Immune response to intrathecal enzyme replacement therapy in mucopolysaccharidosis I patients

Pediatric Research

Volumn 74, Issue 6, 2013, Pages 712-720

  Vera, Moin ^a   Le, Steven ^a   Kan, Shih Hsin ^a   Garban, Hermes ^a   Naylor, David ^a   Mlikotic, Anton ^a   Kaitila, Ilkka ^b   Harmatz, Paul ^c   Chen, Agnes ^a   Dickson, Patricia ^a  

^a HARBOR UCLA MEDICAL CENTER   (United States)

^b HELSINKI UNIVERSITY CENTRAL HOSPITAL   (Finland)

^c CHILDREN S HOSPITAL OAKLAND   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

GAMMA INTERFERON; GRANULOCYTE MACROPHAGE COLONY STIMULATING FACTOR; IMMUNOGLOBULIN D ANTIBODY; IMMUNOGLOBULIN E ANTIBODY; IMMUNOGLOBULIN G; IMMUNOGLOBULIN G ANTIBODY; IMMUNOGLOBULIN M ANTIBODY; INTERLEUKIN 10; INTERLEUKIN 1BETA; INTERLEUKIN 2; INTERLEUKIN 4; INTERLEUKIN 5; INTERLEUKIN 6; INTERLEUKIN 8; LARONIDASE; TUMOR NECROSIS FACTOR ALPHA;

ADOLESCENT; ADULT; ANTIBODY RESPONSE; ARTICLE; BACKACHE; BUTTOCK PAIN; CELLULAR IMMUNITY; CEREBROSPINAL FLUID; CEREBROSPINAL FLUID PRESSURE; CLINICAL ARTICLE; CORNEA TRANSPLANTATION; CYTOKINE RESPONSE; DRUG WITHDRAWAL; ENZYME REPLACEMENT; FEMALE; FLUSHING; HEADACHE; HUMAN; HUMORAL IMMUNITY; HURLER SYNDROME; HYPOXIA; IMMUNOGLOBULIN BLOOD LEVEL; INFLAMMATION; LEUKOCYTOSIS; LOW BACK PAIN; MALE; MUSCLE CRAMP; PAIN; PARESTHESIA; PNEUMONIA; PRIORITY JOURNAL; PROSTATE CANCER; PROTEIN BLOOD LEVEL; PROTEIN CEREBROSPINAL FLUID LEVEL; RESPIRATORY DISTRESS; SEROLOGY; SIDE EFFECT; SPINAL CORD COMPRESSION; UPPER BACK PAIN;

ADULT; CHILD, PRESCHOOL; FEMALE; HUMANS; IDURONIDASE; INFANT; INJECTIONS, SPINAL; MALE; MUCOPOLYSACCHARIDOSIS I; RECOMBINANT PROTEINS; YOUNG ADULT;

EID: 84890775616     PISSN: 00313998     EISSN: 15300447     Source Type: Journal    
DOI: 10.1038/pr.2013.158     Document Type: Article

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