Retroviral-mediated adrenoleukodystrophy-related gene transfer corrects very long chain fatty acid metabolism in adrenoleukodystrophy fibroblasts: Implications for therapy

FEBS Letters

Volumn 448, Issue 2-3, 1999, Pages 261-264

  Flavigny, Elise ^a   Sanhaj, Ahmed ^a   Aubourg, Patrick ^a   Cartier, Nathalie ^a  

^a INSERM   (France)

Author keywords

Adrenoleukodystrophy; ATP binding cassette transporter; Peroxisome

Indexed keywords

ABC TRANSPORTER; VERY LONG CHAIN FATTY ACID;

ADRENOLEUKODYSTROPHY; ARTICLE; CONTROLLED STUDY; GENE AMPLIFICATION; GENE TRANSFER; HUMAN; HUMAN CELL; IMMUNOCYTOCHEMISTRY; LIPOPROTEIN METABOLISM; PEROXISOME; POLYMERASE CHAIN REACTION; PRIORITY JOURNAL; SKIN FIBROBLAST;

ADRENOLEUKODYSTROPHY; ANIMALS; CELLS, CULTURED; FATTY ACIDS; FIBROBLASTS; GENE TRANSFER TECHNIQUES; HUMANS; IMMUNOHISTOCHEMISTRY; MICE; RETROVIRIDAE; TRANSDUCTION, GENETIC;

EID: 0032898425     PISSN: 00145793     EISSN: None     Source Type: Journal    
DOI: 10.1016/S0014-5793(99)00379-8     Document Type: Article

References (28)

1. Moser H.W. Brain. 120:1997;1485-1508.
2. Mosser J., Douar A.-M., Sarde C.-O., Kioschis P., Feil R., Moser H., Poustka A.-M., Mandel J.-L., Aubourg P. Nature. 361:1993;726-730.
3. Higgins C.F. Annu. Rev. Cell. Biol. 8:1992;67-113.
4. Lombard-Platet G., Savary S., Sarde C.O., Mandel J.L., Chimini G. Proc. Natl. Acad. Sci. USA. 93:1996;1265-1269.
5. Holzinger A., Kammerer S., Berger J., Roscher A.A. Biochem. Biophys. Res. Commun. 239:1997;261-264.
6. Kamijo K., Taketani S., Yokota S., Osumi T., Hashimoto T. J. Biol. Chem. 265:1990;4534-4540.
7. Gärtner J., Moser H., Valle D. Nat. Genet. 1:1992;16-23.
8. Holzinger A., Kammerer S., Roscher A.A. Biochem. Biophys. Res. Commun. 237:1997;152-157.
9. Shani N., Jimenez-Sanchez G., Steel G., Dean M., Valle D. Hum. Mol. Genet. 6:1997;1925-1931.
10. Shani N., Watkins P.A., Valle D. Proc. Natl. Acad. Sci. USA. 92:1995;6012-6016.
11. Hettema E.H., Van Roermund C.W.T., Distel B., Van den Berg M., Vilela C., Rodrigues-Pousada C., Wanders R.J.A., Tabak H.F. EMBO J. 15:1996;3813-3822.
12. Shani N., Valle D. Proc. Natl. Acad. Sci. USA. 93:1996;11901-11906.
13. Verleur N., Hettema E.H., Van Roermund C.W.T., Tabak H.F., Wanders R.J.A. Eur. J. Biochem. 249:1997;657-661.
14. Kobayashi T., Shinnoh N., Kondo A., Yamada T. Biochem. Biophys. Res. Commun. 232:1997;631-636.
15. Lu J.F., Lawler A.M., Watkins P.A., Powers J.M., Moser A.B., Moser H.W., Smith K.D. Proc. Natl. Acad. Sci. USA. 94:1997;9366-9371.
16. Forss-Petter S., Werner H., Berger J., Lassmann H., Molzer B., Schwab M.H., Bernheimer H., Zimmermann F., Nave K.-A. J. Neurosci. Res. 50:1997;829-843.
17. Troffer-Charlier N., Doerflinger N., Metzger E., Fouquet F., Mandel J.-L., Aubourg P. Eur. J. Cell. Biol. 75:1998;254-264.
18. Sarde C.O., Thomas J., Sadoulet H., Garnier J.M., Mandel J.-L. Mamm. Genome. 5:1994;810-813.
19. Cartier N., Lopez J., Moullier P., Rocchiccioli F., Rolland M.-O., Jorge P., Mosser J., Mandel J.-L., Bougnères P.-F., Danos O., Aubourg P. Proc. Natl. Acad. Sci. USA. 92:1995;1674-1678.
20. Mosser J., Lutz Y., Stoeckel M.E., Sarde C.O., Kretz C., Douar A.M., Lopez J., Aubourg P., Mandel J.L. Hum. Mol. Genet. 3:1994;265-271.
21. Doerflinger N., Miclea J.M., Lopez J., Chomienne C., Bougnères P., Aubourg P., Cartier N. Hum. Gene Ther. 9:1998;1025-1036.
22. Feigenbaum V., Lombard-Platet G., Guidoux S., Sarde C.O., Mandel J.L., Aubourg P. Am. J. Hum. Genet. 58:1996;1135-1144.
23. Cartier N., Sarde C.-O., Douar A.-M., Mosser J., Mandel J.-L., Aubourg P. Hum. Mol. Genet. 2:1993;1949-1951.
24. Kemp S., Wei H.M., Lu J.F., Braiterman L.T., McGuinness M.C., Moser A.B., Watkins P.A., Smith K.D. Nat. Med. 4:1998;1261-1268.
25. Fouquet F., Zhou J.M., Ralston E., Murray K., Troalen F., Magal E., Robain O., Dubois-Dalcq M., Aubourg P. Neurobiol. Dis. 3:1997;271-285.
26. Albet S., Causeret C., Bentejac M., Mandel J.L., Aubourg P., Maurice B. FEBS Lett. 405:1997;394-397.
27. Edgar A.D., Tomkiewicz C., Costet P., Legendre C., Aggerbeck M., Bouguet J., Staels B., Guyomard C., Pineau T., Barouki R. Toxicol. Lett. 98:1998;13-23.
28. Reddy J.K., Mannaerts G.P. Ann. Rev. Nutr. 14:1994;343-370.