-
1
-
-
0002942277
-
Hereditary jaundice and disorders of bilirubin metabolism
-
Scriver CR, Beaudet AL, Sly WS, Valle D (eds): New York, McGraw-Hill
-
Chowdhury JR, Wolkoff AW, Chowdhury NR, Arias IM: Hereditary jaundice and disorders of bilirubin metabolism; in Scriver CR, Beaudet AL, Sly WS, Valle D (eds): The Metabolic and Molecular Bases of Inherited Disease. New York, McGraw-Hill, 2001, pp 3063-3101.
-
(2001)
The Metabolic and Molecular Bases of Inherited Disease
, pp. 3063-3101
-
-
Chowdhury, J.R.1
Wolkoff, A.W.2
Chowdhury, N.R.3
Arias, I.M.4
-
2
-
-
0001606872
-
Hypertyrosinemia
-
Scriver CR, Beaudet AL, Sly WS, Valle D (eds): New York, McGraw-Hill
-
Mitchell GA, Grompe M, Lambert M, Tanguay RM: Hypertyrosinemia; in Scriver CR, Beaudet AL, Sly WS, Valle D (eds): The Metabolic and Molecular Bases of Inherited Disease. New York, McGraw-Hill, 2001, pp 1777-1805.
-
(2001)
The Metabolic and Molecular Bases of Inherited Disease
, pp. 1777-1805
-
-
Mitchell, G.A.1
Grompe, M.2
Lambert, M.3
Tanguay, R.M.4
-
3
-
-
0003089017
-
The Hyperornithinemias
-
Scriver CR, Beaudet AL, Sly WS, Valle D (eds): New York, McGraw-Hill
-
Valle D, Simell O: The Hyperornithinemias; in Scriver CR, Beaudet AL, Sly WS, Valle D (eds): The Metabolic and Molecular Bases of Inherited Disease. New York, McGraw-Hill, 2001, pp 1857-1895.
-
(2001)
The Metabolic and Molecular Bases of Inherited Disease
, pp. 1857-1895
-
-
Valle, D.1
Simell, O.2
-
4
-
-
0032821708
-
Prospects for in utero human gene therapy
-
Zanjani ED, Anderson WF: Prospects for in utero human gene therapy. Science 1999;285:2084-2088.
-
(1999)
Science
, vol.285
, pp. 2084-2088
-
-
Zanjani, E.D.1
Anderson, W.F.2
-
5
-
-
0142191275
-
Fetal gene therapy
-
David AL, Themis M, Cook T, Coutelle C, Rodeck CH: Fetal gene therapy. Ultrasound Rev Obstet Gynecol 2001;1:14-27.
-
(2001)
Ultrasound Rev Obstet Gynecol
, vol.1
, pp. 14-27
-
-
David, A.L.1
Themis, M.2
Cook, T.3
Coutelle, C.4
Rodeck, C.H.5
-
6
-
-
0033121139
-
Prenatal gene therapy: Can the technical hurdles be overcome?
-
Senut MC, Gage FH: Prenatal gene therapy: can the technical hurdles be overcome? Mol Med Today 1999;5:152-156.
-
(1999)
Mol Med Today
, vol.5
, pp. 152-156
-
-
Senut, M.C.1
Gage, F.H.2
-
7
-
-
0037448352
-
A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency
-
Hacein-Bey-Abina S, von Kalle C, Schmidt M, Le Deist F, Wulffraat N, McIntyre E, Radford I, Villeval JL, Fraser CC, Cavazzana-Calvo M, Fischer A: A serious adverse event after successful gene therapy for X-linked severe combined immunodeficiency. N Engl J Med 2003;348:255-256.
-
(2003)
N Engl J Med
, vol.348
, pp. 255-256
-
-
Hacein-Bey-Abina, S.1
Von Kalle, C.2
Schmidt, M.3
Le Deist, F.4
Wulffraat, N.5
McIntyre, E.6
Radford, I.7
Villeval, J.L.8
Fraser, C.C.9
Cavazzana-Calvo, M.10
Fischer, A.11
-
8
-
-
0034904598
-
Silencing of gene expression: Implications for design of retrovirus vectors
-
Pannell D, Ellis J: Silencing of gene expression: implications for design of retrovirus vectors. Rev Med Virol 2001;11:205-217.
