Subretinal gene therapy of mice with Bardet-Biedl syndrome type 1

Investigative Ophthalmology and Visual Science

Volumn 54, Issue 9, 2013, Pages 6118-6132

  Seo, Seongjin ^a   Mullins, Robert F ^a   Dumitrescu, Alina V ^a,b   Bhattarai, Sajag ^a   Gratie, Daniel ^a   Wang, Kai ^a   Stone, Edwin M ^a   Sheffield, Val ^a,c   Drack, Arlene V ^a,c  

^a UNIVERSITY OF IOWA   (United States)

^b UNIVERSITY OF KANSAS SCHOOL OF MEDICINE   (United States)

^c UNIVERSITY OF IOWA   (United States)

Author keywords

AAV vector; Bardet Biedl syndrome; Gene therapy; Mouse model; Retinal degeneration

Indexed keywords

4',6 DIAMIDINO 2 PHENYLINDOLE; GENE THERAPY AGENT; PARVOVIRUS VECTOR; RHODOPSIN;

ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; BARDET BIEDL SYNDROME; BARDET BIEDL SYNDROME 4 GENE; CONTROLLED STUDY; ELECTRORETINOGRAPHY; GENE; GENE EXPRESSION; GENE THERAPY; HISTOLOGY; IMMUNOHISTOCHEMISTRY; IMMUNOPRECIPITATION; MICROSCOPY; MOUSE; NONHUMAN; OPTIC NERVE; OPTICAL COHERENCE TOMOGRAPHY; PRIORITY JOURNAL; RETINA BIPOLAR GANGLION CELL; RETINA DEGENERATION; RETINAL THICKNESS; SUCROSE GRADIENT; WESTERN BLOTTING;

AAV VECTOR; BARDET BIEDL SYNDROME; GENE THERAPY; MOUSE MODEL; RETINAL DEGENERATION;

ANIMALS; BARDET-BIEDL SYNDROME; BLOTTING, WESTERN; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; ELECTRORETINOGRAPHY; GENETIC THERAPY; GENETIC VECTORS; IMMUNOHISTOCHEMISTRY; INJECTIONS, INTRAOCULAR; MICE; MICROTUBULE-ASSOCIATED PROTEINS; PHOTORECEPTOR CELLS, VERTEBRATE; RETINAL DEGENERATION; SUBRETINAL FLUID; TRANSDUCTION, GENETIC;

EID: 84883878692     PISSN: 01460404     EISSN: 15525783     Source Type: Journal    
DOI: 10.1167/iovs.13-11673     Document Type: Article

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