0035979246 scopus 로고    scopus 로고
    • Effects of DNA sequence and structure on binding of RecA to single-stranded DNA
    • Bar-Ziv R, Libchaber A: Effects of DNA sequence and structure on binding of RecA to single-stranded DNA. Proc Natl Acad Sci USA 98:9068-9073 (2001).
    • (2001) Proc Natl Acad Sci USA , vol.98 , pp. 9068-9073
    • Bar-Ziv, R.1    Libchaber, A.2
  • 5
    • 0038440559 scopus 로고    scopus 로고
    • Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping
    • Bertoni C, Lau C, Rando TA: Restoration of dystrophin expression in mdx muscle cells by chimeraplast-mediated exon skipping. Hum Mol Genet 12:1087-1099 (2003).
    • (2003) Hum Mol Genet , vol.12 , pp. 1087-1099
    • Bertoni, C.1    Lau, C.2    Rando, T.A.3
  • 6
    • 0035868383 scopus 로고    scopus 로고
    • Affinity of mismatch-binding protein MutS for heteroduplexes containing different mismatches
    • Brown J, Brown T, Fox KR: Affinity of mismatch-binding protein MutS for heteroduplexes containing different mismatches. Biochem J 354(Pt 3):627-633 (2001).
    • (2001) Biochem J , vol.354 , Issue.3 PART , pp. 627-633
    • Brown, J.1    Brown, T.2    Fox, K.R.3
  • 7
    • 0036272055 scopus 로고    scopus 로고
    • Isolation of CF cell lines corrected at DeltaF508-CFTR locus by SFHR-mediated targeting
    • Bruscia E, Sangiuolo F, Sinibaldi, Goncz KK, Novelli G, Gruenert DC: Isolation of CF cell lines corrected at DeltaF508-CFTR locus by SFHR-mediated targeting. Gene Ther 9:683-685 (2002).
    • (2002) Gene Ther , vol.9 , pp. 683-685
    • Bruscia, E.1    Sangiuolo, F.2    Sinibaldi3    Goncz, K.K.4    Novelli, G.5    Gruenert, D.C.6
  • 10
    • 0033981578 scopus 로고    scopus 로고
    • Triple-helix formation induces recombination in mammalian cells via a nucleotide excision repair-dependent pathway
    • Faruqi AF, Datta HJ, Carroll D, Seidman MM, Glazer PM: Triple-helix formation induces recombination in mammalian cells via a nucleotide excision repair-dependent pathway. Mol Cell Biol 20:990-1000 (2000).
    • (2000) Mol Cell Biol , vol.20 , pp. 990-1000
    • Faruqi, A.F.1    Datta, H.J.2    Carroll, D.3    Seidman, M.M.4    Glazer, P.M.5
  • 11
    • 0033987325 scopus 로고    scopus 로고
    • Site-directed alteration of genomic DNA by small-fragment homologous replacement
    • Goncz KK, Gruenert DC: Site-directed alteration of genomic DNA by small-fragment homologous replacement. Methods Mol Biol 133:85-99 (2000).
    • (2000) Methods Mol Biol , vol.133 , pp. 85-99
    • Goncz, K.K.1    Gruenert, D.C.2
  • 12
    • 0031796816 scopus 로고    scopus 로고
    • Targeted replacement of normal and mutant CFTR sequences in human airway epithelial cells using DNA fragments
    • Goncz KK, Kunzelmann K, Xu Z, Gruenert DC: Targeted replacement of normal and mutant CFTR sequences in human airway epithelial cells using DNA fragments. Hum Mol Genet 7:1913-1919 (1998).
    • (1998) Hum Mol Genet , vol.7 , pp. 1913-1919
    • Goncz, K.K.1    Kunzelmann, K.2    Xu, Z.3    Gruenert, D.C.4
  • 15
    • 0000169593 scopus 로고    scopus 로고
    • Gene correction with small DNA fragments
    • Gruenert DC: Gene correction with small DNA fragments. Curr Res Molec Ther 1:607-613 (1998).
    • (1998) Curr Res Molec Ther , vol.1 , pp. 607-613
    • Gruenert, D.C.1
  • 16
    • 0032844859 scopus 로고    scopus 로고
    • Opportunities and challenges in targeting genes for therapy
    • Gruenert DC: Opportunities and challenges in targeting genes for therapy. Gene Ther 6:1347-1348 (1999).
