-
2
-
-
0024529259
-
Mortality and causes of death in Dutch hemophiliacs, 1973-1986
-
Rosendaal FR, Varekamp I, Smith C, Brocker-Vriends AHJT, van Dijck H, Vandenbroucke JP, Hermans J, Suurmeijer TPMB, Briet E. Mortality and causes of death in Dutch hemophiliacs, 1973-1986. Br J Haematology. 1989;71:71-76.
-
(1989)
Br J Haematology
, vol.71
, pp. 71-76
-
-
Rosendaal, F.R.1
Varekamp, I.2
Smith, C.3
Brocker-Vriends, A.H.J.T.4
Van Dijck, H.5
Vandenbroucke, J.P.6
Hermans, J.7
Suurmeijer, T.P.M.B.8
Briet, E.9
-
3
-
-
0029121927
-
Some aspects on the management of hemophilia
-
Aledort LM. Some aspects on the management of hemophilia. Thromb Haemost. 1995;74:440-443.
-
(1995)
Thromb Haemost
, vol.74
, pp. 440-443
-
-
Aledort, L.M.1
-
4
-
-
0031955272
-
Prophylactic use of factor VIII: An economic evaluation
-
Bohn RL, Avom J, Glynn RJ, Choodnovskiy I, Haschemeyer R, Aledort LM. Prophylactic use of Factor VIII: an economic evaluation. Thromb Haemost. 1998;79:932-937.
-
(1998)
Thromb Haemost
, vol.79
, pp. 932-937
-
-
Bohn, R.L.1
Avom, J.2
Glynn, R.J.3
Choodnovskiy, I.4
Haschemeyer, R.5
Aledort, L.M.6
-
5
-
-
0031984425
-
Dominant C2 domain epitope specificity of inhibitor antibodies elicited by a heat pasteurized product, factor VIII CPS-P, in previously treated hemophilia A patients without inhibitors
-
Sawamoto Y, Prescott R, Zhong D, Saenko EL, Nauser-Bunschoten E, Peerlinck K, van den Berg M, Scandella D. Dominant C2 domain epitope specificity of inhibitor antibodies elicited by a heat pasteurized product, factor VIII CPS-P, in previously treated hemophilia A patients without inhibitors. Thromb Haemost. 1998;79:62-68.
-
(1998)
Thromb Haemost
, vol.79
, pp. 62-68
-
-
Sawamoto, Y.1
Prescott, R.2
Zhong, D.3
Saenko, E.L.4
Nauser-Bunschoten, E.5
Peerlinck, K.6
Van Den Berg, M.7
Scandella, D.8
-
6
-
-
0029850534
-
Complete short-term correction of canine hemophilia A by in vivo gene therapy
-
Connelly S, Mount J, Mauser A, Gardner JM, Kaleko M, McClelland A, Lothrop CD Jr. Complete short-term correction of canine hemophilia A by in vivo gene therapy. Blood. 1996;88:3846-3853.
-
(1996)
Blood
, vol.88
, pp. 3846-3853
-
-
Connelly, S.1
Mount, J.2
Mauser, A.3
Gardner, J.M.4
Kaleko, M.5
McClelland, A.6
Lothrop C.D., Jr.7
-
7
-
-
0030797290
-
Gene therapy for hemophilia A
-
Connelly S and Kaleko M. Gene therapy for hemophilia A. Thromb Haemost. 1997;78:31-36.
-
(1997)
Thromb Haemost
, vol.78
, pp. 31-36
-
-
Connelly, S.1
Kaleko, M.2
-
8
-
-
0002542902
-
Retroviral vectors
-
T. Friedmann, ed. Cold Spring Harbor, NY: Cold Spring Harbor Laboratory Press
-
Yee JK. Retroviral vectors. In: T. Friedmann, ed. The Development of Human Gene Therapy. Cold Spring Harbor, NY: Cold Spring Harbor Laboratory Press, 1999:21-45.
-
(1999)
The Development of Human Gene Therapy
, pp. 21-45
-
-
Yee, J.K.1
-
9
-
-
0028403237
-
Viral vector systems for gene therapy
-
Jolly DJ. Viral vector systems for gene therapy. Cancer Gene Ther. 1994;1:51-64.
-
(1994)
Cancer Gene Ther
, vol.1
, pp. 51-64
-
-
Jolly, D.J.1
-
10
-
-
0028229147
-
Inactivation of E2a in recombinant adenoviruses improves the prospect for gene therapy in cystic fibrosis
-
Yang Y, Nunes FA, Berencsi K, Gonczol E, Engelhardt JF, Wilson JM. Inactivation of E2a in recombinant adenoviruses improves the prospect for gene therapy in cystic fibrosis. Nat Genet. 1994;7:362-369.
