DOK7 gene therapy benefits mouse models of diseases characterized by defects in the neuromuscular junction

Science

Volumn 345, Issue 6203, 2014, Pages 1505-1508

  Arimura, Sumimasa ^a   Okada, Takashi ^b   Tezuka, Tohru ^a   Chiyo, Tomoko ^b   Kasahara, Yuko ^b   Yoshimura, Toshiro ^c   Motomura, Masakatsu ^d   Yoshida, Nobuaki ^a   Beeson, David ^e   Takeda, Shin'ichi ^b   Yamanashi, Yuji ^a  

^a UNIVERSITY OF TOKYO   (Japan)

^b NATIONAL INSTITUTE OF NEUROSCIENCE   (Japan)

^c NAGASAKI UNIVERSITY   (Japan)

^d NAGASAKI INSTITUTE OF APPLIED SCIENCE   (Japan)

^e UNIVERSITY OF OXFORD   (United Kingdom)

Author keywords

[No Author keywords available]

Indexed keywords

DOK 7 PROTEIN, MOUSE; DOK-7 PROTEIN, MOUSE; DOK7 PROTEIN, HUMAN; MUSCLE PROTEIN;

ADENO ASSOCIATED VIRUS; ANIMAL; ARTICLE; C57BL MOUSE; DISEASE MODEL; FEMALE; GENE THERAPY; GENE VECTOR; GENETICS; HUMAN; INNERVATION; KNOCKOUT MOUSE; LIMB GIRDLE MUSCULAR DYSTROPHY; MALE; METHODOLOGY; MOUSE; NEUROMUSCULAR SYNAPSE; PATHOLOGY; PATHOPHYSIOLOGY; SKELETAL MUSCLE;

ANIMALS; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; FEMALE; GENETIC THERAPY; GENETIC VECTORS; HUMANS; MALE; MICE; MICE, INBRED C57BL; MICE, KNOCKOUT; MUSCLE PROTEINS; MUSCLE, SKELETAL; MUSCULAR DYSTROPHIES, LIMB-GIRDLE; NEUROMUSCULAR JUNCTION;

EID: 84907190391     PISSN: 00368075     EISSN: 10959203     Source Type: Journal    
DOI: 10.1126/science.1250744     Document Type: Article

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