Non-viral delivery of the porphobilinogen deaminase cDNA into a mouse model of acute intermittent porphyria

Molecular Genetics and Metabolism

Volumn 82, Issue 1, 2004, Pages 20-26

  Johansson, Annika ^a   Nowak, Grzegorz ^a   Möller, Christer ^b   Harper, Pauline ^a  

^a KAROLINSKA UNIVERSITY HOSPITAL   (Sweden)

^b HemeBiotech A/S   (Sweden)

Author keywords

Acute intermittent porphyria; Galactose; Liposomes; Luciferase; Non viral gene delivery; Polyethylenimine; Porphobilinogen deaminase

Indexed keywords

1,2 DIOLEOYL 3 TRIMETHYLAMMONIOPROPANE; CHOLESTEROL; COMPLEMENTARY DNA; GALACTOSE; LIPOSOME; LUCIFERASE; NAKED DNA; POLYETHYLENEIMINE; PORPHOBILINOGEN DEAMINASE;

ACUTE INTERMITTENT PORPHYRIA; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BLOOD FLOW; CONTROLLED STUDY; DRUG EFFICACY; DRUG FORMULATION; FEMALE; GENE CONSTRUCT; LIVER; LUNG; MALE; MOUSE; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; POLYMERASE CHAIN REACTION; PORTAL VEIN; PRIORITY JOURNAL; PROTEIN EXPRESSION; REPORTER GENE; TRANSGENIC MOUSE;

ANIMALS; BRAIN; DISEASE MODELS, ANIMAL; DNA, COMPLEMENTARY; FEMALE; GALACTOSE; GENE THERAPY; GENE TRANSFER TECHNIQUES; HYDROXYMETHYLBILANE SYNTHASE; INJECTIONS, INTRAVENOUS; KIDNEY; LIPOSOMES; LIVER; LUCIFERASES; LUNG; MALE; MICE; MICE, INBRED C57BL; POLYETHYLENEIMINE; PORPHYRIA, ACUTE INTERMITTENT;

MURINAE; MUS MUSCULUS;

EID: 1942521286     PISSN: 10967192     EISSN: None     Source Type: Journal    
DOI: 10.1016/j.ymgme.2004.02.008     Document Type: Article

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