RNAi-Mediated Gene Suppression in a GCAP1(L151F) Cone-Rod Dystrophy Mouse Model

PLoS ONE

Volumn 8, Issue 3, 2013, Pages

  Jiang, Li ^a   Li, Tansy Z ^a   Boye, Shannon E ^b   Hauswirth, William W ^b   Frederick, Jeanne M ^a   Baehr, Wolfgang ^a,c  

^a UNIVERSITY OF UTAH HEALTH SCIENCES CENTER   (United States)

^b UNIVERSITY OF FLORIDA COLLEGE OF MEDICINE   (United States)

^c UNIVERSITY OF UTAH   (United States)

Author keywords

[No Author keywords available]

Indexed keywords

GREEN FLUORESCENT PROTEIN; GUANYLATE CYCLASE ACTIVATING PROTEIN 1; GUANYLATE CYCLASE ACTIVATOR; MG1HP4; PARVOVIRUS VECTOR; SHORT HAIRPIN RNA; UNCLASSIFIED DRUG; SMALL INTERFERING RNA;

ALLELE; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CARBOXY TERMINAL SEQUENCE; CONTROLLED STUDY; DISEASE COURSE; DISEASE MODEL; FLUORESCENCE IMAGING; GCAP1 GENE; GENE EXPRESSION; GENE MUTATION; GENE REPRESSION; GENE SILENCING; GENOME; IN VITRO STUDY; MOUSE; NONHUMAN; PROTEIN BINDING; RETINA CONE; RETINA DEGENERATION; RETINA DYSTROPHY; RETINA ROD; RNA INTERFERENCE; SEROTYPE; TRANSGENE; TRANSGENIC MOUSE; ANIMAL; DEPENDOPARVOVIRUS; ELECTRORETINOGRAPHY; GENETICS; HEK293 CELL LINE; HUMAN; METABOLISM; MOLECULAR CLONING; MUTATION; PATHOLOGY; RETINA; RETINITIS PIGMENTOSA;

ALLELES; ANIMALS; CLONING, MOLECULAR; DEPENDOVIRUS; DISEASE MODELS, ANIMAL; ELECTRORETINOGRAPHY; GREEN FLUORESCENT PROTEINS; GUANYLATE CYCLASE-ACTIVATING PROTEINS; HEK293 CELLS; HUMANS; MICE; MICE, TRANSGENIC; MUTATION; RETINA; RETINITIS PIGMENTOSA; RNA INTERFERENCE; RNA, SMALL INTERFERING; TRANSGENES;

EID: 84874604998     PISSN: None     EISSN: 19326203     Source Type: Journal    
DOI: 10.1371/journal.pone.0057676     Document Type: Article

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