-
(1994)
Nat Genet
, vol.7
, pp. 362-369
-
-
Yang, Y.1
Nunes, F.A.2
Berencsi, K.3
Gonczol, E.4
Engelhardt, J.F.5
Wilson, J.M.6
-
11
-
-
0027735897
-
Adenovirus-mediated transfer of the CFTR gene to lung of nonhuman primates: Toxicity study
-
Simon RH, Engelhardt JF, Yang Y, Zepeda M, Weber-Pendleton S, Grossman M, Wilson JM. Adenovirus-mediated transfer of the CFTR gene to lung of nonhuman primates: toxicity study. Hum Gene Ther. 1993;4:771-780.
-
(1993)
Hum Gene Ther
, vol.4
, pp. 771-780
-
-
Simon, R.H.1
Engelhardt, J.F.2
Yang, Y.3
Zepeda, M.4
Weber-Pendleton, S.5
Grossman, M.6
Wilson, J.M.7
-
12
-
-
16944364983
-
Anti-vector immunoglobulin induced by retroviral vectors
-
McCormack JE, Martineau D, DePolo N, Maifert S, Akbarian L, Townsend K, Lee W, Irwin M, Sajjadi N, Jolly DJ, Warner JF. Anti-vector immunoglobulin induced by retroviral vectors. Hum Gene Ther. 1997;8:1263-1273.
-
(1997)
Hum Gene Ther
, vol.8
, pp. 1263-1273
-
-
McCormack, J.E.1
Martineau, D.2
DePolo, N.3
Maifert, S.4
Akbarian, L.5
Townsend, K.6
Lee, W.7
Irwin, M.8
Sajjadi, N.9
Jolly, D.J.10
Warner, J.F.11
-
13
-
-
0032253230
-
Increased gene transfer into human CD34+ progenitor cells using retroviral vectors produced by a canine packaging cell line
-
Bauer G, Sauter S, Ibanez C, Rice CR, Valdez P, Jolly D, Kohn DB. Increased gene transfer into human CD34+ progenitor cells using retroviral vectors produced by a canine packaging cell line. Biol Blood Marrow Transplant. 1998;4:119-127.
-
(1998)
Biol Blood Marrow Transplant
, vol.4
, pp. 119-127
-
-
Bauer, G.1
Sauter, S.2
Ibanez, C.3
Rice, C.R.4
Valdez, P.5
Jolly, D.6
Kohn, D.B.7
-
14
-
-
0001510665
-
Human gene marker/therapy protocols
-
Editorial
-
Human gene marker/therapy protocols. Hum Gene Ther. 1998;9:1803-1847. Editorial.
-
(1998)
Hum Gene Ther
, vol.9
, pp. 1803-1847
-
-
-
15
-
-
0028334389
-
Characterization of replication-competent retroviruses from nonhuman primates with virus-induced T-cell lymphomas and observations regarding the mechanism of oncogenesis
-
Vanin EF, Kaloss M, Broscius C, Nienhuis AW. Characterization of replication-competent retroviruses from nonhuman primates with virus-induced T-cell lymphomas and observations regarding the mechanism of oncogenesis. J Virol. 1994;68:4241-4250.
-
(1994)
J Virol
, vol.68
, pp. 4241-4250
-
-
Vanin, E.F.1
Kaloss, M.2
Broscius, C.3
Nienhuis, A.W.4
-
16
-
-
0028805939
-
Development and analysis of retroviral vectors expressing human factor VIII as a potential gene therapy for hemophilia a
-
Chuah MKL, Vandendriessche T, Morgan RA. Development and analysis of retroviral vectors expressing human factor VIII as a potential gene therapy for hemophilia A. Hum Gene Ther. 1995;6:1363-1377.
-
(1995)
Hum Gene Ther
, vol.6
, pp. 1363-1377
-
-
Chuah, M.K.L.1
Vandendriessche, T.2
Morgan, R.A.3
-
17
-
-
0029098922
-
Sequences within the coding regions of clotting factor VIII and CFTR block transcriptional elongation
-
Koeberl DD, Halbert CL, Krumm A, Miller AD. Sequences within the coding regions of clotting factor VIII and CFTR block transcriptional elongation. Hum Gene Ther. 1995;6:469-479.
