Hepatic gene therapy using adeno-associated virus vectors

Seminars in Liver Disease

Volumn 19, Issue 1, 1999, Pages 61-69

  Patijn, Gijsbert A ^a   Kay, Mark A ^b  

^a LEIDEN UNIVERSITY MEDICAL CENTER   (Netherlands)

^b STANFORD UNIVERSITY SCHOOL OF MEDICINE   (United States)

Author keywords

Adeno associated virus; Gene therapy; Genetic diseases; Hemophilia

Indexed keywords

ADENO ASSOCIATED VIRUS; ENZYME DEFICIENCY; EXPRESSION VECTOR; GENE THERAPY; GENE TRANSFER; GENETIC DISORDER; GENETIC TRANSDUCTION; HEMOPHILIA; HUMAN; LIVER DISEASE; NONHUMAN; PRIORITY JOURNAL; REVIEW; SAFETY; VIRUS RECOMBINANT;

EID: 0032896334     PISSN: 02728087     EISSN: None     Source Type: Journal    
DOI: 10.1055/s-2007-1007098     Document Type: Review

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