-
(2001)
Rev Med Virol
, vol.11
, pp. 205-217
-
-
Pannell, D.1
Ellis, J.2
-
9
-
-
10744232558
-
The hopes and fears of in utero gene therapy for genetic disease - A review
-
Coutelle C, Themis M, Waddington S, Gregory L, Nivsarkar M, Buckley S, Cook T, Rodeck C, Peebles D, David A: The hopes and fears of in utero gene therapy for genetic disease - a review. Placenta 2003;24:S114-S121.
-
(2003)
Placenta
, vol.24
-
-
Coutelle, C.1
Themis, M.2
Waddington, S.3
Gregory, L.4
Nivsarkar, M.5
Buckley, S.6
Cook, T.7
Rodeck, C.8
Peebles, D.9
David, A.10
-
10
-
-
0031736286
-
Ultrasound-guided gene transfer to hepatocytes in utero
-
Wang G, Williamson R, Mueller G, Thomas P, Davidson BL, McCray PB Jr: Ultrasound-guided gene transfer to hepatocytes in utero. Fetal Diagn Ther 1998;13:197-205.
-
(1998)
Fetal Diagn Ther
, vol.13
, pp. 197-205
-
-
Wang, G.1
Williamson, R.2
Mueller, G.3
Thomas, P.4
Davidson, B.L.5
McCray Jr., P.B.6
-
11
-
-
0032694121
-
Ultrasonographically guided direct gene transfer in utero: Successful induction of beta-galactosidase in a rabbit model
-
Baumgartner TL, Baumgartner BJ, Hudon L, Moise KJ Jr: Ultrasonographically guided direct gene transfer in utero: successful induction of beta-galactosidase in a rabbit model. Am J Obstet Gynecol 1999;181:848-852.
-
(1999)
Am J Obstet Gynecol
, vol.181
, pp. 848-852
-
-
Baumgartner, T.L.1
Baumgartner, B.J.2
Hudon, L.3
Moise Jr., K.J.4
-
12
-
-
0033428380
-
Prenatal orogastric gene delivery results in transduction of the small bowel in the fetal rabbit
-
Wu Y, Liu J, Woo S, Finegold MJ, Brandt ML: Prenatal orogastric gene delivery results in transduction of the small bowel in the fetal rabbit. Fetal Diagn Ther 1999;14:323-327.
-
(1999)
Fetal Diagn Ther
, vol.14
, pp. 323-327
-
-
Wu, Y.1
Liu, J.2
Woo, S.3
Finegold, M.J.4
Brandt, M.L.5
-
13
-
-
0034893257
-
In utero AAV-mediated gene transfer to rabbit pulmonary epithelium
-
Boyle MP, Enke RA, Adams RJ, Guggino WB, Zeitlin PL: In utero AAV-mediated gene transfer to rabbit pulmonary epithelium. Mol Ther 2001;4:115-121.
-
(2001)
Mol Ther
, vol.4
, pp. 115-121
-
-
Boyle, M.P.1
Enke, R.A.2
Adams, R.J.3
Guggino, W.B.4
Zeitlin, P.L.5
-
14
-
-
0027228422
-
Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: Concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells
-
USA
-
Burns JC, Friedmann T, Driever W, Burrascano M, Yee JK: Vesicular stomatitis virus G glycoprotein pseudotyped retroviral vectors: concentration to very high titer and efficient gene transfer into mammalian and nonmammalian cells. Proc Natl Acad Sci USA 1993;90:8033-8037.
-
(1993)
Proc Natl Acad Sci
, vol.90
, pp. 8033-8037
-
-
Burns, J.C.1
Friedmann, T.2
Driever, W.3
Burrascano, M.4
Yee, J.K.5
-
15
-
-
0032113403
-
Construction and characterization of bicistronic retroviral vectors encoding the multidrug transporter and beta-galactosidase or green fluorescent protein
-
Aran JM, Gottesman MM, Pastan I: Construction and characterization of bicistronic retroviral vectors encoding the multidrug transporter and beta-galactosidase or green fluorescent protein. Cancer Gene Ther 1998;5:195-206.
