Therapeutic challenges in childhood sickle cell disease Part 1: Current and future treatment options

British Journal of Haematology

Volumn 120, Issue 5, 2003, Pages 725-736

  Amrolia, Persis J ^a   Almeida, Antonio ^a   Halsey, Christina ^b   Roberts, Irene A G ^b   Davies, Sally C ^b  

^a GREAT ORMOND STREET HOSPITAL   (United Kingdom)

^b CENTRAL MIDDLESEX HOSPITAL   (United Kingdom)

Author keywords

Bone marrow transplantation; Hydroxyurea; Sickle cell disease; Transfusion

Indexed keywords

ANTISICKLING AGENT; ARGININE BUTYRATE; BETA GLOBIN; BUSULFAN; BUTYRIC ACID DERIVATIVE; CLOTRIMAZOLE; CYCLOPHOSPHAMIDE; CYCLOSPORIN; DEFERIPRONE; DEFEROXAMINE; FLUDARABINE; HEMOGLOBIN; HEMOGLOBIN F; HYDROXYUREA; LENTIVIRUS VECTOR; MAGNESIUM; MELPHALAN; MYCOPHENOLIC ACID 2 MORPHOLINOETHYL ESTER; NITRIC OXIDE; NS 1652; NS 3623; POLOXAMER; SHORT CHAIN FATTY ACID; THYMOCYTE ANTIBODY; UNCLASSIFIED DRUG;

ACUTE CHEST SYNDROME; ACUTE LYMPHOBLASTIC LEUKEMIA; ALLOIMMUNIZATION; BLOOD TRANSFUSION; BLOOD VESSEL OCCLUSION; BONE MARROW SUPPRESSION; BONE MARROW TRANSPLANTATION; CLINICAL TRIAL; DEHYDRATION; DISEASE SEVERITY; DRUG EFFICACY; DRUG SAFETY; ERYTHROCYTE; GENE THERAPY; GRAFT VERSUS HOST REACTION; HLA MATCHING; HODGKIN DISEASE; HUMAN; INFECTION; INFERTILITY; IRON OVERLOAD; LEUKEMOGENESIS; MULTIPLE ORGAN FAILURE; NAUSEA; NEUROLOGIC DISEASE; NONHUMAN; OXYGEN AFFINITY; PAIN; PATIENT SELECTION; PEDIATRICS; PRIORITY JOURNAL; QUALITY OF LIFE; RASH; REVIEW; SICKLE CELL ANEMIA; SICKLE CELL CRISIS; STEM CELL TRANSPLANTATION; STROKE; SURVIVAL; THALASSEMIA MAJOR; TOXICITY; TREATMENT INDICATION; VOMITING;

ANEMIA, SICKLE CELL; ANTISICKLING AGENTS; BONE MARROW TRANSPLANTATION; CELL ADHESION MOLECULES; CHILD; CLINICAL TRIALS; ERYTHROCYTE TRANSFUSION; FATTY ACIDS, VOLATILE; FETAL BLOOD; GENE THERAPY; HUMANS; HYDROXYUREA; PATIENT SELECTION; STEM CELL TRANSPLANTATION;

EID: 0037335688     PISSN: 00071048     EISSN: None     Source Type: Journal    
DOI: 10.1046/j.1365-2141.2003.04143.x     Document Type: Review

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