RNA interference targeting CUG repeats in a mouse model of myotonic dystrophy

Molecular Therapy

Volumn 21, Issue 2, 2013, Pages 380-387

  Sobczak, Krzysztof ^a,b   Wheeler, Thurman M ^a   Wang, Wenli ^a   Thornton, Charles A ^a  

^a UNIVERSITY OF ROCHESTER MEDICAL CENTER   (United States)

^b ADAM MICKIEWICZ UNIVERSITY   (Poland)

Author keywords

[No Author keywords available]

Indexed keywords

MUSCLEBLIND LIKE 1 PROTEIN; SMALL INTERFERING RNA; TRANSCRIPTION FACTOR; UNCLASSIFIED DRUG;

ALTERNATIVE RNA SPLICING; ANIMAL EXPERIMENT; ANIMAL MODEL; ANIMAL TISSUE; ARTICLE; CAG REPEAT; CONTROLLED STUDY; DNA BASE COMPOSITION; DNA STRUCTURE; DOSE RESPONSE; DOWN REGULATION; ELECTROPORATION; EXON; EXPANDED CUG REPEAT; GENE TARGETING; MOUSE; MYOTONIC DYSTROPHY; NONHUMAN; PROTEIN LOCALIZATION; RNA INTERFERENCE; TRANSCRIPTION REGULATION; TREATMENT DURATION;

MUS MUSCULUS;

EID: 84873414139     PISSN: 15250016     EISSN: 15250024     Source Type: Journal    
DOI: 10.1038/mt.2012.222     Document Type: Article

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