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Volumn 12, Issue 4, 2005, Pages 744-753

Evidence for encapsidation of prokaryotic sequences during recombinant adeno-associated virus production and their in vivo persistence after vector delivery

Author keywords

Adeno associated virus; DNA packaging; Gene transfer

Indexed keywords

BETA GLUCURONIDASE; CHEMOKINE RECEPTOR CCR5; CHORIONIC GONADOTROPIN; ERYTHROPOIETIN; LEVO IDURONIDASE; PARVOVIRUS VECTOR;

EID: 25144482280     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ymthe.2005.06.003     Document Type: Article
Times cited : (80)

References (37)
  • 2
    • 0013658984 scopus 로고
    • AAV DNA replication, integration and genetics
    • (P. Tjissen, Ed.) CRC Press Boca Raton, FL
    • B.J. Carter E. Mendelson and J.P. Trempe AAV DNA replication, integration and genetics (P. Tjissen, Ed.) Handbook of Parvoviruses Vol. I 1990 CRC Press Boca Raton, FL 169-225
    • (1990) Handbook of Parvoviruses , vol.1 , pp. 169-225
    • Carter, B.J.1    Mendelson, E.2    Trempe, J.P.3
  • 3
    • 0024311525 scopus 로고
    • Helper-free stocks of recombinant adeno-associated viruses: Normal integration does not require viral gene expression
    • R.J. Samulski L.S. Chang and T. Shenk Helper-free stocks of recombinant adeno-associated viruses: Normal integration does not require viral gene expression J. Virol. 63 1989 3822-3828
    • (1989) J. Virol. , vol.63 , pp. 3822-3828
    • Samulski, R.J.1    Chang, L.S.2    Shenk, T.3
  • 4
    • 0002988871 scopus 로고    scopus 로고
    • Production of recombinant adeno-associated viral vectors
    • (N. Dracopoli, Ed.) Wiley New York
    • R. Snyder S. Xiao and R.J. Samulski Production of recombinant adeno-associated viral vectors (N. Dracopoli, Ed.) Current Protocols in Human Genetics Vol. 1 1996 Wiley New York 12.1.1-12.1.23
    • (1996) Current Protocols in Human Genetics , vol.1
    • Snyder, R.1    Xiao, S.2    Samulski, R.J.3
  • 5
    • 0032506752 scopus 로고    scopus 로고
    • Novel tools for production and purification of recombinant adeno-associated virus vectors
    • D. Grimm A. Kern K. Rittner and J. Kleinschmidt Novel tools for production and purification of recombinant adeno-associated virus vectors Hum. Gene Ther. 9 1998 2745-2760
    • (1998) Hum. Gene Ther. , vol.9 , pp. 2745-2760
    • Grimm, D.1    Kern, A.2    Rittner, K.3    Kleinschmidt, J.4
  • 6
    • 2642642141 scopus 로고    scopus 로고
    • Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus
    • X. Xiao J. Li and R.J. Samulski Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus J. Virol. 72 1998 2224-2232
    • (1998) J. Virol. , vol.72 , pp. 2224-2232
    • Xiao, X.1    Li, J.2    Samulski, R.J.3
  • 7
    • 0034218551 scopus 로고    scopus 로고
    • Efficient recombinant adeno-associated virus production by a stable rep-cap HeLa cell line correlates with adenovirus-induced amplification of the integrated rep-cap genome
    • G. Chadeuf et al. Efficient recombinant adeno-associated virus production by a stable rep-cap HeLa cell line correlates with adenovirus-induced amplification of the integrated rep-cap genome J. Gene Med. 2 2000 260-268
    • (2000) J. Gene Med. , vol.2 , pp. 260-268
    • Chadeuf, G.1
  • 9
    • 0036893433 scopus 로고    scopus 로고
    • A novel gene expression control system and its use in stable, high titer 293 cell-based adeno-associated virus packaging cell lines
    • C. Qiao B. Wang X. Zhu J. Li and X. Xiao A novel gene expression control system and its use in stable, high titer 293 cell-based adeno-associated virus packaging cell lines J. Virol. 76 2002 13015-13027
    • (2002) J. Virol. , vol.76 , pp. 13015-13027
    • Qiao, C.1    Wang, B.2    Zhu, X.3    Li, J.4    Xiao, X.5
  • 10
    • 13644257036 scopus 로고    scopus 로고
    • Identification of a replication-defective herpes simplex virus for recombinant adeno-associated virus type 2 (rAAV2) particle assembly using stable producer cell lines
