Correction of the biochemical defect in porphobilinogen deaminase deficient cells by non-viral gene delivery

Molecular and Cellular Biochemistry

Volumn 250, Issue 1-2, 2003, Pages 65-71

  Johansson, Annika ^a   Möller, Christer ^b   Harper, Pauline ^a  

^a KAROLINSKA UNIVERSITY HOSPITAL   (Sweden)

^b HemeBiotech A/S   (Sweden)

Author keywords

5 aminolevulinic acid (ALA); Acute intermittent porphyria (AIP); Non viral gene delivery; Plasmid DNA; Porphobilinogen (PBG); Porphobilinogen deaminase (PBGD); Protoporphyrin (PP)

Indexed keywords

AMINOLEVULINIC ACID; HEME; PLASMID DNA; PORPHOBILINOGEN; PORPHOBILINOGEN DEAMINASE; PROTOPORPHYRIN;

ACUTE INTERMITTENT PORPHYRIA; ANIMAL CELL; ANIMAL TISSUE; ARTICLE; CONTROLLED STUDY; ENZYME ACTIVITY; FIBROBLAST; HEME SYNTHESIS; HIGH PERFORMANCE LIQUID CHROMATOGRAPHY; HUMAN; HUMAN CELL; HUMAN TISSUE; INCUBATION TIME; INTERMETHOD COMPARISON; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; PLASMID; PROTEIN EXPRESSION;

AMINOLEVULINIC ACID; ANIMALS; CHROMATOGRAPHY, HIGH PRESSURE LIQUID; FIBROBLASTS; GENE TRANSFER TECHNIQUES; GENETIC TECHNIQUES; GENETIC VECTORS; HEME; HUMANS; HYDROXYMETHYLBILANE SYNTHASE; MICE; PHOTOSENSITIZING AGENTS; PLASMIDS; PORPHYRIA, ACUTE INTERMITTENT; PROTOPORPHYRINS; TIME FACTORS; TRANSFECTION;

ANIMALIA;

EID: 0042386222     PISSN: 03008177     EISSN: None     Source Type: Journal    
DOI: 10.1023/A:1024946216776     Document Type: Article

References (19)

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