-
1
-
-
0026525713
-
Use of adeno-associated virus as a general transduction vector for mammalian cells
-
Muzyczka, N. (1992). Use of adeno-associated virus as a general transduction vector for mammalian cells. Curr. Top. Microbiol. Immunol. 158: 97-129.
-
(1992)
Curr. Top. Microbiol. Immunol.
, vol.158
, pp. 97-129
-
-
Muzyczka, N.1
-
2
-
-
0033122032
-
Adeno-associated virus-mediated gene delivery
-
Snyder, R. O. (1999). Adeno-associated virus-mediated gene delivery. J. Gene Med. 1: 166-175.
-
(1999)
J. Gene Med.
, vol.1
, pp. 166-175
-
-
Snyder, R.O.1
-
3
-
-
0038352973
-
AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B
-
Manna, C. S., et al. (2002). AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B. Blood 19: 19.
-
(2002)
Blood
, vol.19
, pp. 19
-
-
Manna, C.S.1
-
4
-
-
0033761804
-
Adeno-associated virus vectors for gene therapy: More pros than cons?
-
Monahan, P. E., and Samulski, R. J. (2000). Adeno-associated virus vectors for gene therapy: More pros than cons? Mol. Med. Today 6: 433-440.
-
(2000)
Mol. Med. Today
, vol.6
, pp. 433-440
-
-
Monahan, P.E.1
Samulski, R.J.2
-
5
-
-
0026720075
-
Tight control of gene expression in mammalian cells by tetracyclin-responsive promoters
-
Gossen, M., and Bulard, H. (1992). Tight control of gene expression in mammalian cells by tetracyclin-responsive promoters. Proc. Natl. Acad. Sci. USA 89: 5547-5551.
-
(1992)
Proc. Natl. Acad. Sci. USA
, vol.89
, pp. 5547-5551
-
-
Gossen, M.1
Bulard, H.2
-
6
-
-
0030965628
-
Ligand-inducible and liver-specific target gene expression in transgenic mice
-
Wang, Y., DeMayo, F. J., Tsai, S. Y., and O'Malley, B. W. (1996). Ligand-inducible and liver-specific target gene expression in transgenic mice. Nat. Biotechnol. 15: 239-243.
-
(1996)
Nat. Biotechnol.
, vol.15
, pp. 239-243
-
-
Wang, Y.1
DeMayo, F.J.2
Tsai, S.Y.3
O'Malley, B.W.4
-
7
-
-
0029865151
-
Ecdysone-inducible gene expression in mammalian cells and transgenic mice
-
No, D., Yao, T. P., and Evans, R. M. (1996). Ecdysone-inducible gene expression in mammalian cells and transgenic mice. Proc. Natl. Acad. Sci. USA 93: 3346-3351.
-
(1996)
Proc. Natl. Acad. Sci. USA
, vol.93
, pp. 3346-3351
-
-
No, D.1
Yao, T.P.2
Evans, R.M.3
-
8
-
-
9544226448
-
A humanized system for pharmacologic control of gene expression
-
Rivera, V. M., et al. (2002). A humanized system for pharmacologic control of gene expression. Nat. Med. 2: 1028-1032.
-
(2002)
Nat. Med.
, vol.2
, pp. 1028-1032
-
-
Rivera, V.M.1
-
9
-
-
0032170592
-
Control of erythropoietin delivery by doxycyclin in mice after intramuscular injection of adeno-associated vector
-
Bohl, D., Salvetti, A., Moullier, P., and Heard, J. M. (1998). Control of erythropoietin delivery by doxycyclin in mice after intramuscular injection of adeno-associated vector. Blood 92: 1512-1517.
-
(1998)
Blood
, vol.92
, pp. 1512-1517
-
-
Bohl, D.1
Salvetti, A.2
Moullier, P.3
Heard, J.M.4
-
10
-
-
0036827724
-
Lack of immune response against the tetracycline-dependent transactivator correlates with long-term doxycycline-regulated transgene expression in nonhuman primates after intramuscular injection of recombinant adeno-associated virus
-
Favre, D., et al. (2002). Lack of immune response against the tetracycline-dependent transactivator correlates with long-term doxycycline-regulated transgene expression in nonhuman primates after intramuscular injection of recombinant adeno-associated virus. J. Virol. 76: 11605-11611.
-
(2002)
J. Virol.
, vol.76
, pp. 11605-11611
-
-
Favre, D.1
-
11
-
-
0028030082
-
Mechanisms underlying expression of Tn10 encoded tetracycline resistance
-
Hillen, W., and Berens, C. (1994). Mechanisms underlying expression of Tn10 encoded tetracycline resistance. Annu. Rev. Microbiol. 48: 345-369.