-
(1995)
Hum Gene Ther
, vol.6
, pp. 469-479
-
-
Koeberl, D.D.1
Halbert, C.L.2
Krumm, A.3
Miller, A.D.4
-
18
-
-
0028917478
-
Expression of blood clotting factor VIII cDNA is repressed by a transcriptional silencer located in its coding region
-
Hoeben RC, Fallaux FJ, Cramer SJ, van den Wollenberg DJM, van Ormondt H, Briet E, van der Eb AJ. Expression of blood clotting factor VIII cDNA is repressed by a transcriptional silencer located in its coding region. Blood. 1995;85:2447-2454.
-
(1995)
Blood
, vol.85
, pp. 2447-2454
-
-
Hoeben, R.C.1
Fallaux, F.J.2
Cramer, S.J.3
Van Den Wollenberg, D.J.M.4
Van Ormondt, H.5
Briet, E.6
Van Der Eb, A.J.7
-
19
-
-
0027237331
-
Sequences in the coding region of clotting factor VIII act as dominant inhibitors of RNA accumulation and protein production
-
Lynch CM, Israel DI, Kaufman RJ, Miller AD. Sequences in the coding region of clotting factor VIII act as dominant inhibitors of RNA accumulation and protein production. Hum Gene Ther. 1993;4:259-272.
-
(1993)
Hum Gene Ther
, vol.4
, pp. 259-272
-
-
Lynch, C.M.1
Israel, D.I.2
Kaufman, R.J.3
Miller, A.D.4
-
20
-
-
0030070191
-
Sensitization of cells and retroviruses to human serum by (alpha 1-3) galactosyltransferase
-
Takeuchi Y, Porter CD, Strahan KM, Preece AF, Gustafsson K, Cosset FL, Weiss RA, Collins MK. Sensitization of cells and retroviruses to human serum by (alpha 1-3) galactosyltransferase. Nature. 1996;379:85-88.
-
(1996)
Nature
, vol.379
, pp. 85-88
-
-
Takeuchi, Y.1
Porter, C.D.2
Strahan, K.M.3
Preece, A.F.4
Gustafsson, K.5
Cosset, F.L.6
Weiss, R.A.7
Collins, M.K.8
-
21
-
-
0029880213
-
A novel human amphotropic packaging cell line: High titer, complement resistance, and improved safety
-
Rigg RJ, Chen J, Dando JS, Forestell SP, Plavec I, Bohnlein E. A novel human amphotropic packaging cell line: high titer, complement resistance, and improved safety. Virology. 1996;218:290-295.
-
(1996)
Virology
, vol.218
, pp. 290-295
-
-
Rigg, R.J.1
Chen, J.2
Dando, J.S.3
Forestell, S.P.4
Plavec, I.5
Bohnlein, E.6
-
22
-
-
85025388994
-
Canine hemophilia: Observations on the course, the clotting anomaly, and the effect of blood transfusions
-
Graham JB, Buckwalter JA, Hartley LJ, Brinkhous KM. Canine hemophilia: observations on the course, the clotting anomaly, and the effect of blood transfusions. J Exp Med. 1949;90:97-106.
-
(1949)
J Exp Med
, vol.90
, pp. 97-106
-
-
Graham, J.B.1
Buckwalter, J.A.2
Hartley, L.J.3
Brinkhous, K.M.4
-
23
-
-
0019973659
-
A canine model of hemophilic (Factor VIII:C deficiency) bleeding
-
Giles AR, Tinlin S, Greenwood R. A canine model of hemophilic (Factor VIII:C deficiency) bleeding. Blood. 1982;60:727-732.
-
(1982)
Blood
, vol.60
, pp. 727-732
-
-
Giles, A.R.1
Tinlin, S.2
Greenwood, R.3
-
24
-
-
0022649896
-
Evaluation of the cuticle bleeding time in canine haemophilia A
-
Pijnappels MI, Briet E, van der Zwet GT, Huisden R, van Tilburg NH, Eulderink F. Evaluation of the cuticle bleeding time in canine haemophilia A. Thromb Haemost. 1986;55:70-73.
-
(1986)
Thromb Haemost
, vol.55
, pp. 70-73
-
-
Pijnappels, M.I.1
Briet, E.2
Van Der Zwet, G.T.3
Huisden, R.4
Van Tilburg, N.H.5
Eulderink, F.6
-
25
-
-
0029011723
-
Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A
-
Bi L, Lawler AM, Antonarakis SE, High KA, Gearhart JD, Kazazian HH Jr. Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A. Nat Genet. 1995;10:119-121.
-
(1995)
Nat Genet
, vol.10
, pp. 119-121
-
-
Bi, L.1
Lawler, A.M.2
Antonarakis, S.E.3
High, K.A.4
Gearhart, J.D.5
Kazazian H.H., Jr.6
-
26
-
-
0031884476
-
The canine factor VIII cDNA and 5′ flanking sequence
-
Cameron C, Notley C, Hoyle S, McGlynn L, Hough C, Kamisue S, Giles A, Lillicrap D. The canine factor VIII cDNA and 5′ flanking sequence. Thromb Haemost. 1998;79:317-322.
