Ultrasound-enhanced delivery of Morpholino with Bubble liposomes ameliorates the myotonia of myotonic dystrophy model mice

Scientific Reports

Volumn 3, Issue , 2013, Pages

  Koebis, Michinori ^a   Kiyatake, Tamami ^a   Yamaura, Hiroshi ^a   Nagano, Kanako ^a   Higashihara, Mana ^b   Sonoo, Masahiro ^c   Hayashi, Yukiko ^d   Negishi, Yoichi ^e   Endo Takahashi, Yoko ^e   Yanagihara, Dai ^a   Matsuda, Ryoichi ^a   Takahashi, Masanori P ^f   Nishino, Ichizo ^d   Ishiura, Shoichi ^a  

^a UNIVERSITY OF TOKYO   (Japan)

^b NATIONAL DEFENSE MEDICAL COLLEGE   (Japan)

^c TEIKYO UNIVERSITY SCHOOL OF MEDICINE   (Japan)

^d NATIONAL INSTITUTE OF NEUROSCIENCE   (Japan)

^e TOKYO UNIVERSITY OF PHARMACY AND LIFE SCIENCES   (Japan)

^f OSAKA UNIVERSITY GRADUATE SCHOOL OF MEDICINE   (Japan)

Author keywords

[No Author keywords available]

Indexed keywords

CHLORIDE CHANNEL; CLC 1 CHANNEL; CLC-1 CHANNEL; LIPOSOME; MORPHOLINO OLIGONUCLEOTIDE;

ALTERNATIVE RNA SPLICING; ANIMAL; ARTICLE; CELL LINE; DISEASE MODEL; ELECTROMYOGRAPHY; GENE ORDER; GENE TARGETING; GENE TRANSFER; GENE VECTOR; GENETICS; MICROBUBBLE; MOUSE; MYOTONIC DYSTROPHY; ULTRASOUND;

ALTERNATIVE SPLICING; ANIMALS; CELL LINE; CHLORIDE CHANNELS; DISEASE MODELS, ANIMAL; ELECTROMYOGRAPHY; GENE ORDER; GENE TARGETING; GENE TRANSFER TECHNIQUES; GENETIC VECTORS; LIPOSOMES; MICE; MICROBUBBLES; MORPHOLINOS; MYOTONIC DYSTROPHY; ULTRASONICS;

EID: 84880907954     PISSN: None     EISSN: 20452322     Source Type: Journal    
DOI: 10.1038/srep02242     Document Type: Article

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