Long-term and therapeutic-level hepatic gene expression of human factor IX after naked plasmid transfer in vivo

Molecular Therapy

Volumn 3, Issue 6, 2001, Pages 947-957

  Miao, Carol H ^a   Thompson, Arthur R ^a   Loeb, Keith ^b   Ye, Xin ^a  

^a UNIVERSITY OF WASHINGTON   (United States)

^b Fred Hutchinson Cancer Research Center   (United States)

Author keywords

Factor IX; Hemophilia; Liver specific expression; Naked DNA transfer

Indexed keywords

ALPHA 1 ANTITRYPSIN; AMINOTRANSFERASE; ANTIBODY; APOLIPOPROTEIN E; BLOOD CLOTTING FACTOR 9; CELL DNA; COMPLEMENTARY DNA; PLASMID DNA; PLASMID VECTOR; SODIUM CHLORIDE;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CIRCULATION; CONTROLLED STUDY; CYTOTOXICITY; DNA TRANSFER; DNA VECTOR; EPISOME; GENE CASSETTE; GENE EXPRESSION; GENE LOCUS; GENE TRANSFER; GENETIC TRANSCRIPTION; GENOME; INTRON; LIVER; LIVER HISTOLOGY; LIVER INJURY; LIVER REGENERATION; MOUSE; NONHUMAN; PARTIAL HEPATECTOMY; PLASMID; POLYADENYLATION; PROMOTER REGION; REVERSE TRANSCRIPTION POLYMERASE CHAIN REACTION; SIGNAL TRANSDUCTION; SOUTHERN BLOTTING; TISSUE REPAIR; TRANSGENE;

EID: 0034950612     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1006/mthe.2001.0333     Document Type: Article

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