Impact of bone marrow transplantation for symptomatic sickle cell disease: An interim report

Blood

Volumn 95, Issue 6, 2000, Pages 1918-1924

  Walters, Mark C ^b   Storb, Rainer ^b   Patience, Melinda ^b   Leisenring, Wendy ^b   Taylor, Terri ^b   Sanders, Jean E ^b   Buchanan, George E ^b   Rogers, Zora R ^b   Dinndorf, Patricia ^b   Davies, Sally C ^b   Roberts, Irene A G ^b   Dickerhoff, Rosarita ^b   Yeager, Andrew M ^b   Lewis, Hsu ^b   Kurtzberg, Joanne ^b   Ohene Frempong, Kwaku ^b   Bunin, Nancy ^b   Bernaudin, Francoise ^b   Wong, Wing Yen ^b   Scott, J Paul ^b   Margolis, David ^b   Vichinsky, Elliott ^b   Wall, Donna A ^b   Wayne, Allen S ^b   Pegelow, Charles ^b   Redding Lallinger, Rupa ^b   Wiley, Joseph ^b   Klemperer, Martin ^b   Mentzer, William C ^b   Smith, Franklin O ^b   Sullivan, Keith M ^a   more..

^a DUKE UNIVERSITY MEDICAL CENTER   (United States)

^b NONE

Author keywords

[No Author keywords available]

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CYCLOPHOSPHAMIDE; CYCLOSPORIN; METHOTREXATE; PREDNISONE; THYMOCYTE ANTIBODY;

ADOLESCENT; ALLOGENIC BONE MARROW TRANSPLANTATION; ARTICLE; BODY HEIGHT; CENTRAL NERVOUS SYSTEM DISEASE; CHILD; CLINICAL ARTICLE; FEMALE; GRAFT VERSUS HOST REACTION; HUMAN; IMMUNOSUPPRESSIVE TREATMENT; LUNG DISEASE; LUNG FUNCTION TEST; MALE; NUCLEAR MAGNETIC RESONANCE IMAGING; PRIORITY JOURNAL; QUALITY OF LIFE; SICKLE CELL ANEMIA; SURVIVAL;

ADOLESCENT; ANEMIA, SICKLE CELL; BODY HEIGHT; BONE MARROW TRANSPLANTATION; CARDIOVASCULAR DISEASES; CHILD; CHILD, PRESCHOOL; COHORT STUDIES; DISEASE-FREE SURVIVAL; ENDOCRINE GLANDS; FEMALE; FOLLOW-UP STUDIES; HUMANS; LUNG; MALE; TIME FACTORS; TISSUE DONORS;

EID: 0034654139     PISSN: 00064971     EISSN: None     Source Type: Journal    
DOI: None     Document Type: Article

References (41)

