Recombinant human acid α-glucosidase: High level production in mouse milk, biochemical characteristics, correction of enzyme deficiency in GSDII KO mice

Human Molecular Genetics

Volumn 7, Issue 11, 1998, Pages 1815-1824

  Bijvoet, Agnes G A ^a,b   Kroos, Marian A ^a   Pieper, Frank R ^c   Van Der Vliet, Martin ^d   De Boer, Herman A ^e   Van Der Ploeg, Ans T ^b   Verbeet, Martin Ph ^e   Reuser, Arnold J J ^a  

^a ERASMUS UNIVERSITY ROTTERDAM   (Netherlands)

^b SOPHIA CHILDREN S HOSPITAL   (Netherlands)

^c Pharming Group NV   (Netherlands)

^d BioCell Technology   (Netherlands)

^e LEIDEN UNIVERSITY   (Netherlands)

Author keywords

[No Author keywords available]

Indexed keywords

ALPHA GLUCOSIDASE; SOMATOMEDIN B RECEPTOR;

AMINO TERMINAL SEQUENCE; ANIMAL TISSUE; ARTICLE; CHO CELL; ENZYME DEFICIENCY; FEMALE; FIBROBLAST; GENE FUSION; GLYCOGEN STORAGE DISEASE TYPE 2; HUMAN; MOLECULAR WEIGHT; MOUSE; NONHUMAN; PRIORITY JOURNAL; PROMOTER REGION; TRANSGENE; TRANSGENIC ANIMAL;

ALPHA-GLUCOSIDASES; ANIMALS; CATTLE; CHO CELLS; CRICETINAE; FEMALE; FIBROBLASTS; GLYCOGEN STORAGE DISEASE TYPE II; HUMANS; MAMMARY GLANDS, ANIMAL; MICE; MICE, KNOCKOUT; MICE, TRANSGENIC; MILK; RECOMBINANT PROTEINS; TRANSGENES;

ANIMALIA; BOVINAE;

EID: 0031716741     PISSN: 09646906     EISSN: None     Source Type: Journal    
DOI: 10.1093/hmg/7.11.1815     Document Type: Article

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