Long term natural history data in ambulant boys with duchenne muscular dystrophy: 36-month changes

PLoS ONE

Volumn 9, Issue 10, 2014, Pages

  Pane, Marika ^a   Mazzone, Elena Stacy ^a   Sivo, Serena ^a   Sormani, Maria Pia ^b   Messina, Sonia ^c   D'Amico, Adele ^d   Carlesi, Adelina ^d   Vita, Gianluca ^c   Fanelli, Lavinia ^a   Berardinelli, Angela ^e   Torrente, Yvan ^f   Lanzillotta, Valentina ^g   Viggiano, Emanuela ^h   D'Ambrosio, Paola ^h   Cavallaro, Filippo ^c   Frosini, Silvia ⁱ   Barp, Andrea ^j   Bonfiglio, Serena ^k   Scalise, Roberta ^a   De Sanctis, Roberto ^a   Rolle, Enrica ^l   Graziano, Alessandra ^a   Magri, Francesca ^f   Palermo, Concetta ^a   Rossi, Francesca ⁿ   Donati, Maria Alice ^m   Sacchini, Michele ^m   Arnoldi, Maria Teresa ⁿ   Baranello, Giovanni ⁿ   Mongini, Tiziana ^l   Pini, Antonella ^k   Battini, Roberta ⁱ   Pegoraro, Elena ^j   Previtali, Stefano ^o   Bruno, Claudio ^g   Politano, Luisa ^h   Comi, Giacomo P ^f   Bertini, Enrico ^d   Mercuri, Eugenio ^a   more..

^a CATHOLIC UNIVERSITY   (Italy)

^b UNIVERSITY OF GENOA   (Italy)

^c UNIVERSITY OF MESSINA   (Italy)

^d BAMBINO GESÙ CHILDREN S HOSPITAL   (Italy)

^e C MONDINO NATIONAL NEUROLOGICAL INSTITUTE   (Italy)

^f Dino Ferrari Center   (Italy)

^g G GASLINI INSTITUTE   (Italy)

^h SECOND UNIVERSITY OF NAPLES   (Italy)

ⁱ DEPARTMENT OF DEVELOPMENTAL NEUROSCIENCE   (Italy)

^j UNIVERSITY OF PADOVA   (Italy)

^k MAGGIORE HOSPITAL   (Italy)

^l UNIVERSITY OF TURIN   (Italy)

^m UNIVERSITY OF FLORENCE   (Italy)

ⁿ DEPARTMENT OF NEUROSURGERY   (Italy)

^o SAN RAFFAELE HOSPITAL   (Italy)

more..

Author keywords

[No Author keywords available]

Indexed keywords

DEFLAZACORT; PREDNISONE;

AGE; ARTICLE; CHILD; DRUG INTERMITTENT THERAPY; DRUG RESPONSE; DUCHENNE MUSCULAR DYSTROPHY; FUNCTION TEST; FUNCTIONAL ASSESSMENT; HUMAN; LONGITUDINAL STUDY; MAJOR CLINICAL STUDY; MALE; MOTOR PERFORMANCE; MULTICENTER STUDY (TOPIC); OUTCOME ASSESSMENT; SIX MINUTE WALK TEST; STEROID THERAPY; CLINICAL TRIAL; DISEASE COURSE; EXERCISE TEST; ITALY; MULTICENTER STUDY; MUSCULAR DYSTROPHY, DUCHENNE; PRESCHOOL CHILD; TIME; WALKING;

CHILD; CHILD, PRESCHOOL; DISEASE PROGRESSION; EXERCISE TEST; HUMANS; ITALY; LONGITUDINAL STUDIES; MALE; MUSCULAR DYSTROPHY, DUCHENNE; OUTCOME ASSESSMENT (HEALTH CARE); TIME FACTORS; WALKING;

EID: 84907487779     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0108205     Document Type: Article

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