AAV2/8 vectors purified from culture medium with a simple and rapid protocol transduce murine liver, muscle, and retina efficiently

Human Gene Therapy Methods

Volumn 24, Issue 6, 2013, Pages 392-398

  Doria, Monica ^a   Ferrara, Antonella ^a   Auricchio, Alberto ^a,b  

^a TELETHON INSTITUTE OF GENETICS AND MEDICINE TIGEM   (Italy)

^b UNIVERSITY OF NAPLES FEDERICO II   (Italy)

Author keywords

[No Author keywords available]

Indexed keywords

CESIUM CHLORIDE; PARVOVIRUS VECTOR;

ARTICLE; CELL LYSATE; CULTURE MEDIUM; EMBRYO; FILTRATION; HUMAN; HUMAN CELL; IN VITRO STUDY; LIVER; MUSCLE; NONHUMAN; PRIORITY JOURNAL; RETINA; TANGENTIAL FLOW FILTRATION; ULTRACENTRIFUGATION; VIRAL GENE DELIVERY SYSTEM; VIRUS PURIFICATION; VIRUS VIRULENCE;

ANIMALS; CELL LINE, TUMOR; CHEMICAL FRACTIONATION; CULTURE MEDIA; DEPENDOVIRUS; GENETIC THERAPY; GENETIC VECTORS; HEK293 CELLS; HUMANS; LIVER; MICE; MUSCLE, SKELETAL; ORGAN SPECIFICITY; RETINA; TRANSDUCTION, GENETIC; TRANSFECTION;

EID: 84890387154     PISSN: 19466536     EISSN: 19466544     Source Type: Journal    
DOI: 10.1089/hgtb.2013.155     Document Type: Article

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