-
1
-
-
33645127443
-
Genetic medicines: Treatment strategies for hereditary disorders
-
O'Connor TP, Crystal RG: Genetic medicines: treatment strategies for hereditary disorders. Nat Rev Genet 2006; 4: 261-282.
-
(2006)
Nat Rev Genet
, vol.4
, pp. 261-282
-
-
O'connor, T.P.1
Crystal, R.G.2
-
2
-
-
0035019101
-
Molecular therapeutics of liver disease
-
Davern TJ: Molecular therapeutics of liver disease. Liver Dis 2001; 52: 381-414.
-
(2001)
Liver Dis
, vol.52
, pp. 381-414
-
-
Davern, T.J.1
-
3
-
-
0028426914
-
Liver-directed gene therapy: Prospects and problems
-
Strauss M: Liver-directed gene therapy: prospects and problems. Gene Ther 1994; 1: 156-164.
-
(1994)
Gene Ther
, vol.1
, pp. 156-164
-
-
Strauss, M.1
-
4
-
-
0025822386
-
Inherited hepatic enzyme defects as candidates for liver-directed gene therapy
-
Horwich AL: Inherited hepatic enzyme defects as candidates for liver-directed gene therapy. Curr Top Microbiol Immunol 1991; 168: 185-200.
-
(1991)
Curr Top Microbiol Immunol
, vol.168
, pp. 185-200
-
-
Horwich, A.L.1
-
5
-
-
0033999084
-
Gene silencing as a threat to the success of gene therapy
-
Bestor TH: Gene silencing as a threat to the success of gene therapy. J Clin Invest 2000; 105: 409-411.
-
(2000)
J Clin Invest
, vol.105
, pp. 409-411
-
-
Bestor, T.H.1
-
6
-
-
0037348329
-
RNA interference targeting Fas protects mice from fulminant hepatitis
-
Song E, et al: RNA interference targeting Fas protects mice from fulminant hepatitis. Nat Med 2003; 9: 347-351.
-
(2003)
Nat Med
, vol.9
, pp. 347-351
-
-
Song, E.1
-
7
-
-
0032805251
-
Hydrodynamics based transfection in animals by systemic administration of plasmid DNA
-
Liu F, Song Y, Liu D: Hydrodynamics based transfection in animals by systemic administration of plasmid DNA. Gene Ther 1999; 6: 1258-1266.
-
(1999)
Gene Ther
, vol.6
, pp. 1258-1266
-
-
Liu, F.1
Song, Y.2
Liu, D.3
-
8
-
-
0033893570
-
Long-term expression of human alpha1-antitrypsin gene in mouse liver achieved by intravenous administration of plasmid DNA using a hydrodynamics based procedure
-
Zhang G, Song YK, Liu D: Long-term expression of human alpha1-antitrypsin gene in mouse liver achieved by intravenous administration of plasmid DNA using a hydrodynamics based procedure. Gene Ther 2000; 7: 1344-1349.
-
(2000)
Gene Ther
, vol.7
, pp. 1344-1349
-
-
Zhang, G.1
Song, Y.K.2
Liu, D.3
-
9
-
-
0041911490
-
Long-term therapeutic levels of human alpha-1 antitrypsin in plasma after hydrodynamic injection of nonviral DNA
-
Aliño SF, Crespo A, Dasí F: Long-term therapeutic levels of human alpha-1 antitrypsin in plasma after hydrodynamic injection of nonviral DNA. Gene Ther 2003; 10: 1672-1679.
-
(2003)
Gene Ther
, vol.10
, pp. 1672-1679
-
-
Aliño, S.F.1
Crespo, A.2
Dasí, F.3
-
10
-
-
40549090572
-
Minimally invasive and selective hydrodynamic gene therapy of liver segments in the pig and human
-
Khorsandi SE, Bachellier P, Weber JC, Greget M, Jaeck D, Zacharoulis D, Rountas C, Helmy S, Helmy A, Al-Waracky M, Salama H, Jiao L, Nicholls J, Davies AJ, Levicar N, Jensen S, Habib N: Minimally invasive and selective hydrodynamic gene therapy of liver segments in the pig and human. Cancer Gene Ther 2008; 15: 225-230.
