Human COL7A1-corrected induced pluripotent stem cells for the treatment of recessive dystrophic epidermolysis bullosa

Science Translational Medicine

Volumn 6, Issue 264, 2014, Pages

  Sebastiano, Vittorio ^a,b   Zhen, Hanson Hui ^b   Derafshi, Bahareh Haddad ^a   Bashkirova, Elizaveta ^b   Melo, Sandra P ^b   Wang, Pei ^b,d   Leung, Thomas L ^b   Siprashvili, Zurab ^b   Tichy, Andrea ^b   Li, Jiang ^b   Ameen, Mohammed ^b   Hawkins, John ^a   Lee, Susie ^b   Li, Lingjie ^b   Schwertschkow, Aaron ^c   Bauer, Gerhard ^c   Lisowski, Leszek ^b   Kay, Mark A ^b,e   Kim, Seung K ^b   Lane, Alfred T ^b   Wernig, Marius ^a   Oro, Anthony E ^b   more..

^a STANFORD UNIVERSITY SCHOOL OF MEDICINE   (United States)

^b STANFORD UNIVERSITY   (United States)

^c UNIVERSITY OF CALIFORNIA   (United States)

^d UNIVERSITY OF TEXAS HEALTH SCIENCE CENTER AT SAN ANTONIO   (United States)

^e SALK INSTITUTE FOR BIOLOGICAL STUDIES   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

LENTIVIRUS VECTOR; ZINC FINGER NUCLEASE; COL7A1 PROTEIN, HUMAN; COLLAGEN TYPE 7;

ADULT; ANIMAL CELL; ARTICLE; CANCER SUSCEPTIBILITY; CELL DIFFERENTIATION; COL7A1 GENE; CONTROLLED STUDY; CYTOKINE PRODUCTION; EPIDERMOLYSIS BULLOSA; FIBROBLAST; GENE; GENE FREQUENCY; GENE LOCUS; GENE MUTATION; GENETIC HETEROGENEITY; GENETIC VARIABILITY; HUMAN; HUMAN CELL; HUMAN TISSUE; KARYOTYPE; KERATINOCYTE; MOUSE; NONHUMAN; NUCLEAR REPROGRAMMING; PLURIPOTENT STEM CELL; RAT; RECESSIVE DYSTROPHIC EPIDERMOLYSIS BULLOSA; VIRAL GENE THERAPY; ANIMAL; CYTOLOGY; DNA SEQUENCE; EPIDERMOLYSIS BULLOSA DYSTROPHICA; GENE THERAPY; GENETIC PREDISPOSITION; GENETICS; HOMOLOGOUS RECOMBINATION; HUMAN GENOME; METABOLISM; MOLECULAR GENETICS; MUTATION; NUCLEOTIDE SEQUENCE; PATHOLOGY; RECESSIVE GENE; TRANSPLANTATION;

ANIMALS; BASE SEQUENCE; COLLAGEN TYPE VII; EPIDERMOLYSIS BULLOSA DYSTROPHICA; GENES, RECESSIVE; GENETIC PREDISPOSITION TO DISEASE; GENETIC THERAPY; GENOME, HUMAN; HOMOLOGOUS RECOMBINATION; HUMANS; INDUCED PLURIPOTENT STEM CELLS; KERATINOCYTES; MICE; MOLECULAR SEQUENCE DATA; MUTATION; SEQUENCE ANALYSIS, DNA;

EID: 84914166169     PISSN: 19466234     EISSN: 19466242     Source Type: Journal    
DOI: 10.1126/scitranslmed.3009540     Document Type: Article

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