Biodistribution and efficacy of donor T lymphocytes in a murine model of lysosomal storage disease

Molecular Therapy

Volumn 7, Issue 1, 2003, Pages 52-61

  Young, Pampee P ^a   Vogler, Carole ^b   Hofling, A Alex ^a   Sands, Mark S ^a  

^a WASHINGTON UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b SAINT LOUIS UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

Adoptive transfer; Cell trafficking; Gene therapy; Lymphocyte; Lysosomal storage disease; Transplantation

Indexed keywords

BETA GLUCURONIDASE; MYELOABLATIVE AGENT;

ADOPTIVE TRANSFER; ANIMAL CELL; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BODY DISTRIBUTION; CELL ISOLATION; CELL LINEAGE; CHEMICAL ANALYSIS; CONTROLLED STUDY; DRUG EFFICACY; ENZYME RELEASE; GENE OVEREXPRESSION; HEMATOPOIETIC CELL; HISTOCHEMISTRY; IMMUNOSUPPRESSIVE TREATMENT; IN VIVO STUDY; LIVER; LYMPHOCYTE ACTIVATION; LYMPHOCYTE COUNT; LYSOSOME STORAGE DISEASE; MACROPHAGE; MESENTERY LYMPH NODE; MOUSE; NONHUMAN; NONVIRAL GENE DELIVERY SYSTEM; PERIPHERAL LYMPHOCYTE; SMALL INTESTINE; SPLEEN; T LYMPHOCYTE; THYMUS;

ANIMALIA; MURINAE;

EID: 0037221905     PISSN: 15250016     EISSN: None     Source Type: Journal    
DOI: 10.1016/S1525-0016(02)00016-5     Document Type: Article

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