-
(2008)
Cancer Gene Ther
, vol.15
, pp. 225-230
-
-
Khorsandi, S.E.1
Bachellier, P.2
Weber, J.C.3
Greget, M.4
Jaeck, D.5
Zacharoulis, D.6
Rountas, C.7
Helmy, S.8
Helmy, A.9
Al-Waracky, M.10
Salama, H.11
Jiao, L.12
Nicholls, J.13
Davies, A.J.14
Levicar, N.15
Jensen, S.16
Habib, N.17
-
11
-
-
33746235806
-
Mouse and pig nonviral liver gene therapy: Success and trials
-
Herrero MJ, Dasi F, Noguera I, Sanchez M, Moret I, Sanmartin I, Aliño SF: Mouse and pig nonviral liver gene therapy: success and trials. Gene Ther Mol Biol 2005; 9: 169-180.
-
(2005)
Gene Ther Mol Biol
, vol.9
, pp. 169-180
-
-
Herrero, M.J.1
Dasi, F.2
Noguera, I.3
Sanchez, M.4
Moret, I.5
Sanmartin, I.6
Aliño, S.F.7
-
12
-
-
33846922049
-
Pig liver gene therapy by noninvasive interventionist catheterisation
-
Aliño SF, Herrero MJ, Noguera I, Dasí F, Sánchez M: Pig liver gene therapy by noninvasive interventionist catheterisation. Gene Ther 2007; 14: 334-343.
-
(2007)
Gene Ther
, vol.14
, pp. 334-343
-
-
Aliño, S.F.1
Herrero, M.J.2
Noguera, I.3
Dasí, F.4
Sánchez, M.5
-
13
-
-
78649503962
-
Naked DNA delivery to whole pig cardiac tissue by coronary sinus retrograde injection employing noninvasive catheterization
-
Aliño SF, José Herrero M, Bodi V, Noguera I, Mainar L, Dasí F, Sempere A, Sánchez M, Díaz A, Sabater L, Lledó L: Naked DNA delivery to whole pig cardiac tissue by coronary sinus retrograde injection employing noninvasive catheterization. J Gene Med 2010; 12: 920-926.
-
(2010)
J Gene Med
, vol.12
, pp. 920-926
-
-
Aliño, S.F.1
José Herrero, M.2
Bodi, V.3
Noguera, I.4
Mainar, L.5
Dasí, F.6
Sempere, A.7
Sánchez, M.8
Díaz, A.9
Sabater, L.10
Lledó, L.11
-
14
-
-
77950859726
-
Technical requirements for effective regional hydrodynamic gene delivery to the left lateral lobe of the rat liver
-
Sawyer GJ, Zhang X, Fabre JW: Technical requirements for effective regional hydrodynamic gene delivery to the left lateral lobe of the rat liver. Gene Ther 2010; 17: 560-564.
-
(2010)
Gene Ther
, vol.17
, pp. 560-564
-
-
Sawyer, G.J.1
Zhang, X.2
Fabre, J.W.3
-
15
-
-
40249118457
-
Hydrodynamic gene delivery to the pig liver via an isolated segment of the inferior vena cava
-
Fabre JW, Grehan A, Whitehorne M, Sawyer GJ, Dong X, Salehi S, Eckley L, Zhang X, Seddon M, Shah AM, Davenport M, Rela M: Hydrodynamic gene delivery to the pig liver via an isolated segment of the inferior vena cava. Gene Ther 2008; 15: 452-462.
-
(2008)
Gene Ther
, vol.15
, pp. 452-462
-
-
Fabre, J.W.1
Grehan, A.2
Whitehorne, M.3
Sawyer, G.J.4
Dong, X.5
Salehi, S.6
Eckley, L.7
Zhang, X.8
Seddon, M.9
Shah, A.M.10
Davenport, M.11
Rela, M.12
-
16
-
-
33845209883
-
Naked plasmid DNA transfer to the porcine liver using rapid injection with large volume
-
Yoshino H, Hashizume K, Kobayashi E: Naked plasmid DNA transfer to the porcine liver using rapid injection with large volume. Gene Ther 2006; 13: 1696-1702.
-
(2006)
Gene Ther
, vol.13
, pp. 1696-1702
-
-
Yoshino, H.1
Hashizume, K.2
Kobayashi, E.3
-
17
-
-
61649121501
-
Image-guided, lobe-specific hydrodynamic gene delivery to swine liver
-
Kamimura K, Suda T, Xu W, Zhang G, Liu D: Image-guided, lobe-specific hydrodynamic gene delivery to swine liver. Mol Ther 2009; 17: 491-499.