-
(1998)
Thromb Haemost
, vol.79
, pp. 317-322
-
-
Cameron, C.1
Notley, C.2
Hoyle, S.3
McGlynn, L.4
Hough, C.5
Kamisue, S.6
Giles, A.7
Lillicrap, D.8
-
27
-
-
0027196024
-
Sequence of the murine factor VIII cDNA
-
Elder B, Lakich D, Gitschier J. Sequence of the murine factor VIII cDNA. Genomics. 1993;16:374-379.
-
(1993)
Genomics
, vol.16
, pp. 374-379
-
-
Elder, B.1
Lakich, D.2
Gitschier, J.3
-
28
-
-
0027434516
-
An improved retroviral vector for assaying promoter activity. Analysis of promoter interference in pIP211 vector
-
Nakajima K, Ikenaka K, Nakahira K, Morita N, Mikoshiba K. An improved retroviral vector for assaying promoter activity. Analysis of promoter interference in pIP211 vector. FEBS Lett. 1993;315:129-133.
-
(1993)
FEBS Lett
, vol.315
, pp. 129-133
-
-
Nakajima, K.1
Ikenaka, K.2
Nakahira, K.3
Morita, N.4
Mikoshiba, K.5
-
29
-
-
0031803564
-
Generation of a conditionally neo(r)-containing retroviral producer cell line: Effects of neo(r) on retroviral titer and transgene expression
-
Wildner O, Candotti F, Krecko EG, Xanthopoulos KG, Ramsey WJ, Blaese RM. Generation of a conditionally neo(r)-containing retroviral producer cell line: effects of neo(r) on retroviral titer and transgene expression. Gene Ther. 1998;5:684-691.
-
(1998)
Gene Ther
, vol.5
, pp. 684-691
-
-
Wildner, O.1
Candotti, F.2
Krecko, E.G.3
Xanthopoulos, K.G.4
Ramsey, W.J.5
Blaese, R.M.6
-
30
-
-
0028129054
-
Expression of the neomycin-resistance (neo) gene induces alteration in gene expression and metabolism
-
Valera A, Perales JC, Hatzglou M, Bosch F Expression of the neomycin-resistance (neo) gene induces alteration in gene expression and metabolism. Hum Gene Ther. 1994;5:449-456.
-
(1994)
Hum Gene Ther
, vol.5
, pp. 449-456
-
-
Valera, A.1
Perales, J.C.2
Hatzglou, M.3
Bosch, F.4
-
31
-
-
17344364609
-
Strong immunogenic potential of a B7 retroviral expression vector: Generation of HLA-B7-restricted CTL response against selectable marker genes
-
Jung D, Jaeger E, Cayeux S, Blankenstein T, Hilmes C, Karbach J, Moebius U, Knuth A, Huber C, Seliger B. Strong immunogenic potential of a B7 retroviral expression vector: generation of HLA-B7-restricted CTL response against selectable marker genes. Hum Gene Ther. 1998;9:53-62.
-
(1998)
Hum Gene Ther
, vol.9
, pp. 53-62
-
-
Jung, D.1
Jaeger, E.2
Cayeux, S.3
Blankenstein, T.4
Hilmes, C.5
Karbach, J.6
Moebius, U.7
Knuth, A.8
Huber, C.9
Seliger, B.10
-
32
-
-
0030881446
-
A simple and reliable method for screening retroviral producer clones without selectable markers
-
Onodera M, Yachie A, Nelson DM, Wilchin H, Morgan RA, Blaese RM. A simple and reliable method for screening retroviral producer clones without selectable markers. Hum Gene Ther. 1997;8:1189-1194.
-
(1997)
Hum Gene Ther
, vol.8
, pp. 1189-1194
-
-
Onodera, M.1
Yachie, A.2
Nelson, D.M.3
Wilchin, H.4
Morgan, R.A.5
Blaese, R.M.6
-
33
-
-
0029741737
-
Rapid retrovirus titration using competitive polymerase chain reaction
-
Tafuro S, Zentilin L, Falaschi A, Giacca M. Rapid retrovirus titration using competitive polymerase chain reaction. Gene Ther. 1996;3:679-684.