-
(1994)
Annu. Rev. Microbiol.
, vol.48
, pp. 345-369
-
-
Hillen, W.1
Berens, C.2
-
12
-
-
0029022369
-
Transcriptional activation by tetracyclines in mammalian cells
-
Gossen, M., et al. (1995). Transcriptional activation by tetracyclines in mammalian cells. Science 268: 1766-1769.
-
(1995)
Science
, vol.268
, pp. 1766-1769
-
-
Gossen, M.1
-
13
-
-
0034608802
-
Exploring the sequence space for tetracycline-dependent transcriptional activators: Novel mutations yield expanded range and sensitivity
-
Urlinger, S., et al. (2000). Exploring the sequence space for tetracycline-dependent transcriptional activators: Novel mutations yield expanded range and sensitivity. Proc. Natl. Acad. Sci. USA 97: 7963-7968.
-
(2000)
Proc. Natl. Acad. Sci. USA
, vol.97
, pp. 7963-7968
-
-
Urlinger, S.1
-
14
-
-
0027412209
-
Expression of the cystic fibrosis transmembrane conductance regulator from a novel adeno-associated virus promoter
-
Flotte, T. R., et al. (1993). Expression of the cystic fibrosis transmembrane conductance regulator from a novel adeno-associated virus promoter. J. Biol. Chem. 268: 3781-3790.
-
(1993)
J. Biol. Chem.
, vol.268
, pp. 3781-3790
-
-
Flotte, T.R.1
-
15
-
-
0033857632
-
Novel transcriptional regulatory signals in the adeno-associated virus terminal repeat A/D junction element
-
Haberman, R. P., McCown, T. J., and Samulski, R. J. (2000). Novel transcriptional regulatory signals in the adeno-associated virus terminal repeat A/D junction element. J. Virol. 74: 8732-8739.
-
(2000)
J. Virol.
, vol.74
, pp. 8732-8739
-
-
Haberman, R.P.1
McCown, T.J.2
Samulski, R.J.3
-
16
-
-
0033588890
-
Enhanced expression of transgenes from adeno-associated virus vectors with the woodchuck hepatitis virus posttranscriptional regulatory element: Implications for gene therapy
-
Loeb, J. E., Cordier, W. S., Harris, M. E., Weitzman, M. D., and Hope, T. J. (1999). Enhanced expression of transgenes from adeno-associated virus vectors with the woodchuck hepatitis virus posttranscriptional regulatory element: Implications for gene therapy. Hum. Gene Ther. 10: 2295-2305.
-
(1999)
Hum. Gene Ther.
, vol.10
, pp. 2295-2305
-
-
Loeb, J.E.1
Cordier, W.S.2
Harris, M.E.3
Weitzman, M.D.4
Hope, T.J.5
-
17
-
-
0032978712
-
Woodchuck hepatitis virus posttranscriptional regulatory element enhances expression of transgenes delivered by retroviral vectors
-
Zufferey, R., Donello, J., Trono, D., and Hope, T. (1999). Woodchuck hepatitis virus posttranscriptional regulatory element enhances expression of transgenes delivered by retroviral vectors. J. Virol. 73: 2886-2892.
-
(1999)
J. Virol.
, vol.73
, pp. 2886-2892
-
-
Zufferey, R.1
Donello, J.2
Trono, D.3
Hope, T.4
-
18
-
-
0024311525
-
Helper-free stocks of recombinant adeno-associated viruses: Normal integration does not require viral gene expression
-
Samulski, R. J., Chang, L. S., and Shenk, T. (2002). Helper-free stocks of recombinant adeno-associated viruses: Normal integration does not require viral gene expression. J. Virol. 63: 3822-3828.
-
(2002)
J. Virol.
, vol.63
, pp. 3822-3828
-
-
Samulski, R.J.1
Chang, L.S.2
Shenk, T.3
-
19
-
-
0025884056
-
Efficient selection for high-expression transfectants with a novel eukaryotic vector
-
Niwa, H., Yamamura, K., and Miyazaki, J. (1989). Efficient selection for high-expression transfectants with a novel eukaryotic vector. Gene 108: 193-199.
-
(1989)
Gene
, vol.108
, pp. 193-199
-
-
Niwa, H.1
Yamamura, K.2
Miyazaki, J.3
-
20
-
-
0025865925
-
High level desmin expression depends on a muscle-specific enhancer
-
Li, Z., and Paulin, D. (1991). High level desmin expression depends on a muscle-specific enhancer. J. Biol. Chem. 266: 6562-6570.
