Personalized medicine: Cell and gene therapy based on patient-specific iPSC-derived retinal pigment epithelium cells

Advances in Experimental Medicine and Biology

Volumn 854, Issue , 2016, Pages 549-555

  Li, Yao ^b   Chan, Lawrence ^b   Nguyen, Huy V ^c   Tsang, Stephen H ^a,b  

^a Department of Orthopaedic Surgery   (United States)

^b Department of Medicine   (United States)

^c New York Presbyterian Columbia University Medical Center   (United States)

Author keywords

Cell therapy; Disease modeling; Gene correction; Gene therapy; IPS; RPE; Sub retinal transplantation

Indexed keywords

MEMBRANE FRIZZLED RELATED PROTEIN; MEMBRANE PROTEIN; PARVOVIRUS VECTOR; UNCLASSIFIED DRUG;

BEST VITELLIFORM MACULAR DYSTROPHY; CELL DIFFERENTIATION; CELL LOSS; CELL THERAPY; CELL TRANSPLANTATION; CHOROIDEREMIA; CRISPR CAS SYSTEM; DEGENERATIVE DISEASE; DISEASE MODEL; GENE MUTATION; GENE THERAPY; GEOGRAPHIC ATROPHY; HUMAN; LEBER CONGENITAL AMAUROSIS; MACULAR DEGENERATION; MULTICENTER STUDY (TOPIC); NONHUMAN; PERSONALIZED MEDICINE; PIGMENT EPITHELIUM; PLURIPOTENT STEM CELL; PRIORITY JOURNAL; RETINA PIGMENT CELL; RETINAL PIGMENT EPITHELIUM CELL; RETINAL PIGMENT EPITHELIUM CELL TRANSPLANTATION; STARGARDT DISEASE; STEM CELL TRANSPLANTATION; VIRAL GENE DELIVERY SYSTEM; ANIMAL; AUTOTRANSPLANTATION; BIOLOGICAL THERAPY; CYTOLOGY; GENETICS; INDUCED PLURIPOTENT STEM CELL; PROCEDURES; RETINAL DEGENERATION; RETINAL PIGMENT EPITHELIUM; TRANSPLANTATION; TRENDS;

ANIMALS; CELL DIFFERENTIATION; CELL- AND TISSUE-BASED THERAPY; GENETIC THERAPY; HUMANS; INDUCED PLURIPOTENT STEM CELLS; PRECISION MEDICINE; RETINAL DEGENERATION; RETINAL PIGMENT EPITHELIUM; TRANSPLANTATION, AUTOLOGOUS;

EID: 84943329552     PISSN: 00652598     EISSN: 22148019     Source Type: Book Series    
DOI: 10.1007/978-3-319-17121-0_73     Document Type: Chapter

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