메뉴 건너뛰기




Volumn 56, Issue 5, 2014, Pages 269-273

Comparative next-generation sequencing of adeno-associated virus inverted terminal repeats

Author keywords

Adeno associated virus; Inverted terminal repeat; Next generation sequencing

Indexed keywords

RECOMBINANT DNA;

EID: 84900461488     PISSN: 07366205     EISSN: 19409818     Source Type: Journal    
DOI: 10.2144/000114170     Document Type: Article
Times cited : (7)

References (22)
  • 1
    • 79954622209 scopus 로고    scopus 로고
    • Therapeutic in vivo gene transfer for genetic disease using AAV: Progress and challenges
    • Mingozzi, F. and K.A. High. 2011. Therapeutic in vivo gene transfer for genetic disease using AAV: progress and challenges. Nat. Rev. Genet. 12:341-355.
    • (2011) Nat. Rev. Genet. , vol.12 , pp. 341-355
    • Mingozzi, F.1    High, K.A.2
  • 3
    • 84875962928 scopus 로고    scopus 로고
    • Efficacy and long-term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: An open-label trial
    • Gaudet, D., J. Methot, S. Dery, D. Brisson, C. Essiembre, G. Tremblay, K. Tremblay, J. de Wal, et al. 2013. Efficacy and long-term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: an open-label trial. Gene Ther. 20:361-369.
    • (2013) Gene Ther. , vol.20 , pp. 361-369
    • Gaudet, D.1    Methot, J.2    Dery, S.3    Brisson, D.4    Essiembre, C.5    Tremblay, G.6    Tremblay, K.7    de Wal, J.8
  • 8
    • 79961032369 scopus 로고    scopus 로고
    • Calcium Upregulation by Percutaneous Administration of Gene Therapy in Cardiac Disease (CUPID): A phase 2 trial of intracoronary gene therapy of sarcoplasmic reticulum Ca2+-ATPase in patients with advanced heart failure
    • Jessup, M., B. Greenberg, D. Mancini, T. Cappola, D.F. Pauly, B. Jaski, A. Yaroshinsky, K.M. Zsebo, et al. 2011. Calcium Upregulation by Percutaneous Administration of Gene Therapy in Cardiac Disease (CUPID): a phase 2 trial of intracoronary gene therapy of sarcoplasmic reticulum Ca2+-ATPase in patients with advanced heart failure. Circulation 124:304-313.
    • (2011) Circulation , vol.124 , pp. 304-313
    • Jessup, M.1    Greenberg, B.2    Mancini, D.3    Cappola, T.4    Pauly, D.F.5    Jaski, B.6    Yaroshinsky, A.7    Zsebo, K.M.8
  • 10
    • 84869087881 scopus 로고    scopus 로고
    • Patterns of scAAV vector insertion associated with oncogenic events in a mouse model for genotoxicity
    • Rosas, L.E., J.L. Grieves, K. Zaraspe, K.M. La Perle, H. Fu, and D.M. McCarty. 2012. Patterns of scAAV vector insertion associated with oncogenic events in a mouse model for genotoxicity. Mol Ther. 20:2098-2110.
    • (2012) Mol Ther. , vol.20 , pp. 2098-2110
    • Rosas, L.E.1    Grieves, J.L.2    Zaraspe, K.3    La Perle, K.M.4    Fu, H.5    McCarty, D.M.6
  • 11
    • 77957323822 scopus 로고    scopus 로고
    • Adeno-associated virus: A key to the human genome?
    • Henckaerts, E. and R.M. Linden. 2010. Adeno-associated virus: a key to the human genome? Future Virol. 5:555-574.
    • (2010) Future Virol. , vol.5 , pp. 555-574
    • Henckaerts, E.1    Linden, R.M.2
  • 12
    • 0030030227 scopus 로고    scopus 로고
    • Rescue and replication of adeno-associated virus type 2 as well as vector DNA sequences from recombinant plasmids containing deletions in the viral inverted terminal repeats: Selective encapsidation of viral genomes in progeny virions
    • Wang, X.S., S. Ponnazhagan, and A. Srivastava. 1996. Rescue and replication of adeno-associated virus type 2 as well as vector DNA sequences from recombinant plasmids containing deletions in the viral inverted terminal repeats: selective encapsidation of viral genomes in progeny virions. J. Virol. 70:1668-1677.
    • (1996) J. Virol. , vol.70 , pp. 1668-1677
    • Wang, X.S.1    Ponnazhagan, S.2    Srivastava, A.3
  • 13
    • 0020684648 scopus 로고
    • Nucleotide sequence and organization of the adeno-associated virus 2 genome
    • Srivastava, A., E.W. Lusby, and K.I. Berns. 1983. Nucleotide sequence and organization of the adeno-associated virus 2 genome. J. Virol. 45:555-564.
    • (1983) J. Virol. , vol.45 , pp. 555-564
    • Srivastava, A.1    Lusby, E.W.2    Berns, K.I.3
  • 14
    • 0033567129 scopus 로고    scopus 로고
    • Structural analysis of adeno-associated virus transduction circular intermediates
    • Duan, D., Z. Yan, Y. Yue, and J.F. Engelhardt. 1999. Structural analysis of adeno-associated virus transduction circular intermediates. Virology 261:8-14.
    • (1999) Virology , vol.261 , pp. 8-14
    • Duan, D.1    Yan, Z.2    Yue, Y.3    Engelhardt, J.F.4
  • 15
    • 84872046121 scopus 로고    scopus 로고
    • A capillary electrophoresis sequencing method for the identification of mutations in the inverted terminal repeats of adeno-associated virus. Human gene therapy. Part B
    • Mroske, C., H. Rivera, T. Ul-Hasan, S. Chatterjee, and K.K. Wong. 2012. A capillary electrophoresis sequencing method for the identification of mutations in the inverted terminal repeats of adeno-associated virus. Human gene therapy. Part B. Hum Gene Ther Methods. 23:128-136.
    • (2012) Hum Gene Ther Methods. , vol.23 , pp. 128-136
    • Mroske, C.1    Rivera, H.2    Ul-Hasan, T.3    Chatterjee, S.4    Wong, K.K.5
  • 18
    • 84866930809 scopus 로고    scopus 로고
    • AAV vectors containing rDNA homology display increased chromosomal integration and transgene persistence
    • Wang, Z., L. Lisowski, M.J. Finegold, H. Nakai, M.A. Kay, and M. Grompe. 2012. AAV vectors containing rDNA homology display increased chromosomal integration and transgene persistence. Mol Ther. 20:1902-1911.
    • (2012) Mol Ther. , vol.20 , pp. 1902-1911
    • Wang, Z.1    Lisowski, L.2    Finegold, M.J.3    Nakai, H.4    Kay, M.A.5    Grompe, M.6


* 이 정보는 Elsevier사의 SCOPUS DB에서 KISTI가 분석하여 추출한 것입니다.