Erratum to Naïve induced pluripotent stem cells generated from β-thalassemia fibroblasts allow efficient gene correction with CRISPR/Cas9 (Stem Cells Translational Medicine, (2016) 5,(8-19), 10.5966/sctm.2015-0157;Naïve induced pluripotent stem cells generated from β-thalassemia fibroblasts allow efficient gene correction with CRISPR/Cas9

Stem Cells Translational Medicine

Volumn 5, Issue 1, 2016, Pages 8-19

  Yang, Yuanyuan ^a   Zhang, Xiaobai ^a   Yi, Li ^a   Hou, Zhenzhen ^a   Chen, Jiayu ^a   Kou, Xiaochen ^a   Zhao, Yanhong ^a   Wang, Hong ^a   Sun, Xiao Fang ^b   Jiang, Cizhong ^a   Wang, Yixuan ^a   Gao, Shaorong ^a  

^a TONGJI UNIVERSITY   (China)

^b GUANGZHOU MEDICAL UNIVERSITY   (China)

Author keywords

CRISPR Cas9; Gene correction; Na ve state; Reprogramming; Thalassemia patient

Indexed keywords

CRISPR ASSOCIATED PROTEIN; TRANSCRIPTION FACTOR;

ANIMAL MODEL; ARTICLE; BETA THALASSEMIA; CELL CULTURE; CELL DIFFERENTIATION; CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT; FIBROBLAST; FLOW CYTOMETRY; GENE EXPRESSION; GENETIC ANALYSIS; GENETIC ASSOCIATION; HEMATOPOIETIC CELL; HUMAN; HUMAN TISSUE; IMMUNOFLUORESCENCE; KARYOTYPING; MOUSE; MUTATION; NONHUMAN; NUCLEAR REPROGRAMMING; OXIDATIVE PHOSPHORYLATION; PHENOTYPE; PLURIPOTENT STEM CELL; POLYMERASE CHAIN REACTION; TARGETED GENE REPAIR; TERATOMA; ANIMAL; BETA-THALASSEMIA; CRISPR CAS SYSTEM; FEMALE; GENE THERAPY; GENETICS; INDUCED PLURIPOTENT STEM CELL; INSTITUTE FOR CANCER RESEARCH MOUSE; MALE; METABOLISM; PATHOLOGY; PROCEDURES;

ANIMALS; BETA-THALASSEMIA; CRISPR-CAS SYSTEMS; FEMALE; FIBROBLASTS; GENETIC THERAPY; HUMANS; INDUCED PLURIPOTENT STEM CELLS; MALE; MICE; MICE, INBRED ICR;

EID: 84954429170     PISSN: 21576564     EISSN: 21576580     Source Type: Journal    
DOI: 10.5966/sctm.2015-0157     Document Type: Erratum

References (27)

