The burden, epidemiology, costs and treatment for Duchenne muscular dystrophy: An evidence review

Orphanet Journal of Rare Diseases

Volumn 12, Issue 1, 2017, Pages

  Ryder, S ^a   Leadley, R M ^a   Armstrong, N ^a   Westwood, M ^a   De Kock, S ^a   Butt, T ^b   Jain, M ^b   Kleijnen, J ^c  

^a KLEIJNEN SYSTEMATIC REVIEWS LTD   (United Kingdom)

^b BIOMARIN PHARMACEUTICAL INC   (United States)

^c MAASTRICHT UNIVERSITY   (Netherlands)

Author keywords

Burden; Cost; DMD; Duchenne; Epidemiology; Incidence; Prevalence

Indexed keywords

CORTICOSTEROID;

ASSISTED VENTILATION; CANADA; DISEASE COURSE; DISEASE SEVERITY; DUCHENNE MUSCULAR DYSTROPHY; FRANCE; HEALTH CARE COST; HEALTH CARE UTILIZATION; HUMAN; MORTALITY; MOTOR DYSFUNCTION; PHYSIOTHERAPY; PRACTICE GUIDELINE; PREVALENCE; QUALITY OF LIFE; REVIEW; SURVIVAL; SYSTEMATIC REVIEW; UNITED KINGDOM; UNITED STATES; COST OF ILLNESS; ECONOMICS; INCIDENCE;

ADRENAL CORTEX HORMONES; COST OF ILLNESS; HUMANS; INCIDENCE; MUSCULAR DYSTROPHY, DUCHENNE; PREVALENCE; QUALITY OF LIFE;

EID: 85018858970     PISSN: None     EISSN: 17501172     Source Type: Journal    
DOI: 10.1186/s13023-017-0631-3     Document Type: Review

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