-
(1998)
Cancer Gene Ther
, vol.5
, pp. 195-206
-
-
Aran, J.M.1
Gottesman, M.M.2
Pastan, I.3
-
16
-
-
0030822347
-
Successful reconstitution of human hematopoiesis in the SCID-hu mouse by genetically modified, highly enriched progenitors isolated from fetal liver
-
Humeau L, Chabannon C, Firpo MT, Mannoni P, Bagnis C, Roncarolo MG, Namikawa R: Successful reconstitution of human hematopoiesis in the SCID-hu mouse by genetically modified, highly enriched progenitors isolated from fetal liver. Blood 1997;90:3496-3506.
-
(1997)
Blood
, vol.90
, pp. 3496-3506
-
-
Humeau, L.1
Chabannon, C.2
Firpo, M.T.3
Mannoni, P.4
Bagnis, C.5
Roncarolo, M.G.6
Namikawa, R.7
-
17
-
-
0034030812
-
Adenovirus-mediated in utero gene transfer in mice and guinea pigs: Tissue distribution of recombinant adenovirus determined by quantitative TaqMan-polymerase chain reaction assay
-
Senoo M, Matsubara Y, Fujii K, Nagasaki Y, Hiratsuka M, Kure S, Uehara S, Okamura K, Yajima A, Narisawa K: Adenovirus-mediated in utero gene transfer in mice and guinea pigs: tissue distribution of recombinant adenovirus determined by quantitative TaqMan-polymerase chain reaction assay. Mol Genet Metab 2000;69:269-276.
-
(2000)
Mol Genet Metab
, vol.69
, pp. 269-276
-
-
Senoo, M.1
Matsubara, Y.2
Fujii, K.3
Nagasaki, Y.4
Hiratsuka, M.5
Kure, S.6
Uehara, S.7
Okamura, K.8
Yajima, A.9
Narisawa, K.10
-
18
-
-
0034986211
-
Angiographically guided utero-placental gene transfer in rabbits with adenoviruses, plasmid/liposomes and plasmid/polyethyleneimine complexes
-
Heikkila A, Hiltunen MO, Turunen MP, Keski-Nisula L, Turunen AM, Rasanen H, Rissanen TT, Kosma M, Manninen H, Heinonen S, Yla-Herttuala S: Angiographically guided utero-placental gene transfer in rabbits with adenoviruses, plasmid/liposomes and plasmid/polyethyleneimine complexes. Gene Ther 2001;8:784-788.
-
(2001)
Gene Ther
, vol.8
, pp. 784-788
-
-
Heikkila, A.1
Hiltunen, M.O.2
Turunen, M.P.3
Keski-Nisula, L.4
Turunen, A.M.5
Rasanen, H.6
Rissanen, T.T.7
Kosma, M.8
Manninen, H.9
Heinonen, S.10
Yla-Herttuala, S.11
-
19
-
-
0036412405
-
In utero injection of alpha-L-iduronidase-carrying retrovirus in canine mucopolysaccharidosis type I: Infection of multiple tissues and neonatal gene expression
-
Meertens L, Zhao Y, Rosic-Kablar S, Li L, Chan K, Dobson H, Gartley C, Lutzko C, Hopwood J, Kohn D, Kruth S, Hough MR, Dube ID: In utero injection of alpha-L-iduronidase-carrying retrovirus in canine mucopolysaccharidosis type I: infection of multiple tissues and neonatal gene expression. Hum Gene Ther 2002;13:1809-1820.
-
(2002)
Hum Gene Ther
, vol.13
, pp. 1809-1820
-
-
Meertens, L.1
Zhao, Y.2
Rosic-Kablar, S.3
Li, L.4
Chan, K.5
Dobson, H.6
Gartley, C.7
Lutzko, C.8
Hopwood, J.9
Kohn, D.10
Kruth, S.11
Hough, M.R.12
Dube, I.D.13
-
20
-
-
0034985713
-
Rhesus monkey model for fetal gene transfer: Studies with retroviral-based vector systems
-
Tarantal AF, O'Rourke JP, Case SS, Newbound GC, Li J, Lee CI, Baskin CR, Kohn DB, Bunnell BA: Rhesus monkey model for fetal gene transfer: studies with retroviral-based vector systems. Mol Ther 2001;3:128-138.