    • (1999) Gene Ther , vol.6 , pp. 1347-1348
    • Gruenert, D.C.1
  • 21
  • 22
    • 0035831649 scopus 로고    scopus 로고
    • In vivo and in vitro correction of the mdx dystrophin gene nonsense mutation by short-fragment homologous replacement
    • Kapsa R, Quigley A, Lynch GS, et al: In vivo and in vitro correction of the mdx dystrophin gene nonsense mutation by short-fragment homologous replacement. Hum Gene Ther 12:629-642 (2001).
    • (2001) Hum Gene Ther , vol.12 , pp. 629-642
    • Kapsa, R.1    Quigley, A.2    Lynch, G.S.3
  • 23
    • 0036268304 scopus 로고    scopus 로고
    • Targeted gene correction in the mdx mouse using short DNA fragments: Towards application with bone marrow-derived cells for autologous remodelling of dystrophic muscle
    • Kapsa RM, Quigley AF, Vadolas J, Steeper K, Ioannou PA, Byrne E, Kornberg AJ: Targeted gene correction in the mdx mouse using short DNA fragments: towards application with bone marrow-derived cells for autologous remodelling of dystrophic muscle. Gene Ther 9:695-699 (2002).
    • (2002) Gene Ther , vol.9 , pp. 695-699
    • Kapsa, R.M.1    Quigley, A.F.2    Vadolas, J.3    Steeper, K.4    Ioannou, P.A.5    Byrne, E.6    Kornberg, A.J.7
  • 24
    • 0032921514 scopus 로고    scopus 로고
    • Targeted gene repair
    • Kmiec EB: Targeted gene repair. Gene Ther 6:1-3 (1999).
    • (1999) Gene Ther , vol.6 , pp. 1-3
    • Kmiec, E.B.1
  • 25
    • 0141612016 scopus 로고    scopus 로고
    • Targeted gene repair - In the arena
    • Kmiec EB: Targeted gene repair - in the arena. J Clin Invest 112:632-636 (2003).
    • (2003) J Clin Invest , vol.112 , pp. 632-636
    • Kmiec, E.B.1
  • 26
    • 0031953132 scopus 로고    scopus 로고
    • In vivo site-directed mutagenesis of the factor IX gene by chimeric RNA/DNA oligonucleotides
    • Kren BT, Bandyopadhyay P, Steer CJ: In vivo site-directed mutagenesis of the factor IX gene by chimeric RNA/DNA oligonucleotides. Nat Med 4:285-290 (1998).
    • (1998) Nat Med , vol.4 , pp. 285-290
    • Kren, B.T.1    Bandyopadhyay, P.2    Steer, C.J.3
  • 27
    • 0033621041 scopus 로고    scopus 로고
    • Correction of the UDP-glucuronosyltransferase gene defect in the gunn rat model of Crigler-Najjar syndrome type I with a chimeric oligonucleotide
    • Kren BT, Parashar B, Bandyopadhyay P, Chowdhury NR, Chowdhury JR, Steer CJ: Correction of the UDP-glucuronosyltransferase gene defect in the gunn rat model of Crigler-Najjar syndrome type I with a chimeric oligonucleotide. Proc Natl Acad Sci USA 96:10349-10354 (1999).
    • (1999) Proc Natl Acad Sci USA , vol.96 , pp. 10349-10354
    • Kren, B.T.1    Parashar, B.2    Bandyopadhyay, P.3    Chowdhury, N.R.4    Chowdhury, J.R.5    Steer, C.J.6
  • 28
    • 0034329384 scopus 로고    scopus 로고
    • Targeted single-base correction by RNA-DNA oligonucleotides
    • Igoucheva O, Yoon K: Targeted single-base correction by RNA-DNA oligonucleotides. Hum Gene Ther 11:2307-2312 (2000).
    • (2000) Hum Gene Ther , vol.11 , pp. 2307-2312
    • Igoucheva, O.1    Yoon, K.2
  • 29
    • 0034255524 scopus 로고    scopus 로고
    • High-frequency intrachromosomal gene conversion induced by triplex-forming oligonucleotides microinjected into mouse cells
    • Luo Z, Macris MA, Faruqi AF, Glazer PM: High-frequency intrachromosomal gene conversion induced by triplex-forming oligonucleotides microinjected into mouse cells. Proc Natl Acad Sci USA 97:9003-9008 (2000).
