Enzyme replacement therapy in a feline model of Maroteaux-Lamy syndrome

Journal of Clinical Investigation

Volumn 97, Issue 8, 1996, Pages 1864-1873

  Crawley, Allison C ^a   Brooks, Doug A ^a   Muller, Vivienne J ^a   Petersen, Birgit A ^a   Isaac, Elizabeth L ^a   Bielicki, Julie ^a   King, Barbara M ^a   Boulter, Christine D ^a   Moore, Alison J ^b   Fazzalari, Nick L ^b   Anson, Don S ^a   Byers, Sharon ^a   Hopwood, John J ^a  

^a WOMEN S AND CHILDREN S HOSPITAL   (Australia)

^b INSTITUTE OF MEDICAL AND VETERINARY SCIENCE   (Australia)

Author keywords

disease models, animal; dysostoses; genetics, medical; lysosomal storage diseases; mucopolysaccharidosis VI

Indexed keywords

N ACETYLGALACTOSAMINE 4 SULFATASE; RECOMBINANT PROTEIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ARTICLE; BONE MATURATION; BONE MINERALIZATION; CAT; DRUG CLEARANCE; DRUG DISTRIBUTION; DRUG EFFICACY; DRUG HALF LIFE; ENZYME REPLACEMENT; INTRAVENOUS DRUG ADMINISTRATION; MAROTEAUX LAMY SYNDROME; NONHUMAN; PRIORITY JOURNAL; TISSUE DISTRIBUTION; VERTEBRA;

EID: 15844392149     PISSN: 00219738     EISSN: None     Source Type: Journal    
DOI: 10.1172/JCI118617     Document Type: Article

References (44)

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