-
(2001)
Mol Ther
, vol.3
, pp. 128-138
-
-
Tarantal, A.F.1
O'Rourke, J.P.2
Case, S.S.3
Newbound, G.C.4
Li, J.5
Lee, C.I.6
Baskin, C.R.7
Kohn, D.B.8
Bunnell, B.A.9
-
21
-
-
0025679138
-
Operative techniques in the fetal rabbit
-
Nelson JM, Krummel TM, Haynes JH, Flood LC, Sauer L, Flake AW, Harrison MR: Operative techniques in the fetal rabbit. J Invest Surg 1990;3:393-398.
-
(1990)
J Invest Surg
, vol.3
, pp. 393-398
-
-
Nelson, J.M.1
Krummel, T.M.2
Haynes, J.H.3
Flood, L.C.4
Sauer, L.5
Flake, A.W.6
Harrison, M.R.7
-
22
-
-
0028276593
-
Transamniotic fetal feeding: Enhancement of growth in a rabbit model of intrauterine growth retardation
-
Buchmiller TL, Kim CS, Chopourian HL, Fonkalsrud EW: Transamniotic fetal feeding: enhancement of growth in a rabbit model of intrauterine growth retardation. Surgery 1994;116:36-41.
-
(1994)
Surgery
, vol.116
, pp. 36-41
-
-
Buchmiller, T.L.1
Kim, C.S.2
Chopourian, H.L.3
Fonkalsrud, E.W.4
-
23
-
-
0033002990
-
The midgestational rabbit as a model for the creation of membrane defects after needle fetoscopy
-
Gratacos E, Yamamoto H, Papadopulos NA, Adriaenssens T, Phlips T, Lerut TE, Deprest JA: The midgestational rabbit as a model for the creation of membrane defects after needle fetoscopy. Am J Obstet Gynecol 1999;180:1263-1267.
-
(1999)
Am J Obstet Gynecol
, vol.180
, pp. 1263-1267
-
-
Gratacos, E.1
Yamamoto, H.2
Papadopulos, N.A.3
Adriaenssens, T.4
Phlips, T.5
Lerut, T.E.6
Deprest, J.A.7
-
24
-
-
0022486356
-
Human fetal lung development and related animal models
-
Pringle KC: Human fetal lung development and related animal models. Clin Obstet Gynecol 1986;29:502-513.
-
(1986)
Clin Obstet Gynecol
, vol.29
, pp. 502-513
-
-
Pringle, K.C.1
-
25
-
-
0142227889
-
Developmental stages in the rabbit embryo: Guidelines to choose an appropriate experimental model
-
Beaudoin S, Barbet P, Bargy F: Developmental stages in the rabbit embryo: guidelines to choose an appropriate experimental model. Fetal Diagn Ther 2003;18:422-427.
-
(2003)
Fetal Diagn Ther
, vol.18
, pp. 422-427
-
-
Beaudoin, S.1
Barbet, P.2
Bargy, F.3
-
26
-
-
0035383766
-
Induction of stable prenatal tolerance to beta-galactosidase by in utero gene transfer into preimmune sheep fetuses
-
Tran ND, Porada CD, Almeida-Porada G, Glimp HA, Anderson WF, Zanjani ED: Induction of stable prenatal tolerance to beta-galactosidase by in utero gene transfer into preimmune sheep fetuses. Blood 2001;97:3417-3423.
-
(2001)
Blood
, vol.97
, pp. 3417-3423
-
-
Tran, N.D.1
Porada, C.D.2
Almeida-Porada, G.3
Glimp, H.A.4
Anderson, W.F.5
Zanjani, E.D.6
-
27
-
-
0029793791
-
Effect of amniotic fluid on cationic lipid mediated transfection and retroviral infection
-
Douar AM, Themis M, Sandig V, Friedmann T, Coutelle C: Effect of amniotic fluid on cationic lipid mediated transfection and retroviral infection. Gene Ther 1996;3:789-796.