1. Johnson FL, Look AT, Gockerman J, Ruggiero MR, Dalla-Pozza L, Billings FT. Bone-marrow transplantation in a patient with sickle-cell anemia. N Engl J Med. 1984;311:780.
2. Vermylen C, Cornu G, Philippe M, et al. Bone marrow transplantation in sickle cell anaemia. Arch Dis Child. 1991;66:1195.
3. Walters MC, Patience M, Leisenring W, et al. Bone marrow transplantation for sickle cell disease [see comments]. N Engl J Med. 1996;335: 369.
4. Thomas ED, Buckner CD, Sanders JE, et al. Marrow transplantation for thalassaemia Lancet. 1982;2:227.
5. Lucarelli G, Galimberti M, Polchi P, et al. Bone marrow transplantation in patients with thalassemia. N Engl J Med. 1990;322:417.
6. Lucarelli G, Galimberti M, Giardini C, et al. Bone marrow transplantation in thalassemia. The experience of Pesaro. Ann N Y Acad Sci. 1998;850: 270.
7. Mentzer WC, Heller S, Pearle PR, Hackney E, Vichinsky E. Availability of related donors for bone marrow transplantation in sickle cell anemia. Am J Pediatr Hematol Oncol. 1994;16:27.
8. Walters MC, Patience M, Leisenring W, et al. Barriers to bone marrow transplantation for sickle cell anemia. Biol Blood Marrow Transplant. 1996; 2:100.
9. Bernaudin F, Souillet G, Vannier JP, et al. Report of the French experience concerning 26 children transplanted for severe sickle cell disease. Bone Marrow Transplant. 1997;19(suppl 2):112.
10. Walters MC, Patience M, Leisenring W, et al. Collaborative multicenter investigation of marrow transplantation for sickle cell disease: current results and future directions. Biol Blood Marrow Transplant. 1997;3:310.
11. Vermylen C, Comu G, Ferster A, et al. Haemato-poietic stem cell transplantation for sickle cell anaemia: the first 50 patients transplanted in Belgium. Bone Marrow Transplant. 1998;22:1.
12. Powars D, Weidman JA, Odom-Maryon T, Niland JC, Johnson C. Sickle cell chronic lung disease: prior morbidity and the risk of pulmonary failure. Medicine. 1988;67:66.
13. Chao NJ, Schmidt GM, Niland JC, et al. Cyclosporine, methotrexate, and prednisone compared with cyclosporine and prednisone for prophylaxis of acute graft-versus-host disease. N Engl J Med. 1993;329:1225.
14. Storb R, Deeg HJ, Whitehead J, et al. Methotrexate and cyclosporine compared with cyclosporine alone for prophylaxis of acute graft versus host disease after marrow transplantation for leukemia. N Engl J Med. 1986;314:729.
15. Walters MC, Sullivan KM, Bernaudin F, et al. Neurologic complications after allogeneic marrow transplantation for sickle cell anemia [see comments]. Blood. 1995;85:879.
16. Ferster A, Christophe C, Dan B, Devalck C, Sariban E. Neurologic complications after bone marrow transplantation for sickle cell anemia [letter; comment]. Blood. 1995;86:408.
17. Schoenberg JB, Beck GJ, Bouhuys A. Growth and decay of pulmonary function in healthy blacks and whites. Respir Physiol. 1978;33:367.
18. Hill I. Applied Statistics Algorithms. Chichester, UK: Ellis Horwood; 1985.
19. Lansky SB, List MA, Lansky LL, Ritter-Sterr C, Miller DR. The measurement of performance in childhood cancer patients. Cancer. 1987;60:1651.
20. Kaplan EL, Meier P. Nonparametric estimation from incomplete observations. J Am Stat Assoc. 1958;53:457.
21. Kalbfleisch JD, Prentice RL. The Statistical Analysis of Failure Time Data. New York, NY: John Wiley; 1980.
22. Abboud MR, Jackson SM, Barredo J, Holden KR, Cure J, Laver J. Neurologic complications following bone marrow transplantation for sickle cell disease. Bone Marrow Transplant. 1996;17:405.
23. Wolman IJ, Ortolani M. Some clinical features of Cooley's anemia patients as related to transfusion schedules. Ann N Y Acad Sci. 1969;165:407.
24. De Sanctis V, Vullo C, Katz M, et al. Endocrine complications in thalassaemia major. Prog Clin Biol Res. 1989;309:77.
25. Platt OS, Rosenstock W, Espeland MA. Influence of sickle hemoglobinopathies on growth and development. N Engl J Med. 1984;311:7.
26. Singhal A, Morris J, Thomas P, Dover G, Higgs D, Serjeant G. Factors affecting prepubertal growth in homozygous sickle cell disease. Arch Dis Child. 1996;74:502.
27. Giorgiani G, Bozzola M, Locatelli F, et al. Role of busulfan and total body irradiation on growth of prepubertal children receiving bone marrow transplantation and results of treatment with recombinant human growth hormone. Blood. 1995; 86:825.
28. Cohen A, van Lint MT, Uderzo C, et al. Growth in patients after allogeneic bone marrow transplant for hematological diseases in childhood. Bone Marrow Transplant. 1995;15:343.
29. Michel G, Socie G, Gebhard F, et al. Late effects of allogeneic bone marrow transplantation for children with acute myeloblastic leukemia in first complete remission: the impact of conditioning regimen without total-body irradiation - a report from the Societe Francaise de Greffe de Moelle. J Clinic Oncol. 1997;15:2238.
30. Sanders JE. Growth and development after hematopoietic cell transplantation. In: Thomas ED, Blume KG, Forman SJ, eds. Hematopoietic Cell Transplantation. 2nd ed. Malden, MA: Blackwell Science; 1998.
31. Uldall PR, Kerr DN, Tacchi D. Sterility and cyclophosphamide. Lancet. 1972;1:693.
32. Sanders JE, Hawley J, Levy W, et al. Pregnancies following high-dose cyclophosphamide with or without high-dose busulfan or total-body irradiation and bone marrow transplantation. Blood. 1996;87:3045.
33. De Sanctis V, Galimberti M, Lucarelli G, et al. Gonadal function in long term survivors with B thalassemia major following bone marrow transplantation. Bone Marrow Transplant. 1993;12(suppl 1):104.
34. De Simone M, Olioso P, Di Bartolomeo P, et al. Growth and endocrine function following bone marrow transplantation for thalassemia. Bone Marrow Transplant. 1995;15:227.
35. Kar AB, Kamboj VP, Chandra H. Effect of some chemicals on spermatogenesis in rhesus monkeys. J Reprod Fertil. 1968;16:165.
36. Merchant-Larios H, Coello J. The effect of busulfan on ra1 primordial germ cells at the ultrastructural level. Cell Differ. 1979;8:145.
37. Storb R, Yu C, Deeg HJ, et al. Current and future preparative regimens for bone marrow transplantation in thalassemia. Ann N Y Acad Sci. 1998; 850:276.
38. Pegelow CH, Adams RJ, McKie V, et al. Risk of recurrent stroke in patients with sickle cell disease treated with erythrocyte transfusions. J Pediatr. 1995;126:896.
39. Walters M. Hematopoietic cell transplantation for sickle cell disease. In: Thomas ED, Blume KG, Forman SJ. eds. Hematopoietic Cell Transplantation. 2nd ed. Malden, MA: Blackwell Science; 1998.
40. Winter JS, Faiman C, Hobson WC, Prasad AV, Reyes FI. Pituitary-gonadal relations in infancy. I. Patterns of serum gonadotropin concentrations from birth to four years of age in man and chimpanzee. J Clin Endocrinol Metab. 1975;40:545.
41. Penny R. The testis. Pediatr Clin North Am. 1979; 26:107.