Optimized human factor IX expression cassettes for hepatic-directed gene therapy of hemophilia B

Frontiers of Medicine

Volumn 9, Issue 1, 2015, Pages 90-99

  Zhang, Ru ^a   Wang, Qiang ^a   Zhang, Lin ^a   Chen, Saijuan ^a  

^a SHANGHAI SECOND MEDICAL UNIVERSITY   (China)

Author keywords

factor IX; hemophilia B; hydrodynamic gene transfer; liver specific regulatory elements

Indexed keywords

BLOOD CLOTTING FACTOR 9;

ANIMAL; DEPENDOPARVOVIRUS; GENE EXPRESSION PROFILING; GENE EXPRESSION REGULATION; GENE THERAPY; GENE VECTOR; GENETICS; HEMOPHILIA B; MOUSE; PHARMACOLOGY; PROCEDURES;

ANIMALS; DEPENDOVIRUS; FACTOR IX; GENE EXPRESSION PROFILING; GENETIC THERAPY; GENETIC VECTORS; HEMOPHILIA B; MICE; MUTAGENESIS, INSERTIONAL;

EID: 84948692429     PISSN: 20950217     EISSN: 20950225     Source Type: Journal    
DOI: 10.1007/s11684-015-0390-2     Document Type: Article

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