Unraveling the potential of CRISPR-Cas9 for gene therapy

Expert Opinion on Biological Therapy

Volumn 15, Issue 3, 2015, Pages 311-314

  Barrangou, Rodolphe ^a   May, Andrew P ^b  

^a NORTH CAROLINA STATE UNIVERSITY   (United States)

^b Caribou Biosciences Inc   (United States)

Author keywords

Cas9; CRISPR; Gene therapy; Genome editing

Indexed keywords

CAS9 ENDONUCLEASE; CRISPR ASSOCIATED PROTEIN; ENDONUCLEASE; GUIDE RNA; UNCLASSIFIED DRUG;

CELL BASED GENE THERAPY; CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT; CRISPR CAS SYSTEM; DNA END JOINING REPAIR; DNA REPAIR; DOUBLE STRANDED DNA BREAK; GENE MUTATION; GENE TECHNOLOGY; GENE THERAPY; GENETIC DISORDER; GENOME ANALYSIS; GENOME EDITING; HUMAN; IN VIVO STUDY; INDEL MUTATION; NONHUMAN; REVIEW; ANIMAL; GENETICS; GENOME; PROCEDURES; TRENDS;

EUKARYOTA; PROKARYOTA;

ANIMALS; CRISPR-CAS SYSTEMS; DNA REPAIR; GENETIC THERAPY; GENOME; HUMANS;

EID: 84923107960     PISSN: 14712598     EISSN: 17447682     Source Type: Journal    
DOI: 10.1517/14712598.2015.994501     Document Type: Review

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