-
(1996)
Gene Ther
, vol.3
, pp. 679-684
-
-
Tafuro, S.1
Zentilin, L.2
Falaschi, A.3
Giacca, M.4
-
34
-
-
4243893370
-
Sustained high level factor VIII antigen expression in immune-competent rabbits following peripheral intravenous injection of retroviral vector
-
Greengard JS, Bodner M, McCormack J, Edwards WE, Sensintaffar JL, Hsu D, DePolo NJ, Mittlestaedt D, de la Vega Jr. DJ, Brumm D, Jolly DJ, Chang SMW. Sustained high level factor VIII antigen expression in immune-competent rabbits following peripheral intravenous injection of retroviral vector. Blood. 1996;88:273a.
-
(1996)
Blood
, vol.88
-
-
Greengard, J.S.1
Bodner, M.2
McCormack, J.3
Edwards, W.E.4
Sensintaffar, J.L.5
Hsu, D.6
DePolo, N.J.7
Mittlestaedt, D.8
De La Vega D.J., Jr.9
Brumm, D.10
Jolly, D.J.11
Chang, S.M.W.12
-
35
-
-
0009467483
-
Sustained high level factor VIII antigen expression in immune-competent rabbits and dogs following peripheral intravenous injection of retroviral vector
-
Greengard JS, Bodner M, McCormack J, Edwards WE, Sensintaffar JL, Hsu D, DePolo NJ, Mittlestaedt D, de la Vega Jr. DJ, Brumm D, Jolly DJ, Chang SMW. Sustained high level factor VIII antigen expression in immune-competent rabbits and dogs following peripheral intravenous injection of retroviral vector. Thromb Haemost. 1997;78:3.
-
(1997)
Thromb Haemost
, vol.78
, pp. 3
-
-
Greengard, J.S.1
Bodner, M.2
McCormack, J.3
Edwards, W.E.4
Sensintaffar, J.L.5
Hsu, D.6
DePolo, N.J.7
Mittlestaedt, D.8
De La Vega D.J., Jr.9
Brumm, D.10
Jolly, D.J.11
Chang, S.M.W.12
-
36
-
-
0029943193
-
Sustained expression of therapeutic levels of human factor VIII in mice
-
Connelly S, Gardner JM, Lyons RM, McClelland A, Kaleko M. Sustained expression of therapeutic levels of human factor VIII in mice. Blood. 1996:87:4671-4677.
-
(1996)
Blood
, vol.87
, pp. 4671-4677
-
-
Connelly, S.1
Gardner, J.M.2
Lyons, R.M.3
McClelland, A.4
Kaleko, M.5
-
37
-
-
0028991820
-
In vivo delivery and expression of physiological levels of functional human factor VIII in mice
-
Connelly S, Smith TAG, Dhir G, Gardner JM, Mehaffey MG, Zaret KS, McClelland A, Kaleko M. In vivo delivery and expression of physiological levels of functional human factor VIII in mice. Hum Gene Ther. 1995;6:185-193.
-
(1995)
Hum Gene Ther
, vol.6
, pp. 185-193
-
-
Connelly, S.1
Smith, T.A.G.2
Dhir, G.3
Gardner, J.M.4
Mehaffey, M.G.5
Zaret, K.S.6
McClelland, A.7
Kaleko, M.8
-
38
-
-
0028842288
-
Gene therapy for hemophilia A: Production of therapeutic levels of human factor VIII in vivo in mice
-
Dwarki VJ, Belloni P, Nijjar T, Smith J, Cuoto L, Rabier M, Clift S, Berns A, Cohen LK. Gene therapy for hemophilia A: production of therapeutic levels of human factor VIII in vivo in mice. Proc Natl Acad Sci USA. 1995;92:1023-1027.
-
(1995)
Proc Natl Acad Sci USA
, vol.92
, pp. 1023-1027
-
-
Dwarki, V.J.1
Belloni, P.2
Nijjar, T.3
Smith, J.4
Cuoto, L.5
Rabier, M.6
Clift, S.7
Berns, A.8
Cohen, L.K.9
-
39
-
-
0030069229
-
High-level tissue-specific expression of functional human factor VIII in mice
-
Connelly S, Gardner JM, McClelland A, Kaleko M. High-level tissue-specific expression of functional human factor VIII in mice. Hum Gene Ther. 1996;7:183-195.
-
(1996)
Hum Gene Ther
, vol.7
, pp. 183-195
-
-
Connelly, S.1
Gardner, J.M.2
McClelland, A.3
Kaleko, M.4
-
40
-
-
0031424112
-
Biosynthesis, assembly and secretion of coagulation factor VIII
-
Kaufman RJ, Pipe SW, Tagliavacca L, Swaroop M, Moussalli M. Biosynthesis, assembly and secretion of coagulation factor VIII. Blood Coagul Fibrinolysis. 1997;2:3-14.