    • (2000) Proc Natl Acad Sci USA , vol.97 , pp. 9003-9008
    • Luo, Z.1    Macris, M.A.2    Faruqi, A.F.3    Glazer, P.M.4
  • 31
    • 0030803659 scopus 로고    scopus 로고
    • Strand-specific mismatch repair in mammalian cells
    • Modrich P: Strand-specific mismatch repair in mammalian cells. J Biol Chem 272:24727-24730 (1997).
    • (1997) J Biol Chem , vol.272 , pp. 24727-24730
    • Modrich, P.1
  • 32
    • 0035958048 scopus 로고    scopus 로고
    • Foreign DNA integration. Genome-wide perturbations of methylation and transcription in the recipient genomes
    • Muller K, Heller H, Doerfler W: Foreign DNA integration. Genome-wide perturbations of methylation and transcription in the recipient genomes. J Biol Chem 276:14271-14278 (2001).
    • (2001) J Biol Chem , vol.276 , pp. 14271-14278
    • Muller, K.1    Heller, H.2    Doerfler, W.3
  • 33
    • 0042878534 scopus 로고    scopus 로고
    • A comparison of gene repair strategies in cell culture using a lacZ reporter system
    • Nickerson HD, Colledge WH: A comparison of gene repair strategies in cell culture using a lacZ reporter system. Gene Ther 10: 1584-1591 (2003).
    • (2003) Gene Ther , vol.10 , pp. 1584-1591
    • Nickerson, H.D.1    Colledge, W.H.2
  • 34
    • 0032014650 scopus 로고    scopus 로고
    • Mutagenesis mediated by triple helix-forming oligonucleotides conjugated to psoralen: Effects of linker arm length and sequence context
    • Raha M, Lacroix L, Glazer PM: Mutagenesis mediated by triple helix-forming oligonucleotides conjugated to psoralen: effects of linker arm length and sequence context. Photochem Photobiol 67:289-294 (1998).
    • (1998) Photochem Photobiol , vol.67 , pp. 289-294
    • Raha, M.1    Lacroix, L.2    Glazer, P.M.3
  • 35
    • 0034624974 scopus 로고    scopus 로고
    • Rescue of dystrophin expression in mdx mouse muscle by RNA/DNA oligonucleotides
    • Rando TA, Disatnik M-H, Zhou LZ-H: Rescue of dystrophin expression in mdx mouse muscle by RNA/DNA oligonucleotides. Proc Natl Acad Sci USA 97:5363-5368 (2000).
    • (2000) Proc Natl Acad Sci USA , vol.97 , pp. 5363-5368
    • Rando, T.A.1    Disatnik, M.-H.2    Zhou, L.Z.-H.3
  • 36
    • 0345435970 scopus 로고    scopus 로고
    • Insertion of foreign DNA into an established mammalian genome can alter the methylation of cellular DNA sequences
    • Remus R, Kammer C, Heller H, Schmitz B, Schell G, Doerfler W: Insertion of foreign DNA into an established mammalian genome can alter the methylation of cellular DNA sequences. J Virol 73:1010-1022 (1999).
    • (1999) J Virol , vol.73 , pp. 1010-1022
    • Remus, R.1    Kammer, C.2    Heller, H.3    Schmitz, B.4    Schell, G.5    Doerfler, W.6
  • 37
    • 0036276532 scopus 로고    scopus 로고
    • Visible transient expression of EGFP requires intranuclear injection of large copy numbers
    • Schindelhauer D, Laner A: Visible transient expression of EGFP requires intranuclear injection of large copy numbers. Gene Ther 9:727-730 (2002).
    • (2002) Gene Ther , vol.9 , pp. 727-730
    • Schindelhauer, D.1    Laner, A.2
  • 38
    • 0042388177 scopus 로고    scopus 로고
    • Targeted genetic repair: An emerging approach to genetic therapy
    • Sullenger BA: Targeted genetic repair: an emerging approach to genetic therapy. J Clin Invest 112:310-311 (2003).
    • (2003) J Clin Invest , vol.112 , pp. 310-311
    • Sullenger, B.A.1
  • 39
    • 0031047639 scopus 로고    scopus 로고
    • Recombinant DNA technique and sickle cell anemia research
    • Thomas KR, Capecchi MR: Recombinant DNA technique and sickle cell anemia research. Science 275:1404-1405 (1997).