-
(1991)
J. Biol. Chem.
, vol.266
, pp. 6562-6570
-
-
Li, Z.1
Paulin, D.2
-
21
-
-
0032506752
-
Novel tools for production and purification of recombinant adeno-associated virus vectors
-
Grimm, D., Kern, A., Rittner, K., and Kleinschmidt, J. (1998). Novel tools for production and purification of recombinant adeno-associated virus vectors. Hum. Gene Ther. 9: 2745-2760.
-
(1998)
Hum. Gene Ther.
, vol.9
, pp. 2745-2760
-
-
Grimm, D.1
Kern, A.2
Rittner, K.3
Kleinschmidt, J.4
-
22
-
-
0035667722
-
Immediate and long-term safety of recombinant adeno-associated virus injection into the nonhuman primate muscle
-
Favre, D., et al. (2001). Immediate and long-term safety of recombinant adeno-associated virus injection into the nonhuman primate muscle. Mol. Ther. 4: 559-566.
-
(2001)
Mol. Ther.
, vol.4
, pp. 559-566
-
-
Favre, D.1
-
23
-
-
0036140216
-
Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity
-
Rabinowitz, J. E., et al. (2002). Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity. J. Virol. 76: 791-801.
-
(2002)
J. Virol.
, vol.76
, pp. 791-801
-
-
Rabinowitz, J.E.1
-
24
-
-
0032549488
-
Factors influencing recombinant adeno-associated virus production
-
Salvetti, A., et al. (1998). Factors influencing recombinant adeno-associated virus production. Hum. Gene Ther. 9: 695-706.
-
(1998)
Hum. Gene Ther.
, vol.9
, pp. 695-706
-
-
Salvetti, A.1
-
25
-
-
0032924185
-
Gene therapy vectors based on adeno-associated virus type 1
-
Xiao, W., et al. (1999). Gene therapy vectors based on adeno-associated virus type 1. J. Virol. 73: 3994-4003.
-
(1999)
J. Virol.
, vol.73
, pp. 3994-4003
-
-
Xiao, W.1
-
26
-
-
9144271167
-
Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1
-
Arruda, V. R., et al. (2004). Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1. Blood 103: 85-92.
-
(2004)
Blood
, vol.103
, pp. 85-92
-
-
Arruda, V.R.1
-
27
-
-
1642497091
-
Controlled transgene expression by E1 -E4-defective adenovirus vectors harbouring a "tet-on" switch system
-
Fender, P., et al. (2002). Controlled transgene expression by E1S-E4-defective adenovirus vectors harbouring a "tEt-on" switch system. J. Gene Med. 4: 668-675.
-
(2002)
J. Gene Med.
, vol.4
, pp. 668-675
-
-
Fender, P.1
-
28
-
-
0030868549
-
Versatile retrovirus vector systems for regulated gene expression in vitro and in vivo
-
Lindemann, D., Patriquin, E., Feng, S., and Mulligan, R. C. (1997). Versatile retrovirus vector systems for regulated gene expression in vitro and in vivo. Mol. Med. 3: 466-476.
-
(1997)
Mol. Med.
, vol.3
, pp. 466-476
-
-
Lindemann, D.1
Patriquin, E.2
Feng, S.3
Mulligan, R.C.4
-
29
-
-
0032600013
-
A tetracycline controlled activation/repression system with increased potential for gene transfer into mammalian cells
-
Freundlieb, S., Schirra-Muller, C., and Bujard, H. (1999). A tetracycline controlled activation/repression system with increased potential for gene transfer into mammalian cells. J. Gene Med. 1: 4-12.
-
(1999)
J. Gene Med.
, vol.1
, pp. 4-12
-
-
Freundlieb, S.1
Schirra-Muller, C.2
Bujard, H.3
-
30
-
-
0034567011
-
Cell-type-specific and regulatable transgenesis in the adult brain: Adenovirus-encoded combined transcriptional targeting and inducible transgene expression
-
Smith-Arica, J. R., et al. (2000). Cell-type-specific and regulatable transgenesis in the adult brain: Adenovirus-encoded combined transcriptional targeting and inducible transgene expression. Mol. Ther. 2: 579-587.
-
(2000)
Mol. Ther.