-
(1997)
Blood Coagul Fibrinolysis
, vol.2
, pp. 3-14
-
-
Kaufman, R.J.1
Pipe, S.W.2
Tagliavacca, L.3
Swaroop, M.4
Moussalli, M.5
-
41
-
-
0032478548
-
Mutations in the ER-Golgi intermediate compartment protein ERGIC-53 cause combined deficiency of coagulation factors V and VIII
-
Nichols WC, Seligsohn U, Zivelin A, Terry VH, Hertel CE, Wheatley MA, Moussalli MJ, Hauri HP, Ciavarella N, Kaufman RJ, Ginsburg D. Mutations in the ER-Golgi intermediate compartment protein ERGIC-53 cause combined deficiency of coagulation factors V and VIII Cell. 1998;93:61-70.
-
(1998)
Cell
, vol.93
, pp. 61-70
-
-
Nichols, W.C.1
Seligsohn, U.2
Zivelin, A.3
Terry, V.H.4
Hertel, C.E.5
Wheatley, M.A.6
Moussalli, M.J.7
Hauri, H.P.8
Ciavarella, N.9
Kaufman, R.J.10
Ginsburg, D.11
-
42
-
-
0026534020
-
Toward gene therapy in haemophilia a: Retrovirus-mediated transfer of factor VIII gene into murine haematopoeitic progenitor cells
-
Hoeben RC, Einerhand MPW, Briet E, van Ormondt H, Valerio D, van der Eb AJ. Toward gene therapy in haemophilia A: retrovirus-mediated transfer of factor VIII gene into murine haematopoeitic progenitor cells. Thromb Haemost. 1992;67:341-345.
-
(1992)
Thromb Haemost
, vol.67
, pp. 341-345
-
-
Hoeben, R.C.1
Einerhand, M.P.W.2
Briet, E.3
Van Ormondt, H.4
Valerio, D.5
Van Der Eb, A.J.6
-
43
-
-
0027283419
-
Toward gene therapy for hemophilia A: Long-term persistence of factor VIII-secreting fibroblasts after transplantation into immunodeficient mice
-
Hoeben RC, Fallaux FJ, van Tilburg NH, Cramer SJ, van Ormondt H, Briet E, van der Eb AJ. Toward gene therapy for hemophilia A: long-term persistence of factor VIII-secreting fibroblasts after transplantation into immunodeficient mice. Hum Gene Ther. 1993;4:179-186.
-
(1993)
Hum Gene Ther
, vol.4
, pp. 179-186
-
-
Hoeben, R.C.1
Fallaux, F.J.2
Van Tilburg, N.H.3
Cramer, S.J.4
Van Ormondt, H.5
Briet, E.6
Van Der Eb, A.J.7
-
44
-
-
0032501988
-
Bone marrow stromal cells as targets for gene therapy of hemophilia A
-
Chuah MKL, Brems H, Vanslembrouke V, Collen D, Vandendriessche T. Bone marrow stromal cells as targets for gene therapy of hemophilia A. Hum Gene Ther. 1998;9:353-365.
-
(1998)
Hum Gene Ther
, vol.9
, pp. 353-365
-
-
Chuah, M.K.L.1
Brems, H.2
Vanslembrouke, V.3
Collen, D.4
Vandendriessche, T.5
-
45
-
-
16944363593
-
Systemic delivery of human growth hormone or human factor IX in dogs by reintroduced genetically modified autologous bone marrow stromal cells
-
Hurwitz DR, Kirchgesser M, Merrill W, Galanopoulos T, McGrath CA, Emami S, Hansen M, Cherington V, Appel JM, Bizinkauskas CB, Brackmann HH, Levine PH, Greenberger JS. Systemic delivery of human growth hormone or human factor IX in dogs by reintroduced genetically modified autologous bone marrow stromal cells. Hum Gene Ther. 1997;8:137-156.
-
(1997)
Hum Gene Ther
, vol.8
, pp. 137-156
-
-
Hurwitz, D.R.1
Kirchgesser, M.2
Merrill, W.3
Galanopoulos, T.4
McGrath, C.A.5
Emami, S.6
Hansen, M.7
Cherington, V.8
Appel, J.M.9
Bizinkauskas, C.B.10
Brackmann, H.H.11
Levine, P.H.12
Greenberger, J.S.13
-
46
-
-
0009469728
-
Ex vivo gene therapy of hemophilia A and B using bone marrow stromal cells in a canine model
-
American Society Gene Therapy
-
Hurwitz DR, Cherington V, Rubin H, Wang T, Sobolewski J, Galanopoulos T, Natale A, McGrath CA, Levine PH, Greenberger JS, Chiang GG. Ex vivo gene therapy of hemophilia A and B using bone marrow stromal cells in a canine model. In: Proceedings. American Society Gene Therapy. 1998;3.