    • (1997) Science , vol.275 , pp. 1404-1405
    • Thomas, K.R.1    Capecchi, M.R.2
  • 40
    • 0142212286 scopus 로고    scopus 로고
    • Promotion of triplex formation by morpholino modification: Thermodynamic and kinetic studies
    • Torigoe H, Kawahashi K, Tamura Y: Promotion of triplex formation by morpholino modification: thermodynamic and kinetic studies. Nucleic Acids Res 3:157-158 (2003).
    • (2003) Nucleic Acids Res , vol.3 , pp. 157-158
    • Torigoe, H.1    Kawahashi, K.2    Tamura, Y.3
  • 42
    • 0033557144 scopus 로고    scopus 로고
    • Chromosomal mutations induced by triplex-forming oligonucleotides in mammalian cells
    • Vasquez KM, Wang G, Havre PA, Glazer PM: Chromosomal mutations induced by triplex-forming oligonucleotides in mammalian cells. Nucleic Acids Res 27:1176-1181 (1999)
    • (1999) Nucleic Acids Res , vol.27 , pp. 1176-1181
    • Vasquez, K.M.1    Wang, G.2    Havre, P.A.3    Glazer, P.M.4
  • 43
    • 0033766239 scopus 로고    scopus 로고
    • Specific mutations induced by triplex-forming oligonucleotides in mice
    • Vasquez KM, Narayanan L, Glazer PM: Specific mutations induced by triplex-forming oligonucleotides in mice. Science 290:530-533 (2000).
    • (2000) Science , vol.290 , pp. 530-533
    • Vasquez, K.M.1    Narayanan, L.2    Glazer, P.M.3
  • 45
    • 0035914386 scopus 로고    scopus 로고
    • Chromosome targeting at short polypurine sites by cationic triplex-forming oligonucleotides
    • Vasquez KM, Dagle JM, Weeks DL, Glazer PM: Chromosome targeting at short polypurine sites by cationic triplex-forming oligonucleotides. J Biol Chem 276:38536-38541 (2001b).
    • (2001) J Biol Chem , vol.276 , pp. 38536-38541
    • Vasquez, K.M.1    Dagle, J.M.2    Weeks, D.L.3    Glazer, P.M.4
  • 46
    • 0242367234 scopus 로고    scopus 로고
    • Gene therapy-new challenges ahead
    • Williams DA, Baum C: Gene therapy-new challenges ahead. Science 302:400-401 (2003).
    • (2003) Science , vol.302 , pp. 400-401
    • Williams, D.A.1    Baum, C.2
  • 47
    • 0034754799 scopus 로고    scopus 로고
    • Prospects of chimeric RNA-DNA oligonucleotides in gene therapy
    • Wu XS, Liu DP, Liang CC: Prospects of chimeric RNA-DNA oligonucleotides in gene therapy. J Biomed Sci 8:439-445 (2001).
    • (2001) J Biomed Sci , vol.8 , pp. 439-445
    • Wu, X.S.1    Liu, D.P.2    Liang, C.C.3
  • 48
    • 0031935394 scopus 로고    scopus 로고
    • Therapeutic gene targeting
    • Yanez J, Porter AC: Therapeutic gene targeting. Gene Ther 5:149-159 (1998).
    • (1998) Gene Ther , vol.5 , pp. 149-159
    • Yanez, J.1    Porter, A.C.2
  • 50
    • 0035200623 scopus 로고    scopus 로고
    • In vitro differentiation of transplantable neural precursors from human embryonic stem cells
    • Zhang SC, Wernig M, Duncan ID, Brustle O, Thomson JA: In vitro differentiation of transplantable neural precursors from human embryonic stem cells. Nat Biotechnol 19:1129-1133 (2001).
    • (2001) Nat Biotechnol , vol.19 , pp. 1129-1133
    • Zhang, S.C.1    Wernig, M.2    Duncan, I.D.3    Brustle, O.4    Thomson, J.A.5
  • 51
    • 0037336820 scopus 로고    scopus 로고
    • Homologous recombination in human embryonic stem cells
    • Zwaka TP, Thomson J: Homologous recombination in human embryonic stem cells. Nat Biotechnol 21:319-321 (2003).
    • (2003) Nat Biotechnol , vol.21 , pp. 319-321
    • Zwaka, T.P.1    Thomson, J.2


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.