1. Cowan CA, Klimanskaya I, McMahon J et al. Derivationofembryonic stem-cell lines fromhuman blastocysts. N Engl J Med 2004;350:1353-1356.
2. Suss-Toby E, Gerecht-Nir S, Amit M et al. Derivation of a diploid human embryonic stem cell line from a mononuclear zygote. Hum Reprod 2004;19:670-675.
3. Takahashi K, Tanabe K, OhnukiMet al. Induction of pluripotent stem cells from adult human fibroblasts by defined factors. Cell 2007; 131:861-872.
4. Yu J, Vodyanik MA, Smuga-Otto K et al. Induced pluripotent stem cell lines derived fromhuman somatic cells. Science 2007;318:1917-1920.
5. Brons IG, Smithers LE, Trotter MW et al. Derivation of pluripotent epiblast stem cells from mammalian embryos. Nature 2007;448: 191-195.
6. Tesar PJ, Chenoweth JG, Brook FA et al. New cell lines from mouse epiblast share defining features with human embryonic stem cells. Nature 2007;448: 196-199.
7. Nichols J, Smith A. Naive and primed pluripotent states. Cell Stem Cell 2009;4:487-492.
8. Boroviak T, Loos R, Bertone P et al. The ability of inner-cell-mass cells to self-renew as embryonic stem cells is acquired following epiblast specification. Nat Cell Biol 2014;16:516-528.
9. Ying QL, Wray J, Nichols J et al. The ground state of embryonic stem cell self-renewal. Nature 2008;453:519-523.
10. Amit M, Carpenter MK, Inokuma MS et al. Clonally derived human embryonic stem cell lines maintain pluripotency and proliferative potential for prolonged periods of culture. Dev Biol 2000;227:271-278.
11. Bradley A, Evans M, Kaufman MH et al. Formation of germ-line chimaeras from embryo-derived teratocarcinoma cell lines. Nature 1984;309:255-256.
12. Gafni O, Weinberger L, Mansour AA et al. Derivation of novel human ground state naive pluripotent stem cells. Nature 2013;504:282-286.
13. Hanna J, Cheng AW, Saha K et al. Human embryonicstemcellswithbiologicalandepigenetic characteristics similar to those ofmouse ESCs. Proc Natl Acad Sci USA 2010;107:9222-9227.
14. Takashima Y, Guo G, Loos R et al. Resetting transcription factor control circuitry toward ground-state pluripotency in human. Cell 2014;158:1254-1269.
15. Theunissen TW, Powell BE, Wang H et al. Systematic identification of culture conditions for induction and maintenance of naive human pluripotency. Cell Stem Cell 2014;15:471-487.
16. Ware CB, Nelson AM, Mecham B et al. Derivation of naive human embryonic stem cells. Proc Natl Acad Sci USA 2014;111:4484-4489.
17. Guo G, Yang J, Nichols J et al. Klf4 reverts developmentally programmed restriction of ground state pluripotency. Development 2009; 136:1063-1069.
18. Chan YS, Göke J, Ng JH et al. Induction of a human pluripotent state with distinct regulatory circuitry that resembles preimplantation epiblast. Cell Stem Cell 2013;13: 663-675.
19. Ng KM, Tse HF. Modeling hereditary cardiac disease with patient-specific-induced pluripotent stem cells: Opportunities and concerns. J Cardiovasc Pharmacol 2012;60: 406-407.
20. An MC, Zhang N, Scott G et al. Genetic correction of Huntington's disease phenotypes in induced pluripotent stem cells. Cell Stem Cell 2012;11:253-263.
21. Ma N, Liao B, Zhang H et al. Transcription activator-like effector nuclease (TALEN)-mediated gene correction in integration-free b-thalassemia induced pluripotent stem cells. J Biol Chem 2013; 288:34671-34679.
22. Sun N, Zhao H. Seamless correction of the sickle cell disease mutation of the HBB gene in humaninducedpluripotentstemcellsusingTALENs. Biotechnol Bioeng 2014;111:1048-1053.
23. Xie F, Ye L, Chang JC et al. Seamless gene correction ofb-thalassemiamutations in patientspecific iPSCs using CRISPR/Cas9 and piggyBac. Genome Res 2014;24:1526-1533.
24. Zhou T, Benda C, Dunzinger S et al. Generation of human induced pluripotent stem cells from urine samples. Nat Protoc 2012;7:2080-2089.
25. Ran FA, Hsu PD, Wright J et al. Genome engineering using the CRISPR-Cas9 system. Nat Protoc 2013;8:2281-2308.
26. Wang Y, Jiang Y, Liu S et al. Generation of induced pluripotent stem cells from human beta-thalassemia fibroblast cells. Cell Res 2009;19:1120-1123.
27. Zhou W, Choi M, Margineantu D et al. HIF1ainducedswitchfrom bivalent toexclusively glycolytic metabolism during ESC-to-EpiSC/hESC transition. EMBO J 2012;31:2103-2116.