Co-expression of mutated and normal adrenoleukodystrophy protein reduces protein function: Implications for gene therapy of X-linked adrenoleukodystrophy

Human Molecular Genetics

Volumn 9, Issue 18, 2000, Pages 2609-2616

  Unterrainer, Gertraud ^a   Molzer, Brunhilde ^a   Forss Petter, Sonja ^a   Berger, Johannes ^a  

^a UNIVERSITY OF VIENNA   (Austria)

Author keywords

[No Author keywords available]

Indexed keywords

COMPLEMENTARY DNA; DOXYCYCLINE; MUTANT PROTEIN; VERY LONG CHAIN FATTY ACID;

ADRENOLEUKODYSTROPHY; ADULT; ARTICLE; CONTROLLED STUDY; FATTY ACID OXIDATION; FIBROBLAST; FLOW CYTOMETRY; GENE THERAPY; GENETIC TRANSFECTION; HELA CELL; HUMAN; HUMAN CELL; NUCLEOTIDE SEQUENCE; PEROXISOME; PRIORITY JOURNAL; PROTEIN BINDING; PROTEIN EXPRESSION; PROTEIN INDUCTION; PROTEIN LOCALIZATION; WESTERN BLOTTING; X CHROMOSOME LINKAGE;

EID: 0034327372     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/9.18.2609     Document Type: Article

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