Gene therapy for severe combined immunodeficiency caused by adenosine deaminase deficiency: Improved retroviral vectors for clinical trials

Acta Haematologica

Volumn 101, Issue 2, 1999, Pages 89-96

  Onodera, Masafumi ^a,b,c,d   Nelson, David M ^b   Sakiyama, Yukio ^a   Candotti, Fabio ^b   Blaese, R Michael ^b  

^a HOKKAIDO UNIVERSITY   (Japan)

^b NATIONAL HUMAN GENOME RESEARCH INSTITUTE   (United States)

^c JAPAN SCIENCE AND TECHNOLOGY AGENCY   (Japan)

^d UNIVERSITY OF TSUKUBA   (Japan)

Author keywords

Gene therapy; Retroviral vector; Severe combined immunodeficiency, adenosine deaminase; Stem cells, hematopoietic; T lymphocytes, peripheral

Indexed keywords

ADENOSINE DEAMINASE; VIRUS VECTOR;

CLINICAL TRIAL; COMBINED IMMUNODEFICIENCY; CONFERENCE PAPER; CONTROLLED CLINICAL TRIAL; CONTROLLED STUDY; ENZYME DEFICIENCY; GENE THERAPY; GENE TRANSFER; HEMATOPOIETIC STEM CELL; HUMAN; NONHUMAN; PRIORITY JOURNAL; RETROVIRUS; T LYMPHOCYTE;

EID: 0032958538     PISSN: 00015792     EISSN: None     Source Type: Journal    
DOI: 10.1159/000040930     Document Type: Conference Paper

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