-
(1996)
Gene Ther
, vol.3
, pp. 789-796
-
-
Douar, A.M.1
Themis, M.2
Sandig, V.3
Friedmann, T.4
Coutelle, C.5
-
28
-
-
0029115287
-
Retrovirus-mediated gene transfer in lungs of living fetal sheep
-
Pitt BR, Schwarz MA, Pilewski JM, Nakayama D, Mueller GM, Robbins PD, Watkins SA, Albertine KH, Bland RD: Retrovirus-mediated gene transfer in lungs of living fetal sheep. Gene Ther 1995;2:344-350.
-
(1995)
Gene Ther
, vol.2
, pp. 344-350
-
-
Pitt, B.R.1
Schwarz, M.A.2
Pilewski, J.M.3
Nakayama, D.4
Mueller, G.M.5
Robbins, P.D.6
Watkins, S.A.7
Albertine, K.H.8
Bland, R.D.9
-
29
-
-
0030867444
-
Foetal gene delivery in mice by intra-amniotic administration of retroviral producer cells and adenovirus
-
Douar AM, Adebakin S, Themis M, Pavirani A, Cook T, Coutelle C: Foetal gene delivery in mice by intra-amniotic administration of retroviral producer cells and adenovirus. Gene Ther 1997;4:883-890.
-
(1997)
Gene Ther
, vol.4
, pp. 883-890
-
-
Douar, A.M.1
Adebakin, S.2
Themis, M.3
Pavirani, A.4
Cook, T.5
Coutelle, C.6
-
30
-
-
17644448979
-
Intrauterine gene transfer: Gestational stage-specific gene delivery in mice
-
Turkay A, Saunders T, Kurachi K: Intrauterine gene transfer: gestational stage-specific gene delivery in mice. Gene Ther 1999;6:1685-1694.
-
(1999)
Gene Ther
, vol.6
, pp. 1685-1694
-
-
Turkay, A.1
Saunders, T.2
Kurachi, K.3
-
31
-
-
0032551689
-
In utero gene therapy: Transfer and long-term expression of the bacterial neo(r) gene in sheep after direct injection of retroviral vectors into preimmune fetuses
-
Porada CD, Tran N, Eglitis M, Moen RC, Troutman L, Flake AW, Zhao Y, Anderson WF, Zanjani ED: In utero gene therapy: transfer and long-term expression of the bacterial neo(r) gene in sheep after direct injection of retroviral vectors into preimmune fetuses. Hum Gene Ther 1998;9:1571-1585.
-
(1998)
Hum Gene Ther
, vol.9
, pp. 1571-1585
-
-
Porada, C.D.1
Tran, N.2
Eglitis, M.3
Moen, R.C.4
Troutman, L.5
Flake, A.W.6
Zhao, Y.7
Anderson, W.F.8
Zanjani, E.D.9
-
32
-
-
0033959097
-
In utero transfer and expression of exogenous genes in sheep
-
Tran ND, Porada CD, Zhao Y, Almeida-Porada G, Anderson WF, Zanjani ED: In utero transfer and expression of exogenous genes in sheep. Exp Hematol 2000;28:17-30.
-
(2000)
Exp Hematol
, vol.28
, pp. 17-30
-
-
Tran, N.D.1
Porada, C.D.2
Zhao, Y.3
Almeida-Porada, G.4
Anderson, W.F.5
Zanjani, E.D.6
-
33
-
-
13144275215
-
Development of an epithelium-specific expression cassette with human DNA regulatory elements for transgene expression in lung airways
-
USA
-
Chow YH, O'Brodovich H, Plumb J, Wen Y, Sohn KJ, Lu Z, Zhang F, Lukacs GL, Tanswell AK, Hui CC, Buchwald M, Hu J: Development of an epithelium-specific expression cassette with human DNA regulatory elements for transgene expression in lung airways. Proc Natl Acad Sci USA 1997;94:14695-14700.
