Expression of cDNA-encoded human acid α-glucosidase in milk of transgenic mice

Biochimica et Biophysica Acta - Gene Structure and Expression

Volumn 1308, Issue 2, 1996, Pages 93-96

  Bijvoet, Agnes G A ^a   Kroos, Marian A ^a   Pieper, Frank R ^b   De Boer, Herman A ^c   Reuser, Arnold J J ^a   Van Der Ploeg, Ans T ^a   Verbeet, Martin Ph ^c  

^a SOPHIA CHILDREN S HOSPITAL   (Netherlands)

^b Pharming Group NV   (Netherlands)

^c LEIDEN UNIVERSITY   (Netherlands)

Author keywords

Enzyme replacement therapy; Lysosomal storge disease; Recombinant enzyme

Indexed keywords

ALPHA GLUCOSIDASE; COMPLEMENTARY DNA; RECOMBINANT PROTEIN;

ARTICLE; ENZYME SYNTHESIS; FIBROBLAST; HUMAN; HUMAN CELL; LYSOSOME STORAGE DISEASE; MILK; MOUSE; NONHUMAN; PRIORITY JOURNAL; TRANSGENIC MOUSE;

EID: 0030583305     PISSN: 01674781     EISSN: None     Source Type: Journal    
DOI: 10.1016/0167-4781(96)00093-0     Document Type: Article

References (24)

1. [1] Hennighausen, L. (1992) J. Cell. Biochem. 49, 325-332.
2. [2] Lee, S.H. and de Boer, H.A. (1994) J. Control. Release 29, 213-221.
3. [3] Hirschhorn, R. (1995) in The metabolic and molecular bases of inherited disease Scriver (C.R., Beaudet, A.L., Sly, W.S. and Valle. D., Eds.), pp. 2443-2464.
4. [4] Van der Ploeg, A.T., Bolhuis, P.A., Wolterman, R.A., Visser, J.W., Loonen, M.C.B., Busch, H.F.M. and Reuser, A.J.J. (1988) J. Neurol. 235, 392-396.
5. [5] Van der Ploeg, A.T., Loonen, M.C.B., Bolhuis, P.A., Busch, H.M.F., Reuser. A.J.J. and Galjaard, H. (1988) Pediatr. Res. 24, 90-94.
6. [6] Van der Ploeg, A.T., Van der Kraaij, A.M.M., Willemsen, R., Kroos, M.A., Loonen, M.C.B., Koster, J.F. and Reuser. A.J.J. (1990) Pediatr. Res. 28, 344-347.
7. [7] Van der Ploeg, A.T., Kroos, M.A., Willemsen, R., Brons, N.H. and Reuser, A.J.J. (1991) J. Clin. Invest. 87, 513-518.
8. [8] Fuller, M., Van der Ploeg, A., Reuser, A.J.J., Anson, D.S. and Hopwood, J.J. (1995) Eur, J. Biochem. 234, 903-909.
9. [9] Van Hove, J.L.K., Wang. H.W., Wu. L-Y., Brady, R.O. and Chen, Y.-T. (1996) Proc. Natl. Acad. Sci. USA 93, 65-70.
10. [10] Kornfeld, S. (1992) Annu. Rev. Biochem. 61, 307-330.
11. [11] Sands, M.S., Vogler, C., Kyle, J.W., Grubb, J.H., Levy, B., Galvin, N., Sly, W.S. and Birkenmeier. E.H. (1994) J. Clin. Invest. 93. 2324-2331.
12. [12] Shull, R.M., Kakkis, E.D., McEntee, M.F., Kama, S.A., Jonas, A.J. and Neufeld, E.F. (1994) Proc. Natl. Acad. Sci. USA 91, 12937-12941.
13. [13] Brady, R.O. and Barton, N.W. (1994) Biochem. Med. Metab. Biol. 52, 1-9.
14. [14] Hoefsloot, L.H., Willemsen, R., Kroos, M.A., Hoogeveen-Westerveld, M., Hermans, M.M., Van der Ploeg, A.T., Oostra, B.A. and Reuser, A.J. (1990) Biochem. J. 272, 485-492.
15. [15] Meade, H., Gates, L., Lacy, E. and Lonberg, N. (1990) Bio/Technology 8, 443-446.
16. [16] Platenburg, G.J., Kootwijk, E.P.A., Kooiman, P.M., Woloshuk, S.L., Nuijens, J.H., Krimpenfort, P.J.A., Pieper, F.R., de Boer, H.A. and Strijker, R. (1994) Transgenic Res. 3, 99-108.
17. [17] Hogan, B., Beddington, R., Costantini, F. and Lacy, E. (1994) Manipulating the Mouse Embryo: A Laboratory Manual, 2nd. edn., Cold Spring Harbor Laboratory Press, Cold Spring Harbor.
18. [18] De Jonge, A.J.R., De Smit, S., Kroos, M.A. and Reuser, A.J.J. (1985) Hum. Genet. 69, 32-38.
19. [19] Reuser, A.J.J., Kroos, M., Oude Elferink, R.P.J. and Tager, J.M. (1985) J. Biol. Chem. 260, 8336-8341.
20. [20] Palmiter, R.D., Sandgren, E.P., Avarbock, M.R., Allen, D.D. and Brinster, R.L. (1991) Proc. Natl. Acad. Sci. USA 88, 478-482.
21. [21] Bijvoet, A.G.A., Kroos, M.A., Van de Kamp, E.H.M., Oostra, B.A., Verbeet, M.P., Van der Ploeg, A.T. and Reuser, A.J.J. (1995) Am. J. Hum. Genet, 57, A176.
22. [22] Konings, R.N.H., Luiten, R.G.M. and Peeters, B.P.H. (1986) Gene 46, 269-276.
23. [23] Choi, T., Huang, M., Gorman, C. and Jaenisch, R. (1991) Mol. Cell. Biol. 11, 3070-3074.
24. [24] Reuser, A.J.J., Kroos, M.A., Ponne, N.J., Wolterman, R.A., Loonen, M.C.B., Busch, H.F.M., Visser, W.J. and Bolhuis, P.A. (1984) Exp. Cell. Res. 155, 178-189.