, vol.2
, pp. 579-587
-
-
Smith-Arica, J.R.1
-
31
-
-
0035001375
-
Switching on and off transgene expression within lactotrophic cells in the anterior pituitary gland in vivo
-
Smith-Arica, J. R., et al. (2000). Switching on and off transgene expression within lactotrophic cells in the anterior pituitary gland in vivo. Endocrinology 142: 2521-2532.
-
(2000)
Endocrinology
, vol.142
, pp. 2521-2532
-
-
Smith-Arica, J.R.1
-
32
-
-
0036846578
-
Tight control of gene expression by a helper-dependent adenovirus vector carrying the rtTA2(s)-M2 tetracycline transactivator and repressor system
-
Salucci, V., et al. (2002). Tight control of gene expression by a helper-dependent adenovirus vector carrying the rtTA2(s)-M2 tetracycline transactivator and repressor system. Gene Ther. 9: 1415-1421.
-
(2002)
Gene Ther.
, vol.9
, pp. 1415-1421
-
-
Salucci, V.1
-
33
-
-
0034984667
-
Recombinant AAV-mediated delivery of a tet-inducible reporter gene to the rat retina
-
McGee Sanftner, L. H., et al. (2001). Recombinant AAV-mediated delivery of a tet-inducible reporter gene to the rat retina. Mol. Ther. 3: 688-696.
-
(2001)
Mol. Ther.
, vol.3
, pp. 688-696
-
-
McGee Sanftner, L.H.1
-
34
-
-
0036171329
-
Tightly regulated long-term erythropoietin expression in vivo using tet-inducible recombinant adeno-associated viral vectors
-
Rendahl, K. G., et al. (2002). Tightly regulated long-term erythropoietin expression in vivo using tet-inducible recombinant adeno-associated viral vectors. Hum. Gene Ther. 13: 335-342.
-
(2002)
Hum. Gene Ther.
, vol.13
, pp. 335-342
-
-
Rendahl, K.G.1
-
35
-
-
18244382853
-
Stringent control of gene expression in vivo by using novel doxycycline-dependent trans-activators
-
Lamartina, S., et al. (2002). Stringent control of gene expression in vivo by using novel doxycycline-dependent trans-activators. Hum. Gene Ther. 13: 199-210.
-
(2002)
Hum. Gene Ther.
, vol.13
, pp. 199-210
-
-
Lamartina, S.1
-
36
-
-
0034581163
-
Tet repressor-based system for regulated gene expression in eukaryotic cells: Principles and advances
-
Baron, U., and Bujard, H. (2000). Tet repressor-based system for regulated gene expression in eukaryotic cells: Principles and advances. Methods Enzymol. 327: 401-421.
-
(2000)
Methods Enzymol.
, vol.327
, pp. 401-421
-
-
Baron, U.1
Bujard, H.2
-
37
-
-
0037301576
-
Construction of an rtTA2(s)-m2/tts(kid)-based transcription regulatory switch that displays no basal activity, good inducibility, and high responsiveness to doxycycline in mice and non-human primates
-
Lamartina, S., et al. (2003). Construction of an rtTA2(s)-m2/tts(kid)-based transcription regulatory switch that displays no basal activity, good inducibility, and high responsiveness to doxycycline in mice and non-human primates. Mol. Ther. 7: 271-280.
-
(2003)
Mol. Ther.
, vol.7
, pp. 271-280
-
-
Lamartina, S.1
-
38
-
-
0029849257
-
Quantitative analysis of the packaging capacity of recombinant adeno-associated virus
-
Dong, J. Y., Fan, P. D., and Frizzell, R. A. (1996). Quantitative analysis of the packaging capacity of recombinant adeno-associated virus. Hum. Gene Ther. 7: 2101-2112.
-
(1996)
Hum. Gene Ther.
, vol.7
, pp. 2101-2112
-
-
Dong, J.Y.1
Fan, P.D.2
Frizzell, R.A.3
-
39
-
-
0037351165
-
Doxycycline-regulated lentiviral vector system with a novel reverse transactivator rtTA2(S)-M2 shows a tight control of gene expression in vitro and in vivo
-
Koponen, J. K., et al. (2003). Doxycycline-regulated lentiviral vector system with a novel reverse transactivator rtTA2(S)-M2 shows a tight control of gene expression in vitro and in vivo. Gene Ther. 10: 459-466.
-
(2003)
Gene Ther.
, vol.10
, pp. 459-466
-
-
Koponen, J.K.1
-
40
-
-
0034572459
-
Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors
-
Chao, H., et al. (2000). Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors. Mol. Ther. 2: 619-623.
-
(2000)
Mol. Ther.
, vol.2
, pp. 619-623
-
-
Chao, H.1
|