-
(2009)
Mol Ther
, vol.17
, pp. 491-499
-
-
Kamimura, K.1
Suda, T.2
Xu, W.3
Zhang, G.4
Liu, D.5
-
18
-
-
84862128812
-
DNA delivery to 'ex vivo' human liver segments
-
Herrero MJ, Sabater L, Guenechea G, Sendra L, Montilla AI, Abargues R, Navarro V, Aliño SF: DNA delivery to 'ex vivo' human liver segments. Gene Ther 2012; 19: 504-512.
-
(2012)
Gene Ther
, vol.19
, pp. 504-512
-
-
Herrero, M.J.1
Sabater, L.2
Guenechea, G.3
Sendra, L.4
Montilla, A.I.5
Abargues, R.6
Navarro, V.7
Aliño, S.F.8
-
19
-
-
20744458578
-
Hydrodynamic liver gene transfer mechanism involves transient sinusoidal blood stasis and massive hepatocyte endocytic vesicles
-
Crespo A, Peydró A, Dasí F, Benet M, Calvete JJ, Revert F, Aliño SF, et al: Hydrodynamic liver gene transfer mechanism involves transient sinusoidal blood stasis and massive hepatocyte endocytic vesicles. Gene Ther 2005; 12: 927-935.
-
(2005)
Gene Ther
, vol.12
, pp. 927-935
-
-
Crespo, A.1
Peydró, A.2
Dasí, F.3
Benet, M.4
Calvete, J.J.5
Revert, F.6
Aliño, S.F.7
-
20
-
-
65949106796
-
Hydrodynamic gene delivery to the liver: Theoretical and practical issues for clinical application
-
Sawyer GJ, Rela M, Davenport M, Whitehorne M, Zhang X, Fabre JW: Hydrodynamic gene delivery to the liver: theoretical and practical issues for clinical application. Curr Gene Ther 2009; 9: 128-135.
-
(2009)
Curr Gene Ther
, vol.9
, pp. 128-135
-
-
Sawyer, G.J.1
Rela, M.2
Davenport, M.3
Whitehorne, M.4
Zhang, X.5
Fabre, J.W.6
-
21
-
-
79956039707
-
Critical, physiological and surgical considerations for hydrodynamic pressurization of individual segments of the pig liver
-
Fabre JW, Whitehorne M, Grehan A, Sawyer GJ, Zhang X, Davenport M, Rela M: Critical, physiological and surgical considerations for hydrodynamic pressurization of individual segments of the pig liver. Hum Gene Ther 2011; 22: 879-887.
-
(2011)
Hum Gene Ther
, vol.22
, pp. 879-887
-
-
Fabre, J.W.1
Whitehorne, M.2
Grehan, A.3
Sawyer, G.J.4
Zhang, X.5
Davenport, M.6
Rela, M.7
-
22
-
-
0023096851
-
A reproducible model of acute hepatic failure by transient ischemia in the pig
-
de Groot GH, Reuvers CB, Schalm SW, Boks AL, Terpstra OT, Jeekel H, ten Kate F, Bruinvels J: A reproducible model of acute hepatic failure by transient ischemia in the pig. J Surg Res 1987; 42: 92-100.
-
(1987)
J Surg Res
, vol.42
, pp. 92-100
-
-
De Groot, G.H.1
Reuvers, C.B.2
Schalm, S.W.3
Boks, A.L.4
Terpstra, O.T.5
Jeekel, H.6
Ten Kate, F.7
Bruinvels, J.8
-
23
-
-
21344461475
-
An experimental animal model of fulminant hepatic failure in pigs
-
Lee KU, Zheng LX, Cho YB, Kim KH, Ha J, Suh KS, Jung SE: An experimental animal model of fulminant hepatic failure in pigs. J Korean Med Sci 2005; 20: 427-432.
-
(2005)
J Korean Med Sci
, vol.20
, pp. 427-432
-
-
Lee, K.U.1
Zheng, L.X.2
Cho, Y.B.3
Kim, K.H.4
Ha, J.5
Suh, K.S.6
Jung, S.E.7
-
24
-
-
34547657824
-
Cardiovascular function following acute volume overload for hydrodynamic gene delivery to the liver
-
Sawyer GJ, Dong X, Whitehorne M, Grehan A, Seddon M, Shah AM, Zhang X, Fabre JW: Cardiovascular function following acute volume overload for hydrodynamic gene delivery to the liver. Gene Ther 2007; 14: 1208-1217.
-
(2007)
Gene Ther
, vol.14
, pp. 1208-1217
-
-
Sawyer, G.J.1
Dong, X.2
Whitehorne, M.3
Grehan, A.4
Seddon, M.5
Shah, A.M.6
Zhang, X.7
Fabre, J.W.8
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