Outcomes after allogeneic hematopoietic cell transplantation for childhood cerebral adrenoleukodystrophy: The largest single-institution cohort report

Blood

Volumn 118, Issue 7, 2011, Pages 1971-1978

  Miller, Weston P ^a   Rothman, Steven M ^a   Nascene, David ^a   Kivisto, Teresa ^a   Defor, Todd E ^a   Ziegler, Richard S ^a   Eisengart, Julie ^a   Leiser, Kara ^a   Raymond, Gerald ^b   Lund, Troy C ^a   Tolar, Jakub ^a   Orchard, Paul J ^a  

^a UNIVERSITY OF MINNESOTA MEDICAL SCHOOL   (United States)

^b KENNEDY KRIEGER INSTITUTE   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

ADRENOLEUKODYSTROPHY; ALLOGENEIC HEMATOPOIETIC STEM CELL TRANSPLANTATION; ARTICLE; BRAIN DYSFUNCTION; CHILD; CLINICAL TRIAL; COHORT ANALYSIS; DISEASE COURSE; DISEASE SEVERITY; HUMAN; INCIDENCE; MAJOR CLINICAL STUDY; MALE; MORTALITY; PRIORITY JOURNAL; SCORING SYSTEM; SURVIVAL; TREATMENT OUTCOME;

EID: 80051884762     PISSN: 00064971     EISSN: 15280020     Source Type: Journal    
DOI: 10.1182/blood-2011-01-329235     Document Type: Article

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