    • E. Toublanc et al. Identification of a replication-defective herpes simplex virus for recombinant adeno-associated virus type 2 (rAAV2) particle assembly using stable producer cell lines J. Gene Med. 6 2004 555-564
    • (2004) J. Gene Med. , vol.6 , pp. 555-564
    • Toublanc, E.1
  • 11
    • 0033054126 scopus 로고    scopus 로고
    • High-titer recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type I expressing AAV-2 rep and cap
    • J.E. Conway et al. High-titer recombinant adeno-associated virus production utilizing a recombinant herpes simplex virus type I expressing AAV-2 rep and cap Gene Ther. 6 1999 986-993
    • (1999) Gene Ther. , vol.6 , pp. 986-993
    • Conway, J.E.1
  • 12
    • 0030769361 scopus 로고    scopus 로고
    • Identification and elimination of replication-competent adeno-associated virus (AAV) that can arise by non homologous recombination during AAV vector production
    • J.M. Allen D.J. Debelak T.C. Reynolds and A.D. Miller Identification and elimination of replication-competent adeno-associated virus (AAV) that can arise by non homologous recombination during AAV vector production J. Virol. 71 1997 6816-6822
    • (1997) J. Virol. , vol.71 , pp. 6816-6822
    • Allen, J.M.1    Debelak, D.J.2    Reynolds, T.C.3    Miller, A.D.4
  • 13
    • 0032549488 scopus 로고    scopus 로고
    • Factors influencing recombinant adeno-associated virus production
    • A. Salvetti et al. Factors influencing recombinant adeno-associated virus production Hum. Gene Ther. 9 1998 695-706
    • (1998) Hum. Gene Ther. , vol.9 , pp. 695-706
    • Salvetti, A.1
  • 14
    • 0031746558 scopus 로고    scopus 로고
    • Characterization of wild-type adeno-associated virus type 2-like particles generated during recombinant viral vector production and strategies for their elimination
    • X.S. Wang et al. Characterization of wild-type adeno-associated virus type 2-like particles generated during recombinant viral vector production and strategies for their elimination J. Virol. 72 1998 5472-5480
    • (1998) J. Virol. , vol.72 , pp. 5472-5480
    • Wang, X.S.1
  • 15
    • 0037213292 scopus 로고    scopus 로고
    • Evidence for packaging rep-cap sequences into AAV-2 capsids in the absence of the inverted terminal repeat: A model for the generation of rep+ AAV particles
    • P. Nony G. Chadeuf J. Tessier P. Moullier and A. Salvetti Evidence for packaging rep-cap sequences into AAV-2 capsids in the absence of the inverted terminal repeat: A model for the generation of rep+ AAV particles J. Virol. 77 2003 776-781
    • (2003) J. Virol. , vol.77 , pp. 776-781
    • Nony, P.1    Chadeuf, G.2    Tessier, J.3    Moullier, P.4    Salvetti, A.5
  • 16
    • 0034805974 scopus 로고    scopus 로고
    • Novel cis-acting replication element in the adeno-associated virus type 2 genome is involved in amplification of integrated rep-cap sequences
    • P. Nony et al. Novel cis-acting replication element in the adeno-associated virus type 2 genome is involved in amplification of integrated rep-cap sequences J. Virol. 75 2001 9991-9994
    • (2001) J. Virol. , vol.75 , pp. 9991-9994
    • Nony, P.1
  • 17
    • 0036478954 scopus 로고    scopus 로고
    • Chromosomal effects of adeno-associated virus vector integration
    • D. Miller E. Rutledge and D. Russell Chromosomal effects of adeno-associated virus vector integration Nat. Genet. 30 2002 147-148
    • (2002) Nat. Genet. , vol.30 , pp. 147-148
    • Miller, D.1    Rutledge, E.2    Russell, D.3
  • 18
    • 0023942356 scopus 로고
    • In vitro excision of adeno-associated virus DNA from recombinant plasmids: Isolation of an enzyme fraction from HeLa cells that cleaves DNA at poly(G) sequences
    • J. Gottlieb and N. Muzyczka In vitro excision of adeno-associated virus DNA from recombinant plasmids: Isolation of an enzyme fraction from HeLa cells that cleaves DNA at poly(G) sequences Mol. Cell. Biol. 6 1988 2513-2522
    • (1988) Mol. Cell. Biol. , vol.6 , pp. 2513-2522
    • Gottlieb, J.1    Muzyczka, N.2
  • 19
    • 0010390169 scopus 로고
