Outcomes of haematopoietic stem cell transplantation for inherited metabolic disorders: A report from the Australian and New Zealand Children's Haematology Oncology Group and the Australasian Bone Marrow Transplant Recipient Registry

Pediatric Transplantation

Volumn 17, Issue 6, 2013, Pages 582-588

  Mitchell, R ^a   Nivison Smith, I ^b   Anazodo, A ^a   Tiedemann, K ^c   Shaw, P J ^d   Teague, L ^e   Fraser, C J ^f   Carter, T L ^g   Tapp, H ^h   Alvaro, F ⁱ   O'Brien, T A ^a  

^a SYDNEY CHILDREN'S HOSPITAL   (Australia)

^b Australasian Bone Marrow Transplant Recipient Registry   (Australia)

^c ROYAL CHILDREN'S HOSPITAL   (Australia)

^d CHILDREN S HOSPITAL AT WESTMEAD   (Australia)

^e STARSHIP CHILDREN S HOSPITAL   (New Zealand)

^f ROYAL CHILDREN'S HOSPITAL   (Australia)

^g PRINCESS MARGARET HOSPITAL FOR CHILDREN   (Australia)

^h WOMEN S AND CHILDREN S HOSPITAL   (Australia)

ⁱ JOHN HUNTER CHILDREN S HOSPITAL   (Australia)

Author keywords

adrenoleucodystrophy; bone marrow transplantation; Hurler syndrome

Indexed keywords

ALEMTUZUMAB; BUSULFAN; CD34 ANTIGEN; COTRIMOXAZOLE; CYCLOPHOSPHAMIDE; CYTOTOXIC AGENT; FLUDARABINE; GANCICLOVIR; MELPHALAN; THYMOCYTE ANTIBODY;

ADOLESCENT; ANTIBIOTIC PROPHYLAXIS; ARTICLE; ASPARTYLGLYCOSAMINURIA; CAUSE OF DEATH; CHILD; CYTOMEGALOVIRUS INFECTION; FEMALE; FOLLOW UP; GRAFT FAILURE; GRAFT RECIPIENT; GRAFT VERSUS HOST REACTION; HEMATOPOIETIC STEM CELL TRANSPLANTATION; HEMORRHAGIC CYSTITIS; HUMAN; HURLER SYNDROME; INFANT; INTERSTITIAL PNEUMONIA; MAJOR CLINICAL STUDY; MALE; MANNOSIDOSIS; MYELOABLATIVE CONDITIONING; OVERALL SURVIVAL; PNEUMOCYSTIS PNEUMONIA; PRESCHOOL CHILD; RETROSPECTIVE STUDY; SCHOOL CHILD; SURVIVOR; TREATMENT INDICATION; TREATMENT OUTCOME; UMBILICAL CORD BLOOD; UNRELATED DONORS; VEIN OCCLUSION;

EID: 84881124086     PISSN: 13973142     EISSN: 13993046     Source Type: Journal    
DOI: 10.1111/petr.12109     Document Type: Article

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