-
(1997)
Proc Natl Acad Sci
, vol.94
, pp. 14695-14700
-
-
Chow, Y.H.1
O'Brodovich, H.2
Plumb, J.3
Wen, Y.4
Sohn, K.J.5
Lu, Z.6
Zhang, F.7
Lukacs, G.L.8
Tanswell, A.K.9
Hui, C.C.10
Buchwald, M.11
Hu, J.12
-
34
-
-
0038792207
-
Performance- And safety-enhanced lentiviral vectors containing the human interferon-beta scaffold attachment region and the chicken beta-globin insulator
-
Ramezani A, Hawley TS, Hawley RG: Performance- and safety-enhanced lentiviral vectors containing the human interferon-beta scaffold attachment region and the chicken beta-globin insulator. Blood 2003;101:4717-4724.
-
(2003)
Blood
, vol.101
, pp. 4717-4724
-
-
Ramezani, A.1
Hawley, T.S.2
Hawley, R.G.3
-
35
-
-
0028255868
-
Drug-selected coexpression of human glucocerebrosidase and P-glycoprotein using a bicistronic vector
-
USA
-
Aran JM, Gottesman MM, Pastan I: Drug-selected coexpression of human glucocerebrosidase and P-glycoprotein using a bicistronic vector. Proc Natl Acad Sci USA 1994;91:3176-3180.
-
(1994)
Proc Natl Acad Sci
, vol.91
, pp. 3176-3180
-
-
Aran, J.M.1
Gottesman, M.M.2
Pastan, I.3
-
36
-
-
0029846013
-
Complete restoration of glucocerebrosidase deficiency in Gaucher fibroblasts using a bicistronic MDR retrovirus and a new selection strategy
-
Aran JM, Licht T, Gottesman MM, Pastan I: Complete restoration of glucocerebrosidase deficiency in Gaucher fibroblasts using a bicistronic MDR retrovirus and a new selection strategy. Hum Gene Ther 1996;7:2165-2175.
-
(1996)
Hum Gene Ther
, vol.7
, pp. 2165-2175
-
-
Aran, J.M.1
Licht, T.2
Gottesman, M.M.3
Pastan, I.4
-
37
-
-
0035668699
-
Lentiviral vector gene transfer into fetal rhesus monkeys (Macaca mulatta): Lung-targeting approaches
-
Tarantal AF, Lee CI, Ekert JE, McDonald R, Kohn DB, Plopper CG, Case SS, Bunnell BA: Lentiviral vector gene transfer into fetal rhesus monkeys (Macaca mulatta): lung-targeting approaches. Mol Ther 2001;4:614-621.
-
(2001)
Mol Ther
, vol.4
, pp. 614-621
-
-
Tarantal, A.F.1
Lee, C.I.2
Ekert, J.E.3
McDonald, R.4
Kohn, D.B.5
Plopper, C.G.6
Case, S.S.7
Bunnell, B.A.8
-
38
-
-
0346035738
-
Efficient transduction of liver and muscle after in utero injection of lentiviral vectors with different pseudotypes
-
MacKenzie TC, Kobinger GP, Kootstra NA, Radu A, Sena-Esteves M, Bouchard S, Wilson JM, Verma IM, Flake AW: Efficient transduction of liver and muscle after in utero injection of lentiviral vectors with different pseudotypes. Mol Ther 2002;6:349-358.
-
(2002)
Mol Ther
, vol.6
, pp. 349-358
-
-
MacKenzie, T.C.1
Kobinger, G.P.2
Kootstra, N.A.3
Radu, A.4
Sena-Esteves, M.5
Bouchard, S.6
Wilson, J.M.7
Verma, I.M.8
Flake, A.W.9
-
39
-
-
0142181993
-
Long-term correction of bilirubin UDP-glucuronyltransferase deficiency in rats by in utero lentiviral gene transfer
-
Seppen J, van der Rijt R, Looije N, van Til NP, Lamers WH, Oude Elferink RP: Long-term correction of bilirubin UDP-glucuronyltransferase deficiency in rats by in utero lentiviral gene transfer. Mol Ther 2003;8:593-599.
-
(2003)
Mol Ther
, vol.8
, pp. 593-599
-
-
Seppen, J.1
Van Der Rijt, R.2
Looije, N.3
Van Til, N.P.4
Lamers, W.H.5
Oude Elferink, R.P.6
-
40
-
-
0042674017
-
Long-term transgene expression by administration of a lentivirus-based vector to the fetal circulation of immuno-competent mice
-
Waddington SN, Mitrophanous KA, Ellard FM, Buckley SM, Nivsarkar M, Lawrence L, Cook HT, Al-Allaf F, Bigger B, Kingsman SM, Coutelle C, Themis M: Long-term transgene expression by administration of a lentivirus-based vector to the fetal circulation of immuno-competent mice. Gene Ther 2003;10:1234-1240.