-
(1998)
Proceedings
, vol.3
-
-
Hurwitz, D.R.1
Cherington, V.2
Rubin, H.3
Wang, T.4
Sobolewski, J.5
Galanopoulos, T.6
Natale, A.7
McGrath, C.A.8
Levine, P.H.9
Greenberger, J.S.10
Chiang, G.G.11
-
47
-
-
0032510756
-
Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia A
-
Evans GL, Morgan RA. Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia A. Proc Natl Acad Sci USA. 1998;95:5734-5739.
-
(1998)
Proc Natl Acad Sci USA
, vol.95
, pp. 5734-5739
-
-
Evans, G.L.1
Morgan, R.A.2
-
48
-
-
4243963580
-
Correction of factor VIII deficiency in a murine model for hemophilia A through transplant of factor VIII-expressing skin
-
Fakharzadeh SS, Zhang Y, Sarkar R, Kazazian HH. Correction of factor VIII deficiency in a murine model for hemophilia A through transplant of factor VIII-expressing skin. Blood. 1998;92:297a.
-
(1998)
Blood
, vol.92
-
-
Fakharzadeh, S.S.1
Zhang, Y.2
Sarkar, R.3
Kazazian, H.H.4
-
49
-
-
0031829489
-
Direct synovial gene transfer with retroviral vectors in rat adjuvant arthritis
-
Nguyen KH, Boyle DL, McCormack JE, Chada S, Jolly DJ, Firestein GS. Direct synovial gene transfer with retroviral vectors in rat adjuvant arthritis. J Rheumatol. 1998;25:1118-1125.
-
(1998)
J Rheumatol
, vol.25
, pp. 1118-1125
-
-
Nguyen, K.H.1
Boyle, D.L.2
McCormack, J.E.3
Chada, S.4
Jolly, D.J.5
Firestein, G.S.6
-
50
-
-
0032505748
-
Generation of a systemic antitumor immune response with regional intratumoral injections of interferon γ retroviral vector
-
Karavodin LM, Robbins J, Chong K, Hsu D, Ibanez C, Mento S, Jolly DJ, Fong TC. Generation of a systemic antitumor immune response with regional intratumoral injections of interferon γ retroviral vector. Hum Gene Ther. 1998;9:2231-2241.
-
(1998)
Hum Gene Ther
, vol.9
, pp. 2231-2241
-
-
Karavodin, L.M.1
Robbins, J.2
Chong, K.3
Hsu, D.4
Ibanez, C.5
Mento, S.6
Jolly, D.J.7
Fong, T.C.8
-
51
-
-
0031458296
-
Human immunodeficiency virus immunotherapy using a retroviral vector
-
Warner JF, Jolly DJ, Merrit J. Human immunodeficiency virus immunotherapy using a retroviral vector. Curr Top Microbiol Immunol. 1998;226:145-160.
-
(1998)
Curr Top Microbiol Immunol
, vol.226
, pp. 145-160
-
-
Warner, J.F.1
Jolly, D.J.2
Merrit, J.3
-
52
-
-
0027686238
-
In vivo gene therapy of hemophilia B: Sustained partial correction in Factor IX deficient dogs
-
Kay MA, Rothenberg S, Landen CN, Bellinger DA, Leland F, Toman C, Finegold M, Thompson AR, Read MS, Brinkhous KM, Woo SLC. In vivo gene therapy of hemophilia B: sustained partial correction in Factor IX deficient dogs. Science. 1993;262:117-119.
-
(1993)
Science
, vol.262
, pp. 117-119
-
-
Kay, M.A.1
Rothenberg, S.2
Landen, C.N.3
Bellinger, D.A.4
Leland, F.5
Toman, C.6
Finegold, M.7
Thompson, A.R.8
Read, M.S.9
Brinkhous, K.M.10
Woo, S.L.C.11
-
53
-
-
0030819372
-
Genetic immunization with adeno-associated virus vectors expressing herpes simplex virus Type 2 glycoproteins B and D
-
Manning WC, Paliard X, Zhou S, Bland MP, Lee AY, Hong K, Walker CM, Escobedo JA, Dwarki V. Genetic immunization with adeno-associated virus vectors expressing herpes simplex virus Type 2 glycoproteins B and D. J Virol. 1993;71:7960-7962.