    • Cloning of adeno-associated virus into pBR322: Rescue of intact virus from the recombinant plasmid in human cells
    • R.J. Samulski K.I. Berns M. Tam and N. Muzyczka Cloning of adeno-associated virus into pBR322: Rescue of intact virus from the recombinant plasmid in human cells Proc. Natl. Acad. Sci. USA 79 1982 2077-2081
    • (1982) Proc. Natl. Acad. Sci. USA , vol.79 , pp. 2077-2081
    • Samulski, R.J.1    Berns, K.I.2    Tam, M.3    Muzyczka, N.4
  • 20
    • 0023216839 scopus 로고
    • A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication
    • R.J. Samulski L.S. Chang and T. Shenk A recombinant plasmid from which an infectious adeno-associated virus genome can be excised in vitro and its use to study viral replication J. Virol. 61 1987 3096-3101
    • (1987) J. Virol. , vol.61 , pp. 3096-3101
    • Samulski, R.J.1    Chang, L.S.2    Shenk, T.3
  • 21
    • 0025736925 scopus 로고
    • In vitro rescue of an integrated hybrid adeno-associated virus/simian virus 40 genome
    • P. Ward and K.I. Berns In vitro rescue of an integrated hybrid adeno-associated virus/simian virus 40 genome J. Mol. Biol. 218 1991 791-804
    • (1991) J. Mol. Biol. , vol.218 , pp. 791-804
    • Ward, P.1    Berns, K.I.2
  • 22
    • 0031965318 scopus 로고    scopus 로고
    • Role of the adenovirus DNA-binding protein in in vitro adeno-associated virus DNA replication
    • P. Ward F.B. Dean M.E. O'Donnell and K.I. Berns Role of the adenovirus DNA-binding protein in in vitro adeno-associated virus DNA replication J. Virol. 72 1998 420-427
    • (1998) J. Virol. , vol.72 , pp. 420-427
    • Ward, P.1    Dean, F.B.2    O'Donnell, M.E.3    Berns, K.I.4
  • 23
    • 0028050094 scopus 로고
    • Adeno-associated virus DNA replication in vitro: Activation by a maltose binding protein/Rep 68 fusion protein
    • P. Ward E. Urcelay R. Kotin B. Safer and K.I. Berns Adeno-associated virus DNA replication in vitro: Activation by a maltose binding protein/ Rep 68 fusion protein J. Virol. 68 1994 6029-6037
    • (1994) J. Virol. , vol.68 , pp. 6029-6037
    • Ward, P.1    Urcelay, E.2    Kotin, R.3    Safer, B.4    Berns, K.I.5
  • 24
    • 0036366753 scopus 로고    scopus 로고
    • Recombinant adeno-associated viral vector production using stable packaging and producer cell lines
    • L.C. Mathews J.T. Gray M.R. Gallagher and R.O. Snyder Recombinant adeno-associated viral vector production using stable packaging and producer cell lines Methods Enzymol. 346 2002 393-413
    • (2002) Methods Enzymol. , vol.346 , pp. 393-413
    • Mathews, L.C.1    Gray, J.T.2    Gallagher, M.R.3    Snyder, R.O.4
  • 25
    • 0034749286 scopus 로고    scopus 로고
    • Characterization of adenovirus-induced inverted terminal repeat-independent amplification of integrated adeno-associated virus rep-cap sequences
    • J. Tessier and Characterization of adenovirus-induced inverted terminal repeat-independent amplification of integrated adeno-associated virus rep-cap sequences J. Virol. 75 2001 375-383
    • (2001) J. Virol. , vol.75 , pp. 375-383
    • Tessier, J.1
  • 26
    • 0034969457 scopus 로고    scopus 로고
    • Optimization of recombinant adeno-associated virus production using a herpes simplex virus amplicon system
    • E. Feudner M. de Alwis A.J. Thrasher R.R. Ali and S. Fauser Optimization of recombinant adeno-associated virus production using a herpes simplex virus amplicon system J. Virol. Methods 96 2001 97-105
    • (2001) J. Virol. Methods , vol.96 , pp. 97-105
    • Feudner, E.1    de Alwis, M.2    Thrasher, A.J.3    Ali, R.R.4    Fauser, S.5
  • 27
    • 10644230023 scopus 로고    scopus 로고
    • Novel strategy for generation and titration of recombinant adeno-associated virus vectors
    • A.-L. Shiau P.-S. Liu and C.-L. Wu Novel strategy for generation and titration of recombinant adeno-associated virus vectors J. Virol. 79 2005 193-201
    • (2005) J. Virol. , vol.79 , pp. 193-201
    • Shiau, A.-L.1    Liu, P.-S.2    Wu, C.-L.3
  • 28
    • 0036431701 scopus 로고    scopus 로고