-
(2003)
Gene Ther
, vol.10
, pp. 1234-1240
-
-
Waddington, S.N.1
Mitrophanous, K.A.2
Ellard, F.M.3
Buckley, S.M.4
Nivsarkar, M.5
Lawrence, L.6
Cook, H.T.7
Al-Allaf, F.8
Bigger, B.9
Kingsman, S.M.10
Coutelle, C.11
Themis, M.12
-
41
-
-
4243132862
-
Highly efficient EIAV-mediated in utero gene transfer and expression in the major muscle groups affected by Duchenne muscular dystrophy
-
DOI: 10.1038/ sj.gt.3302268
-
Gregory LG, Waddington SN, Holder MV, Mitrophanous KA, Buckley SM, Mosley KL, Bigger BW, Ellard FM, Walmsley LE, Lawrence L, Al-Allaf F, Kingsman S, Coutelle C, Themis M: Highly efficient EIAV-mediated in utero gene transfer and expression in the major muscle groups affected by Duchenne muscular dystrophy. Gene Ther 2004; DOI: 10.1038/ sj.gt.3302268.
-
(2004)
Gene Ther
-
-
Gregory, L.G.1
Waddington, S.N.2
Holder, M.V.3
Mitrophanous, K.A.4
Buckley, S.M.5
Mosley, K.L.6
Bigger, B.W.7
Ellard, F.M.8
Walmsley, L.E.9
Lawrence, L.10
Al-Allaf, F.11
Kingsman, S.12
Coutelle, C.13
Themis, M.14
-
42
-
-
0001860430
-
Developmental anatomy and normal structure
-
MacSween RMN, Burt AD, Portmann BC, Ishak KG, Scheuer PJ, Anthony PP (eds): New York, Churchill Livingstone
-
MacSween RNM, Desmet VJ, Roskams T, Scothorne RJ: Developmental anatomy and normal structure; in MacSween RMN, Burt AD, Portmann BC, Ishak KG, Scheuer PJ, Anthony PP (eds): Pathology of the Liver. New York, Churchill Livingstone, 2002, pp 1-66.
-
(2002)
Pathology of the Liver
, pp. 1-66
-
-
MacSween, R.N.M.1
Desmet, V.J.2
Roskams, T.3
Scothorne, R.J.4
-
43
-
-
0034880427
-
High-efficiency retroviral transduction of fetal liver CD38-CD34++ cells: Implications for in utero and ex utero gene therapy
-
Ohkubo T, Bárcena A, Smith CA, Harrison MR, Muench MO: High-efficiency retroviral transduction of fetal liver CD38-CD34++ cells: implications for in utero and ex utero gene therapy. Fetal Diagn Ther 2001;16:299-307.
-
(2001)
Fetal Diagn Ther
, vol.16
, pp. 299-307
-
-
Ohkubo, T.1
Bárcena, A.2
Smith, C.A.3
Harrison, M.R.4
Muench, M.O.5
-
44
-
-
0041854301
-
The effect of age on hepatic gene transfer with self-inactivating lentiviral vectors in vivo
-
Park F, Ohashi K, Kay MA: The effect of age on hepatic gene transfer with self-inactivating lentiviral vectors in vivo. Mol Ther 2003;8:314-323.
-
(2003)
Mol Ther
, vol.8
, pp. 314-323
-
-
Park, F.1
Ohashi, K.2
Kay, M.A.3
-
45
-
-
0033805136
-
Current experience with fetoscopy and the Eurofoetus registry for fetoscopic procedures
-
Gratacos E, Deprest J: Current experience with fetoscopy and the Eurofoetus registry for fetoscopic procedures. Eur J Obstet Gynecol Reprod Biol 2000;92:151-159.
-
(2000)
Eur J Obstet Gynecol Reprod Biol
, vol.92
, pp. 151-159
-
-
Gratacos, E.1
Deprest, J.2
|