Three-year follow-up after unilateral subretinal delivery of adeno-associated virus in patients with leber congenital amaurosis type 2

Ophthalmology

Volumn 120, Issue 6, 2013, Pages 1283-1291

  Testa, Francesco ^a   Maguire, Albert M ^b,c,d   Rossi, Settimio ^a   Pierce, Eric A ^b,d   Melillo, Paolo ^a   Marshall, Kathleen ^c   Banfi, Sandro ^a,e   Surace, Enrico M ^e   Sun, Junwei ^d   Acerra, Carmela ^a   Wright, J Fraser ^c,d   Wellman, Jennifer ^c   High, Katherine A ^c,d   Auricchio, Alberto ^e,f   Bennett, Jean ^b,c   Simonelli, Francesca ^a,e  

^a SECOND UNIVERSITY OF NAPLES   (Italy)

^b UNIVERSITY OF PENNSYLVANIA   (United States)

^c CHILDREN S HOSPITAL OF PHILADELPHIA   (United States)

^d UNIVERSITY OF PENNSYLVANIA   (United States)

^e TELETHON INSTITUTE OF GENETICS AND MEDICINE TIGEM   (Italy)

^f UNIVERSITY OF NAPLES FEDERICO II   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

PARVOVIRUS VECTOR;

ADENO ASSOCIATED VIRUS; ADOLESCENT; ADULT; ARTICLE; CHILD; CLINICAL ARTICLE; CLINICAL TRIAL (TOPIC); CONTROLLED STUDY; EYE MOVEMENT; FEMALE; FOLLOW UP; GENE; GENE MUTATION; HUMAN; LEBER CONGENITAL AMAUROSIS; LEBER CONGENITAL AMAUROSIS TYPE 2; MALE; NYSTAGMUS; OUTCOME ASSESSMENT; PRIORITY JOURNAL; PUPIL REFLEX; RPE65 GENE; SCHOOL CHILD; VIRAL GENE THERAPY; VISION; VISUAL ACUITY; VISUAL FIELD;

ADOLESCENT; ADULT; CHILD; CIS-TRANS-ISOMERASES; DEPENDOVIRUS; FEMALE; FOLLOW-UP STUDIES; GENETIC THERAPY; GENETIC VECTORS; HUMANS; INJECTIONS, INTRAOCULAR; LEBER CONGENITAL AMAUROSIS; MALE; MUTATION; REFLEX, PUPILLARY; TOMOGRAPHY, OPTICAL COHERENCE; TRANSFECTION; VISUAL ACUITY; VISUAL FIELDS; YOUNG ADULT;

EID: 84878581647     PISSN: 01616420     EISSN: 15494713     Source Type: Journal    
DOI: 10.1016/j.ophtha.2012.11.048     Document Type: Article

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