Improvement and decline in vision with gene therapy in childhood blindness

New England Journal of Medicine

Volumn 372, Issue 20, 2015, Pages 1920-1926

  Jacobson, Samuel G ^a   Cideciyan, Artur V ^a   Roman, Alejandro J ^a   Sumaroka, Alexander ^a   Schwartz, Sharon B ^a   Heon, Elise ^b   Hauswirth, William W ^c  

^a UNIVERSITY OF PENNSYLVANIA   (United States)

^b HOSPITAL FOR SICK CHILDREN   (Canada)

^c UNIVERSITY OF FLORIDA   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ARTICLE; CASE REPORT; CLINICAL TRIAL (TOPIC); DARK ADAPTATION; DISEASE COURSE; FOLLOW UP; GENE THERAPY; HUMAN; LEBER CONGENITAL AMAUROSIS; LONG TERM CARE; PHOTORECEPTOR MEMBRANE; PHOTORECEPTOR OUTER SEGMENT; PRIORITY JOURNAL; TREATMENT OUTCOME; VISION; VISUAL STIMULATION; ADOLESCENT; CLINICAL TRIAL; GENETICS; MULTICENTER STUDY; MUTATION; PATHOLOGY; PHOTORECEPTOR CELL; PHYSIOLOGY; RETINA; YOUNG ADULT;

ADOLESCENT; DISEASE PROGRESSION; FOLLOW-UP STUDIES; GENETIC THERAPY; HUMANS; LEBER CONGENITAL AMAUROSIS; MUTATION; PHOTORECEPTOR CELLS, VERTEBRATE; RETINA; VISION, OCULAR; YOUNG ADULT;

EID: 84929378811     PISSN: 00284793     EISSN: 15334406     Source Type: Journal    
DOI: 10.1056/NEJMoa1412965     Document Type: Article

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