    • Insect cells as a factory to produce adeno-associated virus type 2 vectors
    • M. Urabe C. Ding and R.M. Kotin Insect cells as a factory to produce adeno-associated virus type 2 vectors Hum. Gene Ther. 13 2002 1935-1943
    • (2002) Hum. Gene Ther. , vol.13 , pp. 1935-1943
    • Urabe, M.1    Ding, C.2    Kotin, R.M.3
  • 29
    • 0028290387 scopus 로고
    • Identification of linear DNA sequences that specifically bind the adeno-associated virus Rep protein
    • D.M. McCarty et al. Identification of linear DNA sequences that specifically bind the adeno-associated virus Rep protein J. Virol. 68 1994 4988-4997
    • (1994) J. Virol. , vol.68 , pp. 4988-4997
    • McCarty, D.M.1
  • 30
    • 1642525149 scopus 로고    scopus 로고
    • Optimal design of a single recombinant adeno-associated virus derived from serotypes 1 and 2 to achieve more tightly regulated transgene expression from nonhuman primate muscle
    • P. Chenuaud et al. Optimal design of a single recombinant adeno-associated virus derived from serotypes 1 and 2 to achieve more tightly regulated transgene expression from nonhuman primate muscle Mol. Ther. 9 2004 410-418
    • (2004) Mol. Ther. , vol.9 , pp. 410-418
    • Chenuaud, P.1
  • 31
    • 0032959311 scopus 로고    scopus 로고
    • Cloning and characterization of adeno-associated virus type 5
    • J.A. Chiorini F. Kim L. Yang and R.M. Kotin Cloning and characterization of adeno-associated virus type 5 J. Virol. 73 1999 1309-1319
    • (1999) J. Virol. , vol.73 , pp. 1309-1319
    • Chiorini, J.A.1    Kim, F.2    Yang, L.3    Kotin, R.M.4
  • 32
    • 0031691257 scopus 로고    scopus 로고
    • Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue
    • D. Duan et al. Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue J. Virol. 72 1998 8568-8577
    • (1998) J. Virol. , vol.72 , pp. 8568-8577
    • Duan, D.1
  • 33
    • 0034960344 scopus 로고    scopus 로고
    • Extrachromosomal recombinant adeno-associated virus vector genomes are primarily responsible for stable liver transduction in vivo
    • H. Nakai et al. Extrachromosomal recombinant adeno-associated virus vector genomes are primarily responsible for stable liver transduction in vivo J. Virol. 75 2001 6969-6976
    • (2001) J. Virol. , vol.75 , pp. 6969-6976
    • Nakai, H.1
  • 34
    • 0037333815 scopus 로고    scopus 로고
    • Genetic fate of recombinant adeno-associated virus vector genomes in muscle
    • B.C. Schnepp K.R. Clark D.L. Klemanski C.A. Pacak and P.R. Johnson Genetic fate of recombinant adeno-associated virus vector genomes in muscle J. Virol. 77 2003 3495-3504
    • (2003) J. Virol. , vol.77 , pp. 3495-3504
    • Schnepp, B.C.1    Clark, K.R.2    Klemanski, D.L.3    Pacak, C.A.4    Johnson, P.R.5
  • 35
    • 1542369977 scopus 로고    scopus 로고
    • From virus evolution to vector revolution: Use of naturally occurring serotypes of adeno-associated virus (AAV) as novel vectors for human gene therapy
    • D. Grimm and M.A. Kay From virus evolution to vector revolution: Use of naturally occurring serotypes of adeno-associated virus (AAV) as novel vectors for human gene therapy Curr. Gene Ther. 3 2003 281-304
    • (2003) Curr. Gene Ther. , vol.3 , pp. 281-304
    • Grimm, D.1    Kay, M.A.2
  • 36
    • 0020788648 scopus 로고
    • Cloning of infectious adeno-associated virus genomes in bacterial plasmids
    • C.A. Laughlin J.D. Tratschin H. Coon and B.J. Carter Cloning of infectious adeno-associated virus genomes in bacterial plasmids Gene 23 1983 65-73
    • (1983) Gene , vol.23 , pp. 65-73
    • Laughlin, C.A.1    Tratschin, J.D.2    Coon, H.3    Carter, B.J.4
  • 37
    • 0002025785 scopus 로고
    • Manipulation of adenovirus vectors
    • (E.J. Murray, Ed.) Humana Press Clifton, NJ
    • F.L. Graham and L. Prevec Manipulation of adenovirus vectors (E.J. Murray, Ed.) Gene Transfer and Protocol Vol. 7 1991 Humana Press Clifton, NJ 109-128
    • (1991) Gene Transfer and Protocol , vol.7 , pp. 109-128
    • Graham, F.L.1    Prevec, L.2


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