-
(1993)
J Virol
, vol.71
, pp. 7960-7962
-
-
Manning, W.C.1
Paliard, X.2
Zhou, S.3
Bland, M.P.4
Lee, A.Y.5
Hong, K.6
Walker, C.M.7
Escobedo, J.A.8
Dwarki, V.9
-
54
-
-
0000932019
-
Evaluation of adenoviral vectors for treatment of hemophilia A: Demonstration of an unexpected, non-linear in vivo dose response
-
Shirley PS, Gallo AM, Andrews JL, Smith TAG, Lillicrap D, Kaleko M, Connelly S. Evaluation of adenoviral vectors for treatment of hemophilia A: demonstration of an unexpected, non-linear in vivo dose response. Blood. 1998;92:296a.
-
(1998)
Blood
, vol.92
-
-
Shirley, P.S.1
Gallo, A.M.2
Andrews, J.L.3
Smith, T.A.G.4
Lillicrap, D.5
Kaleko, M.6
Connelly, S.7
-
55
-
-
0003303712
-
A role for whole blood clotting time as a sensitive screening test for F.VIII and F.IX replacement
-
Mustafa RL, Elwell DL, Russell KE, Nichols TC, Read MS. A role for whole blood clotting time as a sensitive screening test for F.VIII and F.IX replacement. Blood. 1998;92:96a.
-
(1998)
Blood
, vol.92
-
-
Mustafa, R.L.1
Elwell, D.L.2
Russell, K.E.3
Nichols, T.C.4
Read, M.S.5
-
56
-
-
0023567169
-
The development and characterisation of antibodies to human Factor VIII in haemophilic dogs
-
Littlewood JD, Barrowcliffe TW. The development and characterisation of antibodies to human Factor VIII in haemophilic dogs. Thromb Haemost. 1987;57:314-321.
-
(1987)
Thromb Haemost
, vol.57
, pp. 314-321
-
-
Littlewood, J.D.1
Barrowcliffe, T.W.2
-
57
-
-
0025279872
-
Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection
-
Miller DG, Adam MA, Miller AD. Gene transfer by retrovirus vectors occurs only in cells that are actively replicating at the time of infection. Mol Cell Biol. 1990;10:4239-4242.
-
(1990)
Mol Cell Biol
, vol.10
, pp. 4239-4242
-
-
Miller, D.G.1
Adam, M.A.2
Miller, A.D.3
-
58
-
-
0028261727
-
Transplantation of spleen cells in patients with hemophilia A: A report of 20 cases
-
Liu L, Xia S, Seifert J. Transplantation of spleen cells in patients with hemophilia A: a report of 20 cases. Transpl Int. 1994;7:201-206.
-
(1994)
Transpl Int
, vol.7
, pp. 201-206
-
-
Liu, L.1
Xia, S.2
Seifert, J.3
-
59
-
-
0023264494
-
Liver transplantation in hemophilia A
-
Bontempo FA, Lewis JH, Gorenc TJ, Spero JA, Ragni MV, Scott JP, Starzl TE. Liver transplantation in hemophilia A. Blood. 1987;69:1721-1724.
-
(1987)
Blood
, vol.69
, pp. 1721-1724
-
-
Bontempo, F.A.1
Lewis, J.H.2
Gorenc, T.J.3
Spero, J.A.4
Ragni, M.V.5
Scott, J.P.6
Starzl, T.E.7
-
60
-
-
0028290674
-
In vivo production of human factor VIII in mice after intrasplenic implantation of primary fibroblasts transfected by receptor-mediated, adenovirus-augmented gene delivery
-
Zatloukal K, Cotten M, Berger M, Schmidt W, Wagner E, Bimstiel ML. In vivo production of human factor VIII in mice after intrasplenic implantation of primary fibroblasts transfected by receptor-mediated, adenovirus-augmented gene delivery. Proc Natl Acad Sci USA. 1994;91:5148-5152.
-
(1994)
Proc Natl Acad Sci USA
, vol.91
, pp. 5148-5152
-
-
Zatloukal, K.1
Cotten, M.2
Berger, M.3
Schmidt, W.4
Wagner, E.5
Bimstiel, M.L.6
-
61
-
-
0032080179
-
Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy
-
Connelly S, Andrews JL, Gallo AM, Kayda DB, Qian J, Hoyer L, Kadan MJ, Gorziglia MI, Trapnell BC, McClelland A Kaleko M. Sustained phenotypic correction of murine hemophilia A by in vivo gene therapy. Blood. 1998;91:3272-3281.
-
(1998)
Blood
, vol.91
, pp. 3272-3281
-
-
Connelly, S.1
Andrews, J.L.2
Gallo, A.M.3
Kayda, D.B.4
Qian, J.5
Hoyer, L.6
Kadan, M.J.7
Gorziglia, M.I.8
Trapnell, B.C.9
McClelland, A.10
Kaleko, M.11
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