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Volumn 2015, Issue 102, 2015, Pages 1-8

Limbal approach-subretinal injection of viral vectors for gene therapy in mice retinal pigment epithelium

Author keywords

Eye; Gene therapy; Mice; Neuroscience; Ophthalmology; Retinal pigment epithelium; Subretinal injection; Virus

Indexed keywords

GREEN FLUORESCENT PROTEIN; PHOTOPROTEIN; RED FLUORESCENT PROTEIN;

EID: 84941197756     PISSN: 1940087X     EISSN: None     Source Type: Journal    
DOI: 10.3791/53030     Document Type: Article
Times cited : (23)

References (20)
  • 1
    • 44249085878 scopus 로고    scopus 로고
    • Safety and efficacy of gene transfer for Leber's congenital amaurosis
    • Maguire, A. M., et al. Safety and efficacy of gene transfer for Leber's congenital amaurosis. N Engl J Med. 358, (21), 2240-2248 (2008).
    • (2008) N Engl J Med , vol.358 , Issue.21 , pp. 2240-2248
    • Maguire, A.M.1
  • 2
    • 84855611189 scopus 로고    scopus 로고
    • Gene therapy for leber congenital amaurosis caused by RPE65 mutations: Safety and efficacy in 15 children and adults followed up to 3 years
    • Jacobson, S. G., et al. Gene therapy for leber congenital amaurosis caused by RPE65 mutations: safety and efficacy in 15 children and adults followed up to 3 years. Arch Ophthalmol. 130, (1), 9-24 (2012).
    • (2012) Arch Ophthalmol , vol.130 , Issue.1 , pp. 9-24
    • Jacobson, S.G.1
  • 3
    • 84886744742 scopus 로고    scopus 로고
    • Preclinical potency and safety studies of an AAV2-mediated gene therapy vector for the treatment of MERTK associated retinitis pigmentosa
    • Conlon, T. J., et al. Preclinical potency and safety studies of an AAV2-mediated gene therapy vector for the treatment of MERTK associated retinitis pigmentosa. Hum Gene Ther Clin Dev. 24, (1), 23-28 (2013).
    • (2013) Hum Gene Ther Clin Dev , vol.24 , Issue.1 , pp. 23-28
    • Conlon, T.J.1
  • 4
    • 84897051037 scopus 로고    scopus 로고
    • Retinal gene therapy in patients with choroideremia: Initial findings from a phase 1/2 clinical trial
    • MacLaren, R. E., et al. Retinal gene therapy in patients with choroideremia: initial findings from a phase 1/2 clinical trial. Lancet. 383, (9923), 1129-1137 (2014).
    • (2014) Lancet , vol.383 , Issue.9923 , pp. 1129-1137
    • Maclaren, R.E.1
  • 5
    • 84907973364 scopus 로고    scopus 로고
    • Vector platforms for gene therapy of inherited retinopathies
    • Trapani, I., Puppo, A., Auricchio, A. Vector platforms for gene therapy of inherited retinopathies. Prog Retin Eye Res. 43, 108-128 (2014).
    • (2014) Prog Retin Eye Res , vol.43 , pp. 108-128
    • Trapani, I.1    Puppo, A.2    Auricchio, A.3
  • 7
    • 68249126178 scopus 로고    scopus 로고
    • Intravitreal injection of therapeutic agents
    • Peyman, G. A., Lad, E. M., Moshfeghi, D. M. Intravitreal injection of therapeutic agents. Retina. 29, (7), 875-912 (2009).
    • (2009) Retina , vol.29 , Issue.7 , pp. 875-912
    • Peyman, G.A.1    Lad, E.M.2    Moshfeghi, D.M.3
  • 8
    • 84884190346 scopus 로고    scopus 로고
    • Retinal detachment model in rodents by subretinal injection of sodium hyaluronate
    • Matsumoto, H., Miller, J. W., Vavvas, D. G. Retinal detachment model in rodents by subretinal injection of sodium hyaluronate. J Vis Exp. (79), (2013).
    • (2013) J Vis Exp , Issue.79
    • Matsumoto, H.1    Miller, J.W.2    Vavvas, D.G.3
  • 9
    • 84873938366 scopus 로고    scopus 로고
    • Subretinal injection of gene therapy vectors and stem cells in the perinatal mouse eye
    • Wert, K. J., Skeie, J. M., Davis, R. J., Tsang, S. H., Mahajan, V. B. Subretinal injection of gene therapy vectors and stem cells in the perinatal mouse eye. J Vis Exp. (69), (2012).
    • (2012) J Vis Exp , Issue.69
    • Wert, K.J.1    Skeie, J.M.2    Davis, R.J.3    Tsang, S.H.4    Mahajan, V.B.5
  • 10
    • 84904574804 scopus 로고    scopus 로고
    • Subretinal transplantation of MACS purified photoreceptor precursor cells into the adult mouse retina
    • Eberle, D., Santos-Ferreira, T., Grahl, S., Ader, M. Subretinal transplantation of MACS purified photoreceptor precursor cells into the adult mouse retina. J Vis Exp. (84), e50932 (2014).
    • (2014) J Vis Exp , Issue.84
    • Eberle, D.1    Santos-Ferreira, T.2    Grahl, S.3    Ader, M.4
  • 11
    • 84880253015 scopus 로고    scopus 로고
    • Gene therapy for blindness
    • Sahel, J. A., Roska, B. Gene therapy for blindness. Annu Rev Neurosci. 36, 467-488 (2013).
    • (2013) Annu Rev Neurosci , vol.36 , pp. 467-488
    • Sahel, J.A.1    Roska, B.2
  • 12
    • 35148862553 scopus 로고    scopus 로고
    • Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors
    • Allocca, M., et al. Novel adeno-associated virus serotypes efficiently transduce murine photoreceptors. J Virol. 81, (20), 11372-11380 (2007).
    • (2007) J Virol , vol.81 , Issue.20 , pp. 11372-11380
    • Allocca, M.1
  • 13
    • 0036376655 scopus 로고    scopus 로고
    • Sustained transduction of ocular cells with a bovine immunodeficiency viral vector
    • Takahashi, K., et al. Sustained transduction of ocular cells with a bovine immunodeficiency viral vector. Hum Gene Ther. 13, (11), 1305-1316 (2002).
    • (2002) Hum Gene Ther , vol.13 , Issue.11 , pp. 1305-1316
    • Takahashi, K.1
  • 14
    • 34249936287 scopus 로고    scopus 로고
    • Gene therapeutic prospects in early onset of severe retinal dystrophy: Restoration of vision in RPE65 Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium
    • Rolling, F., et al. Gene therapeutic prospects in early onset of severe retinal dystrophy: restoration of vision in RPE65 Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium. Bull Mem Acad R Med Belg. 161, (10-12), 497-508 (2006).
    • (2006) Bull Mem Acad R Med Belg , vol.161 , Issue.10-12 , pp. 497-508
    • Rolling, F.1
  • 15
    • 33846933945 scopus 로고    scopus 로고
    • Restoration of vision in RPE65-deficient Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium
    • Le Meur, G., et al. Restoration of vision in RPE65-deficient Briard dogs using an AAV serotype 4 vector that specifically targets the retinal pigmented epithelium. Gene Ther. 14, (4), 292-303 (2007).
    • (2007) Gene Ther , vol.14 , Issue.4 , pp. 292-303
    • Le Meur, G.1
  • 16
    • 38949183082 scopus 로고    scopus 로고
    • Adeno-associated viral vectors and the retina
    • Alexander, J. J., Hauswirth, W. W. Adeno-associated viral vectors and the retina. Adv Exp Med Biol. 613, 121-128 (2008).
    • (2008) Adv Exp Med Biol , vol.613 , pp. 121-128
    • Alexander, J.J.1    Hauswirth, W.W.2
  • 17
    • 84876995610 scopus 로고    scopus 로고
    • Genetic and environmental factors associated with reticular pseudodrusen in age-related macular degeneration
    • Puche, N., et al. Genetic and environmental factors associated with reticular pseudodrusen in age-related macular degeneration. Retina. 33, (5), 998-1004 (2013).
    • (2013) Retina , vol.33 , Issue.5 , pp. 998-1004
    • Puche, N.1
  • 18
    • 79955449947 scopus 로고    scopus 로고
    • Gene transfer for neovascular age-related macular degeneration
    • Campochiaro, P. A. Gene transfer for neovascular age-related macular degeneration. Hum Gene Ther. 22, (5), 523-529 (2011).
    • (2011) Hum Gene Ther , vol.22 , Issue.5 , pp. 523-529
    • Campochiaro, P.A.1
  • 19
    • 84902077336 scopus 로고    scopus 로고
    • Intracellular amyloid beta alters the tight junction of retinal pigment epithelium in 5XFAD mice
    • Park, S. W., et al. Intracellular amyloid beta alters the tight junction of retinal pigment epithelium in 5XFAD mice. Neurobiol Aging. 35, (9), 2013-2020 (2014).
    • (2014) Neurobiol Aging , vol.35 , Issue.9 , pp. 2013-2020
    • Park, S.W.1
  • 20
    • 84902602963 scopus 로고    scopus 로고
    • Intracellular cleavage of amyloid beta by a viral protease NIa prevents amyloid beta-mediated cytotoxicity
    • e98650
    • Shin, B., et al. Intracellular cleavage of amyloid beta by a viral protease NIa prevents amyloid beta-mediated cytotoxicity. PLoS One. 9, (6), e98650 (2014).
    • (2014) Plos One , vol.9 , Issue.